As reported on drugs.com, Revolution Medicines has reported practice-changing efficacy results from a pivotal Phase 3 trial evaluating daraxonrasib in patients with metastatic pancreatic ductal
This, year the PCBers will meet in Indianapolis, Indiana. They will be celebrating 30 years as a community, as well as celebrating a much brighter
Johnson & Johnson announced that the U.S. Food and Drug Administration (FDA) has granted Priority Review to IMAAVY® (nipocalimab-aahu), marking a significant milestone as the
As reported on Business Wire, Enveda, a clinical-stage biotechnology company focused on discovering novel small-molecule medicines, has reported encouraging results from a Phase 1b study
A recent article from Inside Precision Medicine states: For decades, systemic lupus erythematosus (SLE) has resisted tidy solutions, a shapeshifting autoimmune disease that crosses into
AstraZeneca has announced positive results from the pivotal phase III MIRANDA trial of tozorakimab, a groundbreaking first-in-class monoclonal antibody designed to treat Chronic Obstructive Pulmonary
On January 20, 2014, at 54 years old, I experienced what I casually called an “anxiety numbness event.” My left thumb and index finger went
The US Food and Drug Administration (FDA) has approved Idvynso, a groundbreaking two-drug single-tablet regimen combining 100 mg doravirine and 0.25 mg islatravir, for treating
My story began very suddenly on May 4th, 2025, when I was home from graduate school visiting my family. It had been a great day,
Glioblastoma multiforme (GBM) is the most common malignant brain tumor in adults and remains one of the most difficult cancers to treat. Characterized by aggressive
WebMD published a story about a young woman, Maddie, who had spent nine years in wheelchair confinement resulting from a rare metabolic disease related to
Health Canada has officially approved Cysklar® (cysteamine ophthalmic solution) 0.44%, marking a significant breakthrough for Canadians living with cystinosis. According to BusinessWire.com, the approval enables
Putting feelings into words does more than help you reflect. Brain imaging research shows it can shift activity inside emotional circuits. If you are someone
Most people see the bed first. That’s what defines me to them. The bed in the living room, the fact that I’m always in it.
As reported by Business Wire, Enanta Pharmaceuticals has initiated its first clinical study of EDP-978, a novel oral inhibitor of the KIT receptor tyrosine kinase
Editor’s Note: Patient Worthy is honored to share this article from our friend Jessica Lynn. To see the article in its original format, please click
Cancer cachexia represents one of oncology’s most overlooked catastrophes. Patients waste away, lose appetite, and deteriorate despite receiving chemotherapy, yet few treatment options exist to
I had learned that the many twists and turns on our rare disease path were similar to the families we met Originally published on May 11, 2022,
Throughout the week, Patient Worthy is highlighting Huntington's Disease with educational content aimed at raising awareness and fostering greater understanding in our community.
We’ll be sharing information on our socials and bit.ly/425L89T to educate, empower, and support those affected.
If you'd like to share your story with Huntington's Disease, click here: bit.ly/4dV7gru
#HuntingtonsDisease #HD #ShareYourStory #PatientWorthy
Breaking Through: UniQure's Huntington's Gene Therapy Pursues UK Approval After US Setback bit.ly/4f1KjWo Read now at PatientWorthy.com
#PatientWorthy #uniQure #huntington'sDisease
While there is currently no cure for Becker muscular dystrophy, treatment and supportive care can help improve quality of life, preserve mobility, and manage complications over time. From physical therapy and cardiac care to emotional support and adaptive tools, every aspect of management plays a role in helping individuals maintain independence and daily function. Awareness doesn’t just educate — it encourages support, research, and hope for better outcomes in the future. 💙
Click the link to share your story - bit.ly/3VuxFDV
#BeckerMuscularDystrophy #ChronicIllness #PatientWorthy
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