The U.S. Food and Drug Administration (FDA) has approved Yartemlea (narsoplimab‑wuug), marking the first authorized therapy for hematopoietic stem cell transplant‑associated thrombotic microangiopathy (TA‑TMA) in
Young cancer patients with advanced Hodgkin lymphoma now have access to a significantly more effective treatment option that dramatically reduces their need for radiation therapy
As reported by Technology, a major evidence synthesis published in The BMJ has delivered the clearest picture to date of which therapies offer the strongest
Editor’s Note: Patient Worthy is honored to bring you this article, originally written by Kelsey Stanczyk, and shared with us by our friends at the
IgA nephropathy represents one of the most pressing kidney health challenges facing young adults worldwide. This progressive kidney disease develops when the immune system malfunctions,
As reported on PharmaBiz, AstraZeneca’s phase III LATIFY trial has fallen short of its primary objective, with the combination of the ATR inhibitor ceralasertib and
As reported on InsidePrecisionMedicine, a new gene therapy aimed directly at the cells responsible for myelination is showing unprecedented promise for children with Canavan disease,
Prostate cancer doesn’t affect all men equally. Medical researchers have long known that men with African ancestry experience significantly higher rates and more severe outcomes
As reported by The Pharma Letter, the UK Medicines and Healthcare products Regulatory Agency (MHRA) has granted a new indication for argenx’s Vyvgart (efgartigimod alfa),
Editor’s Note: Patient Worthy is proud to share this story from the Courageous Parents Network, originally written by Kelsey Stanczyk. When I first became a
For decades, doctors have prescribed stimulant medications like Ritalin and Adderall to millions of children with ADHD, operating under the assumption that these drugs directly
I’ve learned something brutal over the last few weeks: Most people cannot tolerate the reality of a child nearly dying. So they dilute it. They
As reported on Forbes, a class of drugs first introduced to combat HIV is now demonstrating unexpected promise for patients with rare genetic and mitochondrial
Takeda Pharmaceutical Company has announced breakthrough results from Phase 3 trials of zasocitinib (TAK-279), an innovative oral treatment for moderate-to-severe plaque psoriasis that offers patients
As reported on FierceBioTech, Biohaven closed out the holiday period with disappointing news: its investigational Kv7.2/7.3 potassium‑channel modulator, BHV‑7000, did not demonstrate efficacy in a
Editor’s Note: Patient Worthy is proud to share this story from our friends at Elephants & Tea. To see the story in its original format,
Menopause-related insomnia affects approximately one in four women during the menopausal transition, yet it remains significantly underdiagnosed and undertreated. A new analysis published in Maturitas
As reported by NewsWise, new clinical study led by investigators at the University of North Carolina at Chapel Hill is offering rare hope for families
Obesity is more than a number on a scale—it’s a complex health condition that deserves understanding, proper testing, and personalized care. From accurate diagnosis to effective management and treatment, every step matters. Join us in raising awareness, breaking the stigma, and empowering individuals to access the care and support they deserve. If you have a story to share, click here: bit.ly/4dV7gru
#Obesity #ShareYourStory #PatientWorthy
During Rare Disease Month, Patient Worthy is honored to share a story from Narah @we.are.rare.2023 who has been diagnosed with Fabry Disease.
“I am Narah, originally from Brazil and living in Florida for the past 17 years. I was diagnosed with Fabry disease after living with symptoms since childhood. For years, my symptoms were misunderstood or overlooked. As my primary doctor once told me, “we are looking for rice and beans...and you are a zebra.” That moment captured the reality of living with a rare disease. When your condition doesn’t fit the usual pattern, it often takes much longer to be seen, heard, and diagnosed. Today, I use my voice to raise awareness about Fabry disease and the importance of recognizing rare diseases earlier because rare should never mean invisible.”
#RareDiseaseMonth #RareDisease #RareButNotAlone #WeCareAboutRare #ShareYourStripes #ShareYourStory #PatientWorthy #FabryDisease
Feeding Tube Awareness Week is about visibility, understanding, and respect. Feeding tubes are not a last resort or a failure—they’re a medical tool that provides nourishment, strength, and life. Behind every tube is a person deserving of dignity, patience, and compassion. #FeedingTubeAwarenessWeek #ShareYourStory #PatientWorthy
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
