On February 13th, the U.S. FDA announced the approval of Symdeko, a novel combination of two previously used agents to treat cystic fibrosis (CF). Symdeko combines a drug that has been…
I lost my fiancé, Ashley “Bea” Briggs, due to complications from cystic fibrosis a little over a year ago in early 2017. We met early in the summer of 2015…
According to a story from BBC, Health ministers are starting to put pressure on Vertex Pharmaceuticals to lower the cost of its treatment Orkambi. The drug is indicated for the…
A young woman in Cambridgeshire received a trailblazing double lung transplant. Now she’s started a Kickstarter campaign to publish a book to help other people in similar situations, their friends…
An online patient survey has found that 96% of pulmonary fibrosis patients, and 93% of cystic fibrosis patients, support being able to monitor their lung function at home between visits…
A drug being developed to treat cystic fibrosis has just been granted Fast Track Designation by the US Food and Drug Administration (FDA), reports PR Newswire. This shows that previous…
Researchers at Northern Arizona University (NAU) are using microbial sequencing to better understand the causes of airway inflammatory diseases, including chronic rhinosinutsitis and cystic fibrosis. They hope that by studying…
A potential treatment of pulmonary infection for patients with cystic fibrosis (CF) and chronic obstructive pulmonary disease (COPD) has just been awarded U.S. patent status, reports Medicalxpress. Dr Daniel Hassett, a researcher…
According to a story from cbc.ca, Lilia Zaharieva, a woman from British Columbia with cystic fibrosis, was recently given long term access to a treatment that is currently saving her…
Vanderbilt University Medical Center researchers have discovered a new method of searching existing electronic medical records to help identify genetic diseases in larger populations, reported EurekAlert!. Many people who may…
According to a story from Financial Buzz, the pharmaceutical company Proteostasis Therapeutics recently announced that the company's experimental treatment PTI-428 was granted Orphan Drug Designation by the FDA. PTI-428 is…
For most people, sharing a bathroom with a stranger represents an unpleasant thought. It’s just sort of uncomfortable. For 14-year-old Holly Aspinall, however, it's a real danger. Holly suffers from…
Ben Mudge might closely resemble Chris Hemsworth's Thor with his good looks and shredded physique, but he's also a real life superhero to many, reports Business Insider. Ben has defied…
According to a story from All4Women, Nicole Capper, crowned Mrs. South Africa, is planning to summit Mt. Everest, the highest mountain peak on the planet, in order to help promote…
According to a story from Science Daily, patients with cystic fibrosis have to deal with higher concentrations of bacteria in the lungs within their first few years of life, which…
Corbus Pharmaceuticals has received the Development Award presented by the Cystic Fibrosis Foundation, along with $25 million to support an upcoming study, reports Financial Buzz. Corbus plans to test out…
According to a story from the Vancouver Sun, five rare disease drugs just received coverage in British Columbia. The funding comes from savings accumulated thanks to a recent agreement that…
A new digital platform has been created with hopes to assist cystic fibrosis (CF) patients at the comfort of their own homes, limiting hospital visits, reports Evening Standard. This new…
Elizabeth Jane Allen, known best as "Betty", will be honored this week for the wonderful woman she was and the lasting impact she has made on the cystic fibrosis community, reports…
According to a story from BioPortfolio, the pharmaceutical company Synspira announced the results of a study for poly-N glucosamine (PAAG) as a potential treatment for MRSA, a widespread antibiotic resistant…
The Australian government has announced that almost that new treatments worth $300 million are being added to the Pharmaceutical Benefits Scheme. This program provides subsidized medical treatments to citizens of…
Tiffany and Caleb isn't your typical engaged couple. They are passionately in love and excited for their wedding, but their romance could literally end any moment. NBC 5 Chicago reported…
According to an article from One News Page, the biopharmaceutical company Motif Bio was generously presented with an award from the Cystic Fibrosis Foundation. The award came in the form…
Orla Tinsley, an Irish-born journalist living in New York, has had to put her work in hold and is now on life support at New York-Presbyterian Hospital. As a sufferer…
Earlier this month, researchers at the University of Montreal found an encouraging way to improve treatments to cystic fibrosis patients. They discovered key molecules, known as quorum-sensing inhibitors, could be…
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