According to Pulmonary Fibrosis News, a study with mice showed that a certain compound found in plants, parthenolide, is associated with a sizable reduction in lung fibrosis and the subsequent inflammatory…
An experimental gene therapy designed to treat Duchenne muscular dystrophy has produced exciting preliminary results in a Phase 1/2a clinical trial. Sarepta Therapeutics, the company behind the therapy’s development, announced…
An open-label extension of a Phase II study has shown that the experimental drug lenabasum is fairly safe and tolerable in patients who have diffuse cutaneous systemic sclerosis. The full…
According to a story from Newswise, a team of scientists and researchers have recently completed research that managed to reveal the genetic nature of the unusual rare disease neuromyelitis optica.…
According to a story from UK Healthcare, a team of researchers and scientists at UK Healthcare is preparing to start a clinical trial that will test a new therapy aimed…
Lisa Ray starred in the 2005 film Water. She also appeared in TV shows such as Endgame, Psych, and Top Chef Canada. Now, as an advocate for people with multiple…
The experimental gene therapy LentiGlobin for the treatment of severe sickle cell disease is being investigated in an ongoing Phase 1 clinical trial. Bluebird Bio, the company developing the therapy,…
Clinical data from a Phase 2 study of the experimental drug X4P-001-RD for the treatment of WHIM syndrome has been announced at the European Hematology Association’s 23rdCongress in Stockholm. The…
According to a story from BioPortfolio, the corporation Herantis Pharma Plc recently announced that its Phase 2 clinical trial measuring the effectiveness of Lymfactin, a gene therapy, in the treating…
According to a story from the Ottawa Sun, several hundred people participated in the annual ALS Walk on June 9th, in which people walk down the Sir John A. MacDonald…
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