A rare but serious disease caused by flesh-eating bacteria has been studied, and researchers have identified the mechanism by which it progresses. This has lead them towards potentially effective treatments…
According to a story from cafepharma.com, Akcea Therapeutics, Inc. recently announced that the FDA's Division of Metabolism and Endocrinology Products Advisory Committee voted to recommend approval of the therapy Waylivra…
According to a story from medicalxpress.com, a recent study from the University of Birmingham discovered that the progression of multiple sclerosis could be predicted by spinal fluid analysis. This could…
Janet Williams was prescribed Epilim for seizures while she was pregnant. Now her two sons, Lee and Phillip, who are both in their twenties, have health issues related to the…
A year after being approved as the first new treatment for amyotrophic lateral sclerosis (ALS) in 22 years, Radicava is altering the way physicians treat the illness, which is also known…
The family of Tessa Jowell, a UK politician who recently passed away from a brain tumour, have commended the government for their commitment to improving diagnostic and treatment services for…
According to a story from the Hereford Times, a combination of misdiagnosis and a critical mistake to forgo a simple blood test led to the tragic death of Callum Cartlidge.…
Whenever a rare disease family is in crisis, which happens all too frequently, the request for prayers goes out to others, knowing that the response will bring about comfort. Rare…
Dear UK businesses and decision makers within them, I know it’s mental health awareness week but for my benefit could you for just a couple of minutes focus on the…
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