Nikki Oosthuizen gave her 16-year-old daughter, Kim, a kidney as she suffers from a rare kidney disease, yet only four days later the disease returned and destroyed her kidney function…
2017 was a challenging year for 10-year-old Zach Pickard, but at first glance of his smile and rolling laughter, you would never expect it. Zach is among 144 children in…
Cycle Pharmaceuticals shook hands with US-based firm, Aprecia Pharmaceuticals as they agreed to develop and commercialize treatments for rare diseases using the advanced technology of 3D printing, recently reported Cambridge…
Gene therapy has successfully made its presence known in the medical field this last year, reported ABC News. Dr. Francis Collins of the National Institutes of Health isn't afraid to…
A recent study has revealed a possible mechanism for the repair of nerves damaged by multiple sclerosis. Research at the University of California has found that gene expression in certain…
Organovo Holdings recently stated that its 3D bioprinted therapeutic liver tissue was granted orphan drug status by the Food and Drug Administration (FDA). Taylor Crouch, the company CEO, was excited…
A young boy suffering from a rare disease was faced with a bundle of surprises, including a surprise trip to Disney World, just in time for the holidays. The Burlington…
The world of rare disease is seeing a ray of sunshine with a viable partnership. Two powerhouses of patient advocacy are uniting together to bring about change, awareness and cure-searching.…
Poor mental focus may be a contributing to the paralysis that commonly occurs after a stroke, according to a new study. A person who has had a stroke, when the…
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
