According to a story from news-medical.net, the Genomics England company, which was founded as a subsidiary of the UK's Department of Health and Social Care in 2013, announced recently that…
According to a story from the International Business Times, a total of eleven new medications are about to become a whole lot cheaper for Australia's citizens. Slated to be added…
According to a story from cbc.ca, Lilia Zaharieva, a woman from British Columbia with cystic fibrosis, was recently given long term access to a treatment that is currently saving her…
According to a story from cnbc.com, the pharmaceutical company Novartis recently announced that their anticancer drug Tasigna has been approved for the treatment of patients one year or older that…
According to a story from Financial Content, the drug company Arena Pharmaceuticals recently announced that its data results from Phase II clinical trials has been positive. The trial in question…
According to a story from financialbuzz.com, the biotechnology company BIOPHYTIS has submitted documentation for orphan drug designation from the European Medicines Agency (EMA). This designation will be for Sarconeos, a…
According to a story from globenewswire.com, the pharmaceutical company Amicus Therapeutics recently announced that its drug Galafold had received official approval for public use in Japan. Galafold is the first…
According to a story from pressreleasepoint.com, a group of scientists at the University of Birmingham have a received funding to the tune of £3 million in order to conduct research on…
According to a story from Digital Trends, Google has recently added an option for wheelchair-accessible routes on its widely popular navigation tool, Google Maps. This option will make the app…
You wouldn't know by looking at 5-year-old Grayson Ledbetter that he only had a few years of life left to live. According to The Washington Post, Grayson battles the rare,…
Erin Gard and her mother, Joanne Guthrie-Gard, already spent many years of their lives searching for an effective epilepsy medication for Erin. However, once they found it, they lost access…
According to a story from medscape.com, the 2018 budget recently signed by the president is going to feature some spending increases for health-related services. These changes have the potential to…
Anna Bridgeman, mother from Redbank Plains, luckily avoided death despite experiencing incredibly low kidney function, reported The Queensland Times. Anna had gone through much of her life without any serious…
Happy first week of spring, everybody! Spring has finally begun, at least in our hemisphere-- we're breaking out shorts, sunscreens, allergy medicines, and some new rare disease updates. This week,…
According to a story from webmd.com, diesel exhaust could increase the risk of developing amyotrophic lateral sclerosis, also known as Lou Gehrig disease. People who are exposed to diesel exhaust…
According to a story from People, parents Lester and Noreen Jessop from Utah recently discovered that all three of their children have a rare, life-threatening disease called pantothenate kinase-associated neurodegeneration. Their firstborn…
According to a story from engadget.com, the tech company AliveCor, known for its KardiaBand device for Apple Watch, is currently developing new capabilities for its innovative watch strap. Currently, the…
26-year-old Rebecca Smith's pregnancy was going as smooth as can be until she was 8-months pregnant, reported Hertfordshire Mercury. Rebecca discovered a lump on her neck and went in for…
According to a story from Xconomy National, some patient advocacy organizations are beginning to speak out about exorbitantly high drug prices despite the fact that many of them receive funding…
According to a story from guttmacher.org, the U.S. Department of Health and Human Services proposed a host of new regulations purported to enforce over 20 federal provisions related to "conscience…
According to a story from PR Newswire, the pharmaceutical companies Sanofi and and Regeneron Pharmaceuticals are implementing a plan to make Praluent injections more accessible and affordable for patients with…
The apparent goal behind the current Right to Try legislation is to create better access to life saving medication. Many people are excited about the possibilities such a bill could…
According to a story from pharmpro.com, the pharmaceutical company Abeona Therapeutics announced that it has been given Rare Pediatric Disease Designation for its ABO-202 program by the U.S. Food and…
According to a story from Financial Buzz, the pharmaceutical company Proteostasis Therapeutics recently announced that the company's experimental treatment PTI-428 was granted Orphan Drug Designation by the FDA. PTI-428 is…
Losing a child has to be one of the most heart-wrenching experiences a family can encounter, yet losing a child when it could have been prevented is even more devastating.…
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