FDA Commissioner Releases Statement on Targeted Therapies, New Efficiency Measures, and Modernizing Development
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FDA Commissioner Releases Statement on Targeted Therapies, New Efficiency Measures, and Modernizing Development

According to a story from Pharma Voice, Dr. Scott Gottlieb, the current commissioner of the US Food and Drug Administration (FDA) has recently released a statement in regards to efforts…

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Two Phase 2 Clinical Studies of a Drug for Rare Epilepsies Have Been Initiated

Two Phase 2 clinical trials called ‘Elektra’ and ‘Arcade’ have been initiated. They will investigate the drug OV935/TAK-935 as a potential treatment for paediatric patients with rare epilepsies. For more…

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Takeda and Ovid Have Provided an Update on the Clinical Development Program for an Investigational Anti-Epileptic Drug
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Takeda and Ovid Have Provided an Update on the Clinical Development Program for an Investigational Anti-Epileptic Drug

  Takeda Pharmaceutical Company Limited and Ovid Therapeutics have released an overview of the clinical development program for TAK-935/OV935, an investigational drug that is being developed as a potential anti-epileptic…

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New Partnership May Have Implications for Those with Dravet, Alzheimer’s, Epilepsy, and More

According to Newswire, the two companies, BioMotiv and Cure Network Dolby Acceleration Partners (CNDAP) partnered up together in order to create small molecules that can potentially treat various neurological disorders, including…

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Three Planned Studies of an Experimental Drug to Treat Rare Epilepsies Have Been Announced
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Three Planned Studies of an Experimental Drug to Treat Rare Epilepsies Have Been Announced

The organisations Takeda Pharmaceutical Company and Ovid Therapeutics are collaborating over the development of the experimental drug TAK-935/OV935 as a possible treatment for several rare epilepsy syndromes. Takeda has just…

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A Phase 3 Study Has Shown Encouraging Results for an Investigational Treatment for Dravet Syndrome
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A Phase 3 Study Has Shown Encouraging Results for an Investigational Treatment for Dravet Syndrome

Zogenix, Inc has announced the top-line results from a Phase 3 study of the investigational drug ZX008 (low-dose fenfluramine hydrochloride) for the treatment of young patients with Dravet syndrome. The…

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First Drug Made From Cannabis Approved by the FDA For Dravet Syndrome and Lennox-Gastaut Syndrome
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First Drug Made From Cannabis Approved by the FDA For Dravet Syndrome and Lennox-Gastaut Syndrome

According to a story from the Washington Post, the US Food and Drug Administration (FDA) has cleared the approval of Epidiolex®, a solution whose active ingredient is a refined version…

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Most Epilepsy Patients Benefit From Current Medications, But Look Forward to New Treatments

According to a story from Scimex, a recent assessment of available treatments for Dravet syndrome and other types of epilepsy has reaffirmed that anticonvulsant medications are still the most effective…

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Scottish Mother Prepares to Obtain Cannabidiol Oil For Her Son With Rare Epilepsy
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Scottish Mother Prepares to Obtain Cannabidiol Oil For Her Son With Rare Epilepsy

According to a story from edinburghnews.com, mother Karen Gray is about to seek access to cannabidiol oil for her five-year-old son, Murray, who has a rare type of epilepsy, Myoclonic Astatic…

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A Groundbreaking Marijuana-Derived Treatment is Getting Closer to FDA Approval for Treating Rare Forms of Epilepsy
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A Groundbreaking Marijuana-Derived Treatment is Getting Closer to FDA Approval for Treating Rare Forms of Epilepsy

According to a story from statnews.com, a drug derived from substances originating in the cannabis plant may be nearing approval by the U.S. Food and Drug Administration. The drug is…

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An Experimental Drug Was Helping A Girl With Dravet Syndrome. Will She Lose Access After the Trial?
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An Experimental Drug Was Helping A Girl With Dravet Syndrome. Will She Lose Access After the Trial?

According to a recent story from CityNews Toronto, Alara Ozkose's Dravet syndrome was preventing her from being able to live a life that was even close to normal. She was…

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UK Family Travels to The Netherlands To Find Treatment For Their Daughter With Dravet Syndrome
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UK Family Travels to The Netherlands To Find Treatment For Their Daughter With Dravet Syndrome

According to BelfastLive, Darren and Danielle Gibson, the parents of little six-year-old Sophia battling Dravet syndrome, traveled out of the country in search of the care she needs. For the…

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What Do You Know About Cannabidiol Drug Interactions?
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What Do You Know About Cannabidiol Drug Interactions?

Recent studies have shown promising results that cannabidiol (CBD) helps relieve different forms of epileptic seizures like those from Lennox-Gastaut syndrome and Dravet syndrome. Lennox–Gastaut syndrome (LGS) is particularly severe, childhood…

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Editor’s Choice: Soo Many Promising Results, Advancements and Treatment Options for the Rare Disease World!

TGIF Patient Worthians! This week we have promising results on promising results. First up is news on a Dravet syndrome treatment. Second is a Lupus Nephritis drug in the works! Third…

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