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Living With Primary Hyperoxaluria: A Rare Patient Story
Molly Ouimet was three years old when she got her first kidney stone. Molly, who wasn't very vocal at the time, had a difficult time explaining the pain that she…
Alnylam Seeks FDA Approval for First Treatment of Primary Hyperoxaluria Type 1
Copyscape score: 2% Alnylam has recently completed the third phase of their clinical trial of lumasiran, which was created for the treatment of primary hyperoxaluria type 1 (PH1). While they…
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New PH1 Treatment Clears Phase 3 Study
Big development for those in the primary hyperoxaluria type 1 (PH1) community! Alnylam Pharmaceuticals just announced that its Phase 3 study of lumasiran, an investigational therapy for the treatment of primary…
Watch: Pharma Company Produces Cartoon Series for PH1 Awareness among Kids
Alnylam Pharmaceuticals has developed and produced a cartoon series aimed at educating people -- especially young people -- about the pediatric rare disease primary hyperoxaluria type 1 (PH1). The campaign…
Pediatric Clinical Trial Initiated for Primary Hyperoxaluria Type 1!
Alnylam Pharmaceuticals has been developing lumasiran as a potential treatment for primary hyperoxaluria type 1 (PH1). This investigation began with ILLUMINATE-A, a clinical trial whose results should be announced by…
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New Updates on Studies of Lumasiran in Patients With Primary Hyperoxaluria Type 1
Alnylam has provided updates about their programs for patients with primary hyperoxaluria type 1 (PH1), a rare condition that affects the kidneys and bladder. As part of their Alnylam Act® program,…
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Proof of Concept Data Released for Potential Primary Hyperoxaluria Treatment
According to a story from BioPortfolio, the drug development company Dicerna Pharmaceuticals recently announced the release of proof of concept data in its Phase I trial testing the company's experimental…
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Study Shows Encouraging Results For an Experimental Treatment For Primary Hyperoxaluria Type 1
A phase 1/2 study of the drug lumasiran for the treatment of primary hyperoxaluria Type 1 has produced encouraging results, reports Alnylam Pharmaceuticals. The full article can be read here,…
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A Study of an Investigational Drug For Primary Hyperoxaluria Has Dosed its First Patient
Dicerna Pharmaceuticals has dosed the first patient with primary hyperoxaluria in Group B of a clinical trial of the investigational drug DCR-PHXC. Dicerna has also announced that DCR-PHXC has just…
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Is Hope on the Horizon for a Primary Hyperoxaluria Type 1 Cure?
This past July, professionals, patients, and families with loved ones who struggle with primary hyperoxaluria Type 1, 2 and 3 were offered a glimpse of hope and a better future.…
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Girl with PH1 Undergoes Dual Live-Donor Liver-Kidney Transplant
An Indian family found out their little girl, Parvathy, only three months old, had primary hyperoxaluria type 1. In simple terms, those words meant she was born without the enzyme…
Organ Donation Could Change The Life of This Child with PH1
According to QC Online, at six months old, Lorelei Lovelady was diagnosed with primary hyperoxaluria type 1 (PH1). Now, almost 9 months, the disease has caused her to need a new liver…
