Colorectal cancer
Skipping A Colonoscopy Almost Cost Me Everything
Editor’s Note: Patient Worthy is proud and honored to share Jennifer’s story with cystic fibrosis and colon cancer, originally published on the Cystic Fibrosis Research
Bridging Nutrition Science and Patient Care: ANA and Jazz Pharmaceuticals Launch Cardiovascular Health Initiative
- April 2, 2026
The Mentor She Wished She Had – How Elizabeth Became a Lifeline for EB Families
How to Build a Lasting Legacy While Living with Chronic Illness
The Dravet Syndrome Foundation of Spain’s Annual Meeting 2026
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THE LATEST FROM PATIENT WORTHY
Seizures
Momentum Builds Across Biotech Pipeline: Seizure Breakthrough, Cell Therapy Revival, and Obesity Medicine Gains
The biotechnology sector experienced significant positive developments this week, with Xenon Pharmaceuticals’ seizure medication achieving a decisive late-stage victory while regulatory pathways accelerated for several
Breast Cancer
GLP-1 Receptor Agonists and Breast Cancer: Promising Signals, Pressing Questions
As reported on Healio, glucagon-like peptide-1 (GLP-1) receptor agonists, best known for treating diabetes and obesity, are emerging as unexpected players in breast cancer care.
Triple-negative breast cancer
Study: Engineered Immune Cells and Targeted Treatments May Slow the Spread of Triple-Negative Breast Cancer
CAR T- cells are immune cells that are engineered in a laboratory to attack cancer. The therapy has worked as planned for certain blood cancers
BRCA-mutated Breast Cancer
Breakthrough DNA Repair Inhibitor Advances Rapidly Toward Clinic: Artios’ ART6043 Earns FDA Fast Track Status for Resistant Breast Cancer
Artios Pharma has achieved a significant milestone in cancer treatment development with the U.S. Food and Drug Administration’s granting of Fast Track designation to ART6043,
Multiple Myeloma
Bristol Myers Squibb Reports Positive Phase 3 Data for Mezigdomide-Based Oral Regimen in Relapsed or Refractory Multiple Myeloma
As reported on drugs.com, Bristol Myers Squibb (BMS) has announced encouraging interim results from the Phase 3 portion of the SUCCESSOR-2 clinical trial evaluating oral
Hunter Syndrome
FDA Explains Rejection of Regenxbio’s Hunter Syndrome Gene Therapy
As reported on FierceBioTech, the U.S. Food and Drug Administration has released its complete response letter (CRL) detailing why it declined to approve Regenxbio’s experimental
Breast Cancer
Roche’s Phase III persevERA Trial of Giredestrant Misses Primary Endpoint in Advanced ER-Positive Breast Cancer
As covered on PharmaBiz, Roche has reported topline results from the phase III persevERA Breast Cancer study, which evaluated the oral selective oestrogen receptor degrader
Rare Disease
BASELINE
Editor’s Note: Patient Worthy is proud to share this article from our friends at the Courageous Parents Network. A parent often can sense when there
Breast Cancer
Daiichi Sankyo Advances Enhertu for High-Risk Breast Cancer: New Hope After Neoadjuvant Therapy
Daiichi Sankyo has taken a significant step forward in expanding treatment options for early-stage breast cancer patients by submitting a supplemental New Drug Application (sNDA)
Psoriatic Arthritis
FDA Approves BMS’s Sotyktu for Psoriatic Arthritis
As reported in a recent article by Pharmaceutical Technology, Bristol Myers Squibb (BMS) has secured US Food and Drug Administration (FDA) approval for Sotyktu (deucravacitinib)
Brain Cancer
Learning Her Again: A Mother’s Understanding of Baseline
Editor’s Note: Patient Worthy is honored to share this caregiver story with you, originally written by Aisling Melton, Parent Champion at Courageous Parents Network. In
Primary Biliary Cholangitis
Accelerated Pathway Opens for GSK’s Pruritus Solution in China’s Rare Liver Disease Population
GlaxoSmithKline has achieved a significant regulatory milestone as China’s National Medical Products Administration granted priority review status to linerixibat, an investigational treatment for cholestatic pruritus
Breast Cancer
FDA Grants Priority Review to Enhertu for HER2‑Positive Early Breast Cancer With Residual Disease
As reported on PharmaBiz, the US Food and Drug Administration (FDA) has accepted and granted Priority Review to AstraZeneca and Daiichi Sankyo’s supplemental Biologics License
Amyloidosis
Two Intellia Clinical Trials Released by the FDA
Two of Intellia Therapeutics’ clinical trials that had been on hold since October 2025 have now been released by the FDA. According to The New
Hunter Syndrome
Gene Therapy Setback: REGENXBIO’s RGX-121 Faces Regulatory Hurdles in Ultra-Rare Disease Treatment
REGENXBIO encountered a significant regulatory obstacle when the FDA issued a complete response letter regarding its biologics license application for RGX-121, an investigational gene therapy
Parkinson's Disease
Serina Therapeutics Begins First-in-Patient Dosing in Phase 1b Trial of SER‑252 for Advanced Parkinson’s Disease
As reported on RTT News, Serina Therapeutics has initiated patient dosing in its Phase 1b registrational study of SER‑252, marking a significant milestone for the
Phenylketonuria
New Gene Editing Program Aims to Address Root Cause of PKU
For families affected by phenylketonuria (PKU), newborn screening can mean the difference between a healthy future and lifelong complications. PKU is a rare inherited metabolic
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Thank you Arelis for sharing your journey with vertical sleeve gastrectomy (VSG).
"I’m Arelis—most people call me Reli. I had VSG on June 23rd, 2020.
As a first-generation Dominican American, food has always been a big part of my culture and my life. By the time I got to college, I had tried just about everything to lose weight—gyms, bootcamps, pills, programs, even Dominican home remedies.
By 2018, I was around 275 pounds. I had been diagnosed with PCOS, experienced a few miscarriages, was dealing with chronic back pain, and had high cholesterol. That’s when I realized it was time to make a real change—for me.
Choosing weight loss surgery has truly changed my life—not just physically, but mentally and emotionally as well. I’ve maintained a 135-pound weight loss, which has helped me better manage my back pain and improve my cholesterol without needing medication.
More importantly, this journey has given me a completely new mindset, meaningful connections, and a version of myself I’m really proud of.
I didn’t just lose weight—I found myself."
#StoryShare #VSG #WeightLossSurgery #PatientWorthy #SleeveGastrectomy #WeightLossJourney
On World Autism Day, we celebrate minds that experience the world in beautifully different ways. Autism reminds us that there is no single right way to think, communicate, or connect. When we choose acceptance, practice understanding, and honor uniqueness, we create a world where everyone belongs just as they are. #autism #autismawareness #autismacceptance #inclusionmatters #WorldAutismAwarenessDay #CelebrateDifferences #PatientWorthy
Bridging Nutrition Science and Patient Care: ANA and Jazz Pharmaceuticals Launch Cardiovascular Health Initiative bit.ly/4uRSSZ6 Read now at PatientWorthy.com
#PatientWorthy #narcoplepsy #idiopathichypersomnia #JazzPharmaceuticals #americannutritionassociation #ana
