
The Silent Struggle – Mental Wellness in NF2 Surgery
Editor’s Note: This article was shared with us by our friends at the Cure NF2 Foundation, in honor of May 22nd being World NF2 Awareness

Editor’s Note: This article was shared with us by our friends at the Cure NF2 Foundation, in honor of May 22nd being World NF2 Awareness

Exelixis has taken a major step forward in its colorectal cancer development pipeline by securing supplies of Merck’s Keytruda for an upcoming phase 3 clinical

Betty Vertin is a mother, writer and a fierce defender of the decisions she and her husband Jason made about the seven children they brought

According to the CDC, a look back at April 2026 cumulative reports showed more than 139 pediatric deaths with approximately 250,000 people hospitalized. In simple

Atossa Therapeutics Inc. has achieved a significant regulatory milestone with the U.S. Food and Drug Administration’s grant of Rare Pediatric Disease (RPD) designation to (Z)-endoxifen

An article from University of Michigan highlighted Jolanta Grembecka and her husband Tomasz Cierpicki, both assistant professors in U of M’s Department of Pathology, who

Milenia Makani is an abstract artist living in London. She lives with Hypermobile Ehlers-Danlos Syndrome (hEDS), and has launched an international art fundraiser to support

What happens when a pharmaceutical first-mover discovers its historic achievement may not be a blockbuster? Arvinas and Pfizer found an answer this week by handing

What is Parkinson’s Disease – known as PD for short? Parkinson’s Disease was first discovered in 1817 by a British doctor named James Parkinson. From

A recent article by Dr. Rosalie Greenberg explores the possible relationship of infections caused by ticks and psychiatric conditions in children, including PANS or PANDA

Abeona Therapeutics Inc. has announced a significant expansion in access to ZEVASKYN, marking the activation of Children’s Hospital of Philadelphia (CHOP) as the sixth Qualified

As reported on PharmaBiz, Regenxbio has announced encouraging topline findings from the pivotal Phase III portion of its ongoing AFFINITY DUCHENNE clinical program evaluating RGX-202,

Biossil, based in Toronto and co-founded by Dr. Alexander Mosa (Chair, CSO and co-founder) and Anthony Mouchantaf (CEO and co-founder), is making headway for rare

As reported on PharmaTimes, Poolbeg Pharma has secured a Canadian patent protecting the use of p38 MAPK inhibitors, including its lead candidate POLB 001, for preventing

Editor’s Note: This story was originally published on Linked-In and is shared with permission by Olga Lucia Torres. She waited an hour and fifteen minutes to

As reported on Healio, emerging real-world evidence suggests that glucagon-like peptide-1 (GLP-1) receptor agonists—and related dual agonists—may play a significant role in lowering the risk

I remember the day I realized something was wrong, as clearly as if it happened this past weekend. It was a beautiful morning in June.

Systemic lupus erythematosus punishes patients twice. First comes the disease itself, an autoimmune disorder where the body attacks its own tissues, causing debilitating fatigue, joint
A diagnosis may change parts of your life, but it does not change your value. You are more than a chart, a symptom, a test result, or a label. Your strength, kindness, resilience, dreams, and the impact you have on others cannot be measured by a diagnosis. On the hardest days and the best days, your worth remains the same.
#chronicillness #chronicillnessawareness #invisibleillness #raredisease #rarediseaseawareness #quote #inspirationalquote #PatientWorthy
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Cure GM1 Foundation #gotoyourconference #findyourtribeCaregiver Check-In, Week 2: find your people.
Connection eases the weight. Send the text. Reply to the message. Sit on a call with another GM1 family. You do not have to explain everything to be understood here.
Reach out to one person in this community this week. A note, a voice message, a wave. It matters.
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@Stephy'sPlace #griefI missed you quietly today.
So quietly that no one noticed.
I missed you as I climbed out of bed and as I brushed my teeth; when I waited at the lights on the drive into work and as I heard the rain outside my window.
I missed you as I ordered lunch and as I kicked off my shoes when I got home; as I switched off the lights and climbed into bed for the night.
I missed you without tears or noise or fanfare.
But oh how I felt it.
I felt it in the morning, at lunchtime, in the evening and at night. I felt it as I woke, as I waited, as I worked. I felt it at home, on the road, in the light, in the dark, in the rain.
I felt it in every one of those moments, each one sitting heavier and heavier as the weight of me missing you kept growing and growing.
Yes, I missed you so quietly today.
But I felt it so loudly.
‘Quietly’ By: Becky Hemsley
Artwork by Lilymoon
www.stephysplace.org
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