Back in 2014, the FDA gave the green light for eight brand new drugs for orphan diseases. Among the pack was BioMarin Pharmaceutical's very own VimiZim. Weird name right? Well,…
You may have seen Sanele Junior Xaba in an ad for Adidas Original, posing in mythical depictions for European artists, or photographed nude, covered by only butterflies in the magazine Label.…
A simple facebook post has led to a life changing event for a young boy with CLOVES Syndrome. Keep reading to find out how, or follow the original story here.…
Bradley Lowery won the hearts of many as a football mascot. After an ongoing battle with neuroblastoma, he lost his life earlier this year. Neuroblastoma is a rare form of…
Press Release: Lend Your Voice to the Fight to Breathe Faced by the UK’s Cystic Fibrosis Community Cystic fibrosis families from around the UK have joined forces to release a…
Global Genes is one of the world's most prominent rare disease advocacy groups and early next year, they will host the second annual RARE in the SQUARE event. At this…
When you suffer with severe atopic dermatitis you can get pretty desperate to do anything to relieve the itch and other symptoms. So taking a bleach-bath is not out of…
Brielle Manning has been fighting through seizures for over a year, but the dust has settled and her family is now seeing some relief. Brielle suffers from an incredibly rare…
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