The findings were recently published in Nature Immunology and reported by Precision Medicine suggesting that a factor called Interferon Regulatory Factor 4 (IRF4) takes responsibility
As reported on NPR, Tatiana Schlossberg, journalist and granddaughter of former U.S. President John F. Kennedy, has disclosed that she is battling a rare and
As reported on BioSpace, the U.S. Food and Drug Administration (FDA) has launched an investigation into reports of serious adverse events, including one fatality, associated
Three-year-old Oliver Chu has stunned clinicians after becoming the first person with Hunter syndrome (MPS II) to receive an experimental gene therapy and showing striking
Editor’s Note: Patient Worthy is pleased to share this article from our friends at Elephants & Tea, originally written by Cecily Liu. To see the
The United Leukodystrophy Foundation (ULF) is proud and excited to announce a partnership with Marc Nolan, a Chicago-based footwear brand, who is launching a new
The U.S. Food and Drug Administration (FDA) has approved Koselugo (selumetinib), an oral MEK inhibitor developed by Alexion, AstraZeneca Rare Disease, for adults with neurofibromatosis
Hundreds more patients in England with relapsed or refractory diffuse large B-cell lymphoma (DLBCL) will gain earlier access to glofitamab (Columvi) after new guidance from
Vera Therapeutics has taken a major step toward transforming treatment for immunoglobulin A nephropathy (IgAN), submitting a Biologics License Application to the U.S. Food and
My journey started abruptly last year. It was a completely normal day—until it wasn’t. I’m an RN, and I slept most of the day before
I’m Jenna, a 36-year-old married mother of one son, and I have neuroendocrine cancer (NETs). It is a rare type of cancer, and 60% of
The holidays can stir up many emotions: joy, nostalgia, and sometimes heartache.
If you’re missing someone this season or feeling the weight of what’s changed, know that it’s okay to slow down, protect your peace, and do the holidays your way.
Not every tradition has to stay the same. Sometimes healing looks like creating new ones, honoring old ones quietly, or simply making space to rest.
#ChronicIllnessCommunity #RareDiseaseWarrior #CancerAwareness #ShareYourStory #PatientWorthy
Gilead's Dual-Action HIV Breakthrough: Single-Tablet Bictegravir-Lenacapavir Regimen Shows Promise in Phase 3 Trial bit.ly/4j4NkVN Read now at PatientWorthy.com
#PatientWorthy #HIV #HIVTreatment #clinicaltrials
The FDA has given early approval to Enhertu as a frontline treatment for HER2+ metastatic breast cancer. Read more here:
patientworthy.com/2025/12/30/fda-approves-enhertu-combination-for-first-line-her2-positive-breast...
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