In May 2023, the U.S. Food and Drug Administration (FDA) approved Vyjuvek, a gene therapy, for dystrophic epidermolysis bullosa (DEB). This treatment has brought support to numerous people living with…
As the world becomes increasingly technological, researchers and scientists are leveraging these advances for scientific improvement. Artificial intelligence (AI) is now being used to develop products, screen drug candidates,…
For the last few decades, there has been increased interest in understanding the effects of sleep (or lack of!) on our overall health. A recent study sought to understand the…
There is no doubt that artificial intelligence (AI) is going to change the future of healthcare. AI can be used in disease prediction, treatment, identification, diagnosis, and management. For example,…
Vision loss is a symptom associated with a number of disorders, one of which is Usher syndrome. Medical professionals have spent years trying to fully comprehend the underlying mechanisms of…
It's January -- do you know what that means? That's right - it's National Glaucoma Awareness Month! According to the Richmond Register, glaucoma diagnoses are rising on a national level.…
A recent article emphasized the importance of being educated about our eyes. As one of the most essential organs in the body, it’s important to know some key facts. Eye…
According to a recent article, a mother was able to see her baby daughter clearly after being diagnosed with the rare Stargardt disease. Stargardt Disease Stargardt disease is an inherited…
Sometimes, companies work together to develop the best therapeutic options for patients. According to Optical Prism, biopharmaceutical company reVision Therapeutics, Inc. and specialty pharmaceutical company Aequus Pharmaceuticals Inc. recently joined…
On July 14, 2021, biopharmaceutical company Alkeus Pharmaceuticals, Inc. ("Alkeus") shared via press release that its therapy ALK-001 (C20-D3-vitamin A) received Breakthrough Therapy designation from the FDA for the treatment…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
Recently, pharmaceutical company Alimera Sciences announced that the first patient was enrolled in the NEW DAY clinical trial to test ILUVIEN as a potential treatment for patients with diabetic macular…
Vision loss is a major symptom of Stargardt disease, so a main goal of treatments is to combat this loss. In order to test the effectiveness of these treatments, there…
As reported in Liverpool Echo; Faye was just 12 she began to have difficulty walking. She didn't realize it was her first encounter with the devastating disease that she had…
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