InformedDNA, Foundation Fighting Blindness Partnership Will Screen Patients for Usher Syndrome, RP Clinical Trials
source: pixabay.com

InformedDNA, Foundation Fighting Blindness Partnership Will Screen Patients for Usher Syndrome, RP Clinical Trials

ProQR Therapeutics is working to develop unique therapeutic solutions for genetic eye diseases. Currently, the company is evaluating its therapeutic candidate ultevursen within the Phase 2/3 Sirius and Celeste clinical trials; you can read…

Continue Reading InformedDNA, Foundation Fighting Blindness Partnership Will Screen Patients for Usher Syndrome, RP Clinical Trials
INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 2)
Daniel de Boer. Photo courtesy of: ProQR and FTI Consulting

INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 2)

If you would like to read the first part of this interview, please take a look at Part 1 here. In the first part of the interview, I spoke with…

Continue Reading INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 2)
INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 1)
Daniel de Boer. Photo courtesy of: ProQR and FTI Consulting

INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 1)

Clinical trials, drug development, and medical research have the potential to change the therapeutic landscape for patients with a wide variety of conditions. At ProQR, founder and CEO Daniel de…

Continue Reading INTERVIEW: How ProQR’s Sirius and Celeste Studies Could Change the Therapeutic Landscape for USH2A-Mediated RP and Usher Syndrome (Pt. 1)
Researchers Identify Underlying Mechanism and Possible Treatment of Usher Syndrome
source: pixabay.com

Researchers Identify Underlying Mechanism and Possible Treatment of Usher Syndrome

Vision loss is a symptom associated with a number of disorders, one of which is Usher syndrome. Medical professionals have spent years trying to fully comprehend the underlying mechanisms of…

Continue Reading Researchers Identify Underlying Mechanism and Possible Treatment of Usher Syndrome
Scotch Plains, NJ Names September 18 as Usher Syndrome Awareness Day
Skitterphoto / Pixabay

Scotch Plains, NJ Names September 18 as Usher Syndrome Awareness Day

At Patient Worthy, we love to see patient advocates and the impact that these advocates have on their communities. For example, brothers Ethan and Gavin Morrobel have worked tirelessly as…

Continue Reading Scotch Plains, NJ Names September 18 as Usher Syndrome Awareness Day

Doctors Are Unable to Diagnose Many Rare Diseases. Genome Sequencing is Changing That Scenario

After twenty-two years physician Huang Chun-jung finally learned why his vision and hearing have fallen to thirty percent of normalcy, thanks to research conducted by the National Health Research Institutes…

Continue Reading Doctors Are Unable to Diagnose Many Rare Diseases. Genome Sequencing is Changing That Scenario