
MASH (formerly NASH) Patient Stories Needed
Your story has the power to educate, motivate, and make a real difference in the lives of others. We are looking for patients with Metabolic
Your story has the power to educate, motivate, and make a real difference in the lives of others. We are looking for patients with Metabolic
NS Pharma, Inc., a subsidiary of Nippon Shinyaku Co., Ltd., has received a significant regulatory boost for its experimental treatment targeting Duchenne muscular dystrophy (DMD).
Immuneering’s midstage pancreatic deep cyclic MEK protein inhibitor, (DCI), almost doubled the standard overall survival. It is a deep cycle inhibitor that targets key pathways
Editor’s Note: Patient Worthy is honored to share this story from our friends at Elephants & Tea. To see the article in its original form,
A new analysis has uncovered stark differences in the rates of breast anaplastic large cell lymphoma (ALCL), a rare cancer often linked to breast implants,
A recent preprint reported by medRxiv explores the complex relationship between genetic mutations and clinical presentation in Colombian patients with congenital adrenal hyperplasia (CAH) due
Editor’s Note: This article was translated into English from Spanish; there may be inconsistencies or minor errors. Sports and the fight against Dravet syndrome will
Alera Bio, a Chicago-based biotech company dedicated to rare neurological diseases, has announced a significant breakthrough in the quest to treat MCT-8 deficiency, otherwise known
A recent study by UCLA researchers of in-home murders of children twelve and under revealed that according to the National Violent Death Reporting System and
Editor’s Note: This opinion piece was originally written by Kim Higbee. The opinions expressed in this article may not be a reflection of Patient Worthy,
When Ashley Rowland’s daughter, Aubrie, was diagnosed with a rare mitochondrial disease called AARS2-related leukoencephalopathy before her first birthday, Ashley’s world changed forever. Seven years
Rare cancers, defined by their low incidence, collectively constitute nearly a quarter of all cancer diagnoses in the US and Europe, and represent a significant
In the shadows of his weight struggles, Sean Mulroney’s journey began at the staggering weight of 687 pounds in 2016. It was a weight that
A major new synthesis of research has confirmed that people living with antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV) face a markedly increased risk of developing
Editor’s Note: Patient Worthy is proud to share this article from our friends at Glanzmann’s Research Foundation. To see the article in its original form,
Recent research has brought to light striking genetic differences in chronic lymphocytic leukemia (CLL) among African American (AA) patients, suggesting that their disease may follow
Misfolded proteins found in motor neurons are the cause of muscle weakness and paralysis. People with Amyotrophic Lateral Sclerosis (ALS) generally live two to four
A recent study published in Clinical Lymphoma, Myeloma, and Leukemia offers new hope for older adults with myelofibrosis (MF), suggesting that allogeneic hematopoietic stem cell
Alkermes’ Alixorexton Shows Promise in Narcolepsy Type 1: Vibrance-1 Phase 2 Results to Be Unveiled at World Sleep 2025 bit.ly/48oo6OT Read now at PatientWorthy.com
#PatientWorthy #Narcolepsy #ClinicalTrials
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11 Foods for a Stronger Liver: What to Eat and Why It Matters bit.ly/4onMzse Read now at PatientWorthy.com
#PatientWorthy #LiverHealth #liver Diet
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Narcolepsy is more than just feeling tired. it’s a complex neurological disorder that affects sleep-wake cycles and daily life. There are two types: Type 1 Narcolepsy includes cataplexy, a sudden loss of muscle tone often triggered by emotions, and is linked to low levels of hypocretin, a brain chemical that regulates wakefulness. Type 2 Narcolepsy, on the other hand, does not involve cataplexy and typically has normal hypocretin levels, but still causes overwhelming daytime sleepiness and disrupted nighttime sleep. Both types deserve greater understanding and support. Awareness leads to better diagnosis, treatment, and compassion for those living with this invisible condition. To learn more about narcolepsy visit our website at patientworthy.com
To share your journey, click the link below
bit.ly/4dV7gru
#NarcolepsyAwareness #Type1Narcolepsy #Type2Narcolepsy #SleepDisorders #InvisibleIllness #PatientCenteredCare
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