Crohn's disease
Fighting for Himself and Others: Wojciech’s Battle Against Crohn’s Disease and More
I am sharing my journey to give a voice to patients who suffer from extreme poly-pathology and are often left behind by the medical system.
Epidermolysis Bullosa Care Enters a New Era With Gene-Targeted and Wound-Healing Therapies
- May 29, 2026
Biogen–Denali Parkinson’s Therapy Falters in Mid-Stage Trial, Shifting Focus to Targeted Subgroups
Caplyta Gains FDA Approval for Schizophrenia Relapse Prevention with Significant Clinical Benefit
HPV Vaccination Linked to Significant Reduction in Cancer Risk Among Males
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THE LATEST FROM PATIENT WORTHY
Colorectal cancer
Pre-Surgery Immunotherapy Rewrites Colorectal Cancer Survival: Zero Recurrence at Three Years
For decades, colorectal cancer treatment has followed the same playbook: surgeons remove the tumor, then patients endure months of chemotherapy hoping to catch any remaining
Parkinson's Disease
AskBio Advances Parkinson’s Gene Therapy Program With Commercial-Scale Manufacturing
AskBio Inc., a gene therapy company operating independently under Bayer AG, has taken a key step forward in the development of its investigational Parkinson’s disease
Lupus
Dismissal, Derision, and Misdiagnosis: Olga’s Lupus Story
Editor’s Note: This story was originally published on Linked-In and is shared with permission by Olga Lucia Torres. In college, a clinician told me I
Lupus
Breaking Ground: New Targeted Lupus Treatment Enters Critical Phase 3 Testing
Enpatoran offers hope for millions suffering from lupus skin manifestations Pharmaceutical company Merck KGaA has announced a significant milestone in lupus treatment research. As reported
Obesity
Vanda Initiates Thetis Trial to Address GLP‑1–Related Vomiting
As reported on PharmaBiz, Vanda Pharmaceuticals has launched a new clinical trial, known as Thetis, to evaluate whether its neurokinin‑1 (NK‑1) receptor antagonist Nereus (tradipitant)
Pancreatic Cancer
After Losing His Mother to Pancreatic Neuroendocrine Tumors, Michael Fitzpatrick Is Now a 26-Year Survivor of the Same Condition
Editor’s Note: Patient Worthy is honored to present this article, shared with us by our friends at the Seena Magowitz Foundation. When doctors diagnosed Michael
Epidermolysis Bullosa
Ireland Embraces Hope: Revolutionary EB Gel Treatment Now Available Through HSE
A major breakthrough for the 300 Irish patients living with butterfly skin. For the first time in Ireland, patients battling epidermolysis bullosa, a rare and
Rare Disease
Two Mothers. One Trial. Two Different Outcomes: A Mother’s Day Reflection from Clinical Research
Editor’s Note: Patient Worthy is honored to share this story submitted to us by Regina Portnoy, a clinical researcher with over 20 years of experience.
Osteosarcoma
The Timeless Passages of My Mind and Soul
Editor’s Note: Patient Worthy is honored to share this patient story from our friends at Elephants & Tea. To see the story in its original
Rare Disease
Topical Curcumin Gel Shows Promise for Knee Osteoarthritis Pain in Early Clinical Trial
As shared on drugs.com, Vascarta Inc. has reported encouraging results from a Phase 1b clinical study evaluating its investigational topical/transdermal curcumin gel, VAS-101, for the
Generalized arterial calcification of infancy-1 (GACI1)
Sir’Savion’s Story
Editor’s Note: Patient Worthy is honored to share this article from our friends at the Brighter Hope Foundation. To see the article in its original
Ovarian Cancer
Labcorp Brings Breakthrough Diagnostic to Identify Platinum-Resistant Ovarian Cancer Patients
Labcorp announced the nationwide availability of Agilent Technologies’ PD-L1 IHC 22C3 pharmDx, the only FDA-approved companion diagnostic designed to identify patients with platinum-resistant ovarian cancer
Pancreatic Cancer
Daraxonrasib Delivers Landmark Survival Gains in Previously Treated Metastatic Pancreatic Cancer
As reported on drugs.com, Revolution Medicines has reported practice-changing efficacy results from a pivotal Phase 3 trial evaluating daraxonrasib in patients with metastatic pancreatic ductal
Primary Biliary Cholangitis
The PBCers Conference
This, year the PCBers will meet in Indianapolis, Indiana. They will be celebrating 30 years as a community, as well as celebrating a much brighter
Autoimmune hemolytic anemia
FDA Priority Review Accelerates Path for IMAAVY as First Treatment for Warm Autoimmune Hemolytic Anemia
Johnson & Johnson announced that the U.S. Food and Drug Administration (FDA) has granted Priority Review to IMAAVY® (nipocalimab-aahu), marking a significant milestone as the
Atopic dermatitis
Enveda’s Oral Candidate ENV-294 Shows Early Promise in Atopic Dermatitis
As reported on Business Wire, Enveda, a clinical-stage biotechnology company focused on discovering novel small-molecule medicines, has reported encouraging results from a Phase 1b study
Lupus
Insights into Gazyva as a Treatment for Lupus/SLE
A recent article from Inside Precision Medicine states: For decades, systemic lupus erythematosus (SLE) has resisted tidy solutions, a shapeshifting autoimmune disease that crosses into
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Mission: Cure chronic pancretitis
NCBRS Worldwide FoundationWe are calling for nominations to receive a £5,000 Benefact Group Movement for Good Award to help us towards our research and annual gatherings.
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