Elevar Therapeutics has achieved a significant regulatory milestone with the US Food and Drug Administration’s acceptance of a resubmitted New Drug Application for rivoceranib in
Sharing My Stripes 🦓 This Rare Disease Month, I’m honored to share my journey living as someone with a rare disease and what Rare Disease
Editor’s Note: Patient Worthy is honored to share part 9 of 10 of Elena Genik’s blog documenting her experiences with Graves disease and thyroid eye
When patients and families face a life-or-death disease, bureaucracy often feels like the enemy. Yet in early February 2026, the FDA delivered something rare: a
Hi! My name is Tessa, and I have a rare disease called Acromegaly. My journey started in 2015 when we discovered I had a 9x10x12
Editor’s Note: Patient Worthy is pleased to share this article, submitted to us by George Simpson, who volunteers for the CMT Research Foundation. There are
Primary biliary cholangitis (PBC) represents a chronic, progressive autoimmune liver disease characterized by the destruction of small bile ducts, leading to cholestasis and potentially fatal
Editor’s Note: The above photograph is credited to Patient Voice. “Ringing the bell” is an enduring image associated with cancer survivorship. It represents victory, celebration
Editor’s Note: Patient Worthy is honored to share part 6 of 10 of Elena Genik’s series of blog posts detailing her journey with Graves disease and thyroid eye
Otsuka has launched an ambitious awareness initiative designed to fundamentally shift how healthcare professionals understand and approach attention-deficit/hyperactivity disorder (ADHD). As reported by FiercePharma.com, the
When my son was eight months old, he had already been hospitalized more times than I can count for infections that seemed far too severe
It took two new cases of the deadly Nipah virus to remind people in West Bengal, India of the 1998 outbreak that killed over one
Takeda Pharmaceutical has reached a significant milestone in the development of oveporexton (TAK-861), with the US Food and Drug Administration officially accepting and granting Priority
As reported on MedicalXpress, the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion for several therapies this
Editor’s Note: Patient Worthy is proud to share part 7 of 10 of Elena Genik’s blog series, detailing her experiences with Graves disease and thyroid
As reported on the Manila Times, Aucta Pharmaceuticals has officially introduced PYQUVI™ (deflazacort) oral suspension 22.75 mg/mL, marking the company’s entry into the U.S. commercial
CureDuchenne is hosting several free events in 2026 to support families living with Duchenne and Becker muscular dystrophy. These events, called CureDuchenne CARES, will take
Twelve‑month, real‑world data from a large U.S. registry suggest that faricimab provides effective, durable, and safe treatment for retinal vein occlusion (RVO), reinforcing findings from
🌟 March is Developmental Disabilities Awareness Month! 🌟
This month, we celebrate the incredible strengths, stories, and contributions of people with developmental disabilities. 💙🧡
It is also a powerful reminder that inclusion is not just a value; it is a practice. When communities remove barriers, create opportunities, and champion accessibility, everyone thrives.
Let’s use March to:
✨ Amplify voices and lived experiences
✨ Challenge stigma and outdated assumptions
✨ Advocate for inclusion in schools, workplaces, and communities
✨ Celebrate the diversity and talent within the disability community
Together, we can build a world where everyone is welcomed, supported, and empowered.
#DDAM #InclusionMatters #DevelopmentalDisabilitiesAwarenessMonth #PatientWorthy
Potocki-Lupski syndrome reminds us that development looks different for everyone. With compassion, early support, and opportunity, individuals with PTLS can build meaningful and rewarding lives #PTLS #SupportRareDiseases #PatientWorthy 💚 ❇️
Living with Huntington's disease doesn't mean losing control. Discover how management strategies and treatments can help alleviate symptoms and improve quality of life. From therapies to medications, learn how to take charge. Click the link below to share your story with us! bit.ly/3VuxFDV #HD #chronicillness #PatientWorthy
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