Takeda Pharmaceutical Company has announced breakthrough results from Phase 3 trials of zasocitinib (TAK-279), an innovative oral treatment for moderate-to-severe plaque psoriasis that offers patients
As reported on FierceBioTech, Biohaven closed out the holiday period with disappointing news: its investigational Kv7.2/7.3 potassium‑channel modulator, BHV‑7000, did not demonstrate efficacy in a
Editor’s Note: Patient Worthy is proud to share this story from our friends at Elephants & Tea. To see the story in its original format,
Menopause-related insomnia affects approximately one in four women during the menopausal transition, yet it remains significantly underdiagnosed and undertreated. A new analysis published in Maturitas
As reported by NewsWise, new clinical study led by investigators at the University of North Carolina at Chapel Hill is offering rare hope for families
Axsome Therapeutics has reached a significant regulatory milestone with the US Food and Drug Administration’s acceptance of a supplemental New Drug Application (NDA) for AXS-05
As reported by Forbes, the U.S. Food and Drug Administration has granted approval to Flow Neuroscience for the first prescription brain stimulation device designed for
Soleno Therapeutics has achieved a significant milestone in the treatment of a rare genetic disorder, announcing the publication of pivotal clinical study results for VYKAT™
Editor’s Note: Patient Worthy is proud to share this caregiver story submitted to us by Missy Williams. Nine years later, I can still picture the
ImmunityBio’s latest clinical findings reveal a significant development in the ongoing battle against non-muscle-invasive bladder cancer, with three-year follow-up data suggesting that combining Anktiva with
Editor’s Note: Patient Worthy is proud to share this article, originally written by Katie Tat, from our friends at Elephants & Tea. To see the
As reported on Science Daily, a recent clinical study suggests that a traditional Chinese herbal remedy may offer a unique advantage in treating major depressive
FibroBiologics Inc, a clinical-stage biotechnology company, has announced a significant breakthrough in regenerative medicine by submitting a Phase 1/2 Investigational New Drug (IND) application to
Editor’s Note: Patient Worthy is honored to share Michelle Patidar’s patient story, provided to us by our friends at Elephants & Tea. To see the
My chronic health journey is super complicated. When I first started experiencing my symptoms I wouldn’t tell anyone what I was feeling. I would wake
When pharmaceutical companies develop medications for serious diseases like prostate cancer, few anticipate how those treatments might transform care for entirely different patient populations. Yet,
Altimmune has released updated 48-week results from its phase 2 trial of pemvidutide, a GLP-1/glucagon dual receptor agonist being developed for metabolic dysfunction-associated steatohepatitis (MASH),
CRISPR Therapeutics has announced encouraging early results for zugocaptagene geleucel (zugo-cel), its investigational allogeneic CAR T therapy targeting CD19, in both autoimmune diseases and hematologic
Cure Syngap1Funding Priorities. Biorepository. Genetic Testing. How to move for a clinical trail! #S10e197
Monday, February 2, 2026 - Week 6
🎧👀 View full episode here: youtu.be/0fH3Q5olwJI
All US Families, please take the time to fill out the ProMMiS Survey. It takes 5 minutes. It's super important. Even if you haven't been there, we need your feedback.
English: curesyngap1.org/SurveyProMMiS
Spanish: curesyngap1.org/encuestaProMMiS
Our funding priorities for 2026 are Genetics, Behaviors & Isoforms. www.linkedin.com/posts/graglia_syngap1-curesyngap1-grants-activity-7421952845693788160-EHeK
Pubmed 2026 is at 6!
pubmed.ncbi.nlm.nih.gov/?term=syngap1&filter=years.2026-2026&sort=date
Coolest paper on Pubmed… GC rich areas were missed, so not only do we need to push for testing, but also REtesting.
pubmed.ncbi.nlm.nih.gov/41577710/
Bravo to CURE SYNGAP1 Poland (please send me a shirt) & thank you to CAMP4
Event: www.linkedin.com/posts/curesyngap1_it-was-a-day-to-remembera-perfect-combination-activity-7422379...
Don’t move to or from US/EU/LatAm etc. This question keeps coming. Please stay where you are and advocate like crazy. Set up CURE SYNGAP1 [Your location]
Biorepository needs more samples. Check out the list and map here docs.google.com/presentation/d/1IjaHILXj7AlBDlbTJgvYrkBS_0bnI8VCnTIiPXJ7JGM/edit?usp=sharing and contribute blood. The data and research we do with these samples is invaluable.
Annual update to Champions of Hope! curesyngap1.org/champions-of-hope/
May 28, San Francisco, CA: cureSYNGAP1.org/SF26
SOCIAL MATTERS
4,661 LinkedIn. www.linkedin.com/company/curesyngap1/
1,520 YouTube. www.youtube.com/@CureSYNGAP1
11.2k Twitter twitter.com/cureSYNGAP1
45k Insta www.instagram.com/curesyngap1/
$CAMP stock is at $3.83 on 27 Jan. ‘26 www.google.com/finance/beta/quote/CAMP:NASDAQ
Like and subscribe to this podcast wherever you listen. curesyngap1.org/podcasts/syngap10/
Episode 197 of #Syngap10 #CureSYNGAP1 #Podcast
#battendisease #rareneurology #familysupport BDSRA FoundationFriday the 13th will actually be your lucky day because you can chat with Heather Dainiak! ☕ Join our Director of Family Support for this month’s Coffee Chat next Friday. This is a low-pressure space to connect, reflect on the start of a new year, and talk about what care looks like right now, for ourselves and our families. Learn more: ow.ly/s6MQ50Y6B1l
Want more programming like this? Please donate to the BDSRA Foundation: ow.ly/NfyF50Y6B1n
I Didn't Ask For Any Of This with Allan Finnegan AA Cure In Sight Ocular Melanoma🎙️ New Episode!! 👏
I Didn't Ask For Any Of This with Allan Finnegan
📺 youtu.be/0UjPkER7V8g
🎧 www.podbean.com/eas/pb-xbczy-1a359d2
In this new episode of the Eye Believe Podcast, we are honored to share a powerful conversation with Allan Finnegan—a reverend, comedian, and former Britain’s Got Talent finalist who is living with metastatic ocular melanoma. 💙
Allan brings incredible warmth, humor, and faith to this hope-filled interview as he reflects on life, purpose, and finding light even in the hardest seasons. He also shares about his new book, I Didn’t Ask for Any of This, a moving reminder of resilience and meaning through uncertainty.
This is an unforgettable episode you won’t want to miss.
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