9% Copyscape An investigational drug called CLR 131 has received Rare Pediatric Disease Designation from the US FDA for the treatment of Ewing’s sarcoma. The source press release can be…
According to a story from wday.com, Paisley Forsell was what you might call a bit of an adrenaline junkie. She likes to live a high energy, active lifestyle. She loves…
According to information provided by the National Hemophilia Foundation, people living with hemophilia now have the opportunity for a greater level of financial support. This new form of aid comes…
A research team led by scientists from the Beth Israel Deaconess Medical Center (BIDMC) have found that arsenic, in combination with the drug all-trans retinoic acid (ATRA), may have the potential…
According to a story from MD Magazine, the US Food and Drug Administration (FDA) has approved the medication migalastat, also known as Galafold, for the treatment of Fabry disease. This…
According to HSC News, researchers at the University of Southern California have engineered a device that may have a sizable impact on those with pediatric hydrocephalus. By troubleshooting the issues…
The award-winning actor Alan Alda has shared his diagnosis of Parkinson’s disease during an interview on the CBS This Morning show. The source video of the interview can be found here on…
A recently published study in the Journal of Biosciences and Medicines has concluded that orthoses may help to improve the gait and balance of patients with Charcot-Marie-Tooth disease. Orthoses are…
A recent study into Periodic Fever, Aphtous stomatitis, Pharyngitis and Adenitis (PFAPA) syndrome investigated the impact of the condition on children and found that is was associated with a reduction…
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