As reported on BioSpace, Moderna has entered a commercialization partnership with Italy‑based Recordati to support the development of mRNA‑3927, an investigational mRNA therapy for propionic
Osteosarcoma is a diagnosis no family should ever have to face. It is the most common primary bone cancer in children and adolescents, yet treatment
A groundbreaking genetic study published in The Journal of Clinical Endocrinology & Metabolism and reported by ScienceDaily.com has revealed that obesity and high blood pressure
Twenty years is a long time to believe a cancer chapter has closed. For two decades after my radical prostatectomy, I lived with the quiet
Editor’s Note: Patient Worthy is honored to share part 1 in an ongoing 10-part series, written and shared with us by Elena Genik. When Everything
A growing body of research shows that sleep quality, dietary sodium, and hypertension are more closely linked than once believed — and two major healthcare
Vera Therapeutics announced a major milestone in drug development on January 7, 2026, when the U.S. Food and Drug Administration granted Priority Review to the
As reported by the European Pharmacy Review, a combination approach using Johnson & Johnson’s small‑molecule therapy Caplyta (lumateperone) alongside standard antidepressants continues to show promising
A newly published Phase 1/2 study in The New England Journal of Medicine, and reported on by the Manila Times, highlights promising early results for tividenofusp
A New Approach to a Persistent Problem Celcuity has reached a critical inflection point in its pursuit of a novel breast cancer treatment. The FDA’s
As reported on Healio, glucagon-like peptide-1 (GLP-1)–based therapies are rapidly reshaping the landscape of diabetes and chronic kidney disease (CKD) management. Originally developed for glycemic
Immunoglobulin A nephropathy (IgAN) remains one of the most common primary glomerular diseases worldwide, yet effective treatments are limited. A new study, recently published in
If you got past the title without rolling your eyes or getting angry (I understand if you did either or both as you will see
Breaking the Cycle of Prescription Dependency The opioid epidemic that has devastated American communities for decades may finally have a novel challenger. According to Bezinga.com,
As reported by Clinical Trials Arena, Axsome Therapeutics has begun dosing patients in its FORWARD Phase III clinical trial, a pivotal study designed to evaluate
Brussels — On February 24, 2026, the acclaimed Netflix documentary The Remarkable Life of Ibelin received the Media & Awareness Raising Award at the EURORDIS
The Three-Year Fight That Changed Everything When Giles Turner learned his postcode could determine whether he received life-saving cancer treatment, he didn’t accept it quietly.
As reported on PM Live, a new clinical trial hub focused on epidermolysis bullosa (EB) has been established at University Medical Center Groningen (UMCG) in
Finding the exact location of a change in the genome can bring long-awaited answers, turning years of uncertainty into clarity. For many in the rare disease community, pinpointing this spot is a key step toward an accurate diagnosis, understanding inheritance, and opening the door to more informed care and support. #rarewordoftheweek #raredisease #rarediseaseawareness #rarediseasemonth #PatientWorthy
Gaten Matarazzo's journey with cleidocranial dysplasia is a testament to resilience, advocacy, and the power of using your voice. This Rare Disease Month, we celebrate him and all those living with rare conditions! #rarediseasemonth #cleidocranialdysplasia #gatenmatarazzo #raredisease
#shareyourstory with us here: bit.ly/4dV7gru
We're honored to share Kristen's story about living with myelofibrosis. Read here:
patientworthy.com/2026/02/17/we-will-never-ring-the-bell-my-myelofibrosis-story/
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