CIRM Awards $12 Million Grant for Clinical Study of Gene Therapy for Cystinosis Patients
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CIRM Awards $12 Million Grant for Clinical Study of Gene Therapy for Cystinosis Patients

According to a press release from the California Institute for Regenerative Medicine (CIRM), the Institute's governing body has approved a grant of nearly $12 million to University of California, San…

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Diagnostic Timeline for Lysosomal Storage Disorders like Fabry Disease Significantly Reduced in South Africa

The Problem Lysosomal storage disorders (LSDs) affect approximately one out of every 7,000 people. There are around 50 different types of LSDs. These include Fabry disease, Batten disease, Gaucher disease,…

Continue Reading Diagnostic Timeline for Lysosomal Storage Disorders like Fabry Disease Significantly Reduced in South Africa
An Honest Interview on Living with Cystinosis, Kidney Transplants, and Cancer
Lyme is contracted by ticks, which means nature and hiking-lovers are at a higher risk.

An Honest Interview on Living with Cystinosis, Kidney Transplants, and Cancer

Many persons living with rare disease require a transplant of certain organs. Though this is not a cure for the rare disease Cystinosis, a kidney transplant is often required once the disease…

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Dad Plans to Promote Awareness About Cystinosis, His Daughter’s Rare Disease as Father’s Day Approaches
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Dad Plans to Promote Awareness About Cystinosis, His Daughter’s Rare Disease as Father’s Day Approaches

According to a story from CBS News, Clay Emerson, from New Jersey, is hoping to use Father's Day in order to raise awareness about his three year old daughter's rare…

Continue Reading Dad Plans to Promote Awareness About Cystinosis, His Daughter’s Rare Disease as Father’s Day Approaches