As reported on MedicalXpress, the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion for several therapies this
Editor’s Note: Patient Worthy is proud to share part 7 of 10 of Elena Genik’s blog series, detailing her experiences with Graves disease and thyroid
As reported on the Manila Times, Aucta Pharmaceuticals has officially introduced PYQUVI™ (deflazacort) oral suspension 22.75 mg/mL, marking the company’s entry into the U.S. commercial
CureDuchenne is hosting several free events in 2026 to support families living with Duchenne and Becker muscular dystrophy. These events, called CureDuchenne CARES, will take
Twelve‑month, real‑world data from a large U.S. registry suggest that faricimab provides effective, durable, and safe treatment for retinal vein occlusion (RVO), reinforcing findings from
The U.S. Food and Drug Administration has agreed to review Otsuka Pharmaceutical’s application for centanafadine, a new extended‑release therapy under investigation for attention‑deficit hyperactivity disorder
Editor’s Note: Patient Worthy is honored to share part 6 of 10 of Elena Genik’s series of blog posts detailing her journey with Graves disease
A first-of-its-kind Phase 3b study has shown that combining Eli Lilly’s Taltz (ixekizumab) with Zepbound (tirzepatide) delivers superior benefits for adults living with both active
As reported by Bioengineer, new insights published by Nastoupil L.J. in Nature Reviews Clinical Oncology (2026) highlight an important evolution in the management of relapsed
Editor’s Note: Patient Worthy is honored to share this article from our friends at Heal Canada, written by Karen Hawthorne. Anemia is one of the
A new study in Nature Communications and reported by Scienmag.com overturns a central assumption in eye biology by showing that key stem cells for the
In a recent statement by AstraZeneca, AstraZeneca and Daiichi Sankyo’s antibody‑drug conjugate Datroway (datopotamab deruxtecan) has been granted Priority Review by the U.S. Food and
Editor’s Note: Patient Worthy is pleased to share part 5 of 10 in an ongoing series of blog posts, provided to us by Elena Genik.
A trio of Swiss biotechnology companies is advancing diverse therapeutic pipelines, with recent developments spanning inflammatory skin disease, immune‑mediated hair loss, and hard‑to‑treat cancers. Together,
As reported on BioSpace, Moderna has entered a commercialization agreement with Recordati valued at up to $160 million to support late‑stage development and future market
Scientists find polymer-coated nanoparticles together with therapeutic drugs offer promise for cancer treatment, including treatment for ovarian cancer. According to Science Daily, these nanoparticles may
A UCLA Health study published on UCLAHealth.org suggests that numbers already used to gauge heart health may also offer an early warning for serious eye
As reported on ScienceDaily, a research team at the Icahn School of Medicine at Mount Sinai has unveiled a novel immunotherapy that tackles metastatic cancer
ALS isn’t just a diagnosis — it’s a reality that reshapes everyday life, relationships and independence.
Awareness means learning beyond the surface, listening to lived experiences and understanding why continued research, access to care and early recognition matter. The more we educate ourselves, the better we can support individuals and families navigating this disease.
Knowledge builds compassion. Compassion builds change.
#ALSAwareness #LouGehrigsDisease #RareDiseaseOfTheWeek #RareDiseaseAwareness #ShareYourStory #PatientWorthy
Huntington’s Disease (HD) is more than a diagnosis—it’s a lifelong journey for individuals and families.
HD is a rare, inherited condition that gradually affects movement, thinking, and behavior. Symptoms can include involuntary movements, balance and speech difficulties, changes in memory or decision‑making, and shifts in mood or personality. Both Adult‑Onset HD and the rarer Juvenile HD bring unique challenges, but early recognition and supportive care can make a powerful difference.
💙 Awareness leads to understanding. Understanding leads to compassion.
If you're interested in sharing your story with Huntington's Disease, click the link below.
bit.ly/4dV7gru
#HuntingtonsDisease #HDAwareness #PatientWorthy #ShareYourStory
Parent Project Muscular Dystrophy #charlie!Tomorrow is Rare Disease Day, and this week PPMD is spotlighting stories from our Duchenne and Becker community.
Meet Charlie from New York, living with #Duchenne #musculardystrophy.
“Community is everything—those who have taken this journey and those that are side by side with us on our journey, provide strength and courage at the most challenging times. The PPMD community is our Duchenne lifeline, they’re always there and ready to help,” says Charlie’s mom, Cheryl.
Learn more about Rare Disease Day and share your story to come together and raise awareness for the global rare disease community: www.rarediseaseday.org/
#RareDiseaseDay #EndDuchenne
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
