Receiving a rare disease diagnosis can be difficult, frustrating, and scary. Laura Hamilton, the host of A Place in the Sun, is no stranger to this phenomenon; last year she…
In a recent press release, biopharmaceutical company Swedish Orphan Biovitrum AB ("Sobi") shared that the first patient was dosed in a Phase 3 clinical trial evaluating avatrombopag for pediatric patients…
According to BioSpace, biotechnology company Argenx recently announced positive results from their Phase III ADAPT clinical trial. The company, who seeks to find breakthroughs in immunology and translate them…
Abbey Luffman was a 16-year-old from Owego, New York excited about getting her learner's permit. She was also very generous; she didn't even hesitate to check the box for organ…
Ella Casano is a 12-year-old living with Idiopathic Thrombocytopenic Purpura (ITP) who had a brilliant idea about how she could help other children living with rare diseases like her own.…
According to a story from Market Screener, an analysis of real-world data (data gathered outside of the clinical setting) suggests that the drug eltrombopag, marketed as Revolade, offers substantial advantages…
Idiopathic thromocytopenic purpura (ITP) is a rare bleeding disease that affects about 3 in 100,000 people in the US-- or, at least, that's how many people are diagnosed-- according to SELF.…
Some diseases are a mystery. If the name of the disorder starts with "idiopathic," it means that no one really knows what causes it. That's the case with a rare…
There is so much about how our bodies work that we take for granted. The careful concert of organs, systems, and structures that allow us to breathe, walk, talk, and…
In April of this year, Rigel Pharmaceuticals, Inc. announced that it has submitted a New Drug Application (NDA) to the U.S. FDA for fostamatinib, a drug for patients with chronic…
What’s the biggest nightmare of any parent? Is it the fear of a kidnapper? Is it some horrible, lifelong medical condition that needs constant medicine or repeated hospitalization? Is it…
Some memories come to mind so vividly you remember every sensation: the smells, the sights, the sounds, the feelings. For me, many of my most vivid childhood memories involve the…
If you're living with thrombocytopenia (that is, a severely low level of platelets in your blood), then Dr. Mei X. Wu may be your new best friend. The associate professor…
Idiopathic thrombocytopenic purpura (ITP) is a rare immune disorder that can cause bleeding (from an insufficient platelet count) or bruising because the body is destroying the patient's blood platelets. Normally,…
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