The biotech sector witnessed significant momentum as four clinical-stage companies announced compelling data across muscular dystrophy, immunology, and obesity treatment areas, triggering substantial stock market
As reported by MedicalXpress, Researchers have uncovered a surprising immune function in specialized intestinal cells that may reshape our understanding of gut health and autoimmune
Genentech announced landmark clinical trial results demonstrating that giredestrant, an investigational selective estrogen receptor degrader (SERD), significantly outperforms standard endocrine therapy in treating early-stage ER-positive
Madrid, December 3, 2025 – The research laboratory of the Dravet Syndrome Foundation was one of the initiatives awarded 3,000 Euros in the 11th edition
A rare and life-threatening kidney disease affecting young adults and children finally has an effective and approved therapy due to the pioneering and leadership of
A team of doctors at NYU Langone transplanted a pig kidney into a brain-dead patient and reversed its rejection twice during the 61-day study. Currently,
As reported on BioPharmaDive, new clinical trial data presented at the American Society of Hematology (ASH) annual meeting suggests that an early treatment regimen combining
Key Insight: As reported by Healio, metabolic dysfunction-associated steatotic liver disease (MASLD) is not exclusive to individuals with obesity. New research presented at The Liver
There may be several reasons that HCC cancer of the liver cannot be removed. It may be due to the size of the tumor, or
Parabilis Medicines has achieved a significant milestone in cancer drug development, receiving FDA Fast Track designation for FOG-001, a groundbreaking first-in-class therapy targeting desmoid tumors.
Breaking a system into small independent and interchangeable modules that can perform certain functions is called modularity. For many years the KRAS oncogene proved to
As reported on MedicalXpress, esearchers at the Children’s Hospital of Philadelphia (CHOP) and the University of Pennsylvania are pioneering a new approach to treating rare
In a significant development for neurodegenerative disease treatment, BioPharma Dive reports that AC Immune has unveiled compelling evidence that its novel immunological strategy may fundamentally
An experimental cancer vaccine from the Johns Hopkins Kimmel Cancer Center and the Bloomberg~Kimmel Institute for Cancer Immunotherapy has delivered encouraging results in a phase
Chiesi Group has entered an exclusive licensing agreement with Aliada Therapeutics, a subsidiary of AbbVie, to develop therapies that can cross the blood-brain barrier (BBB)
As reported on Healio, new findings presented at The Liver Meeting highlight the potential of resmetirom (Rezdiffra, Madrigal Pharmaceuticals) in managing metabolic dysfunction-associated steatohepatitis (MASH)
Researchers at the University of Southampton have uncovered a hidden culprit in blood cancer, a unique sugar molecule that disguises aggressive lymphoma cells and renders
A new artificial intelligence model, popEVE, could accelerate diagnoses for rare, single-variant genetic diseases by scoring how likely each genetic change in a patient’s genome
January is Thyroid Health Awareness Month!
Your thyroid is a small gland with a big job! It helps regulate metabolism, energy levels, and overall well-being. Yet millions of people live with undiagnosed thyroid conditions, often experiencing symptoms like fatigue, weight changes, and mood fluctuations without knowing the cause. This month, let’s shine a light on thyroid health by encouraging regular check-ups, learning the signs, and sharing resources. Early detection can make a life-changing difference. Together, we can raise awareness and empower others to take charge of their health. 💙 #ThyroidAwareness #HealthMatters #RareDiseaseAdvocacy #PatientWorthy
From Cancer Treatment to Childhood Health: How Foresee's Injectable Drug Addresses a Rare Pediatric Challenge bit.ly/3N713zt- Read now at PatientWorthy.com
#PatientWorthy #centralprecociouspuberty #camcevi
For #FactFriday, we're highlighting Thyroid Eye Disease—an autoimmune condition that affects the eyes and can impact quality of life. Learn these important facts about TED and help spread awareness! #thyroideyedisease #TED #PatientWorthy
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