This Surgeon Preserved His Hand Function Thanks to New Amyloidosis Drug
sasint / Pixabay

This Surgeon Preserved His Hand Function Thanks to New Amyloidosis Drug

According to a story from the Irish Examiner, treatment with the recently approved drug patisiran helped a British surgeon named Carlos Heras-Palou save both his hands and his career. Patisiran…

Continue Reading This Surgeon Preserved His Hand Function Thanks to New Amyloidosis Drug

This Dad Climbed a Literal Mountain for His Daughter with Pompe Disease

The Malaysia Lysosomal Diseases Association (MLDA) was formed in 2011 by the hands of eight families. Their goal was to raise awareness and funds for those diagnosed with lysosomal storage…

Continue Reading This Dad Climbed a Literal Mountain for His Daughter with Pompe Disease
NZ Patient With Diffuse Large B Cell Lymphoma Fundraising to Travel to US For Treatment
Holgi / Pixabay

NZ Patient With Diffuse Large B Cell Lymphoma Fundraising to Travel to US For Treatment

According to a story from stuff.co.nz., Janelle Brunton-Rennie and Kurt Brunton were celebrating their third wedding anniversary this past January. Little did they know that the next day, their lives…

Continue Reading NZ Patient With Diffuse Large B Cell Lymphoma Fundraising to Travel to US For Treatment
Proof of Concept Data Released for Potential Primary Hyperoxaluria Treatment
jarmoluk / Pixabay

Proof of Concept Data Released for Potential Primary Hyperoxaluria Treatment

According to a story from BioPortfolio, the drug development company Dicerna Pharmaceuticals recently announced the release of proof of concept data in its Phase I trial testing the company's experimental…

Continue Reading Proof of Concept Data Released for Potential Primary Hyperoxaluria Treatment