Orphazyme Preps to File European Marketing Application for Experimental Niemann-Pick disease Type C Drug
stevepb / Pixabay

Orphazyme Preps to File European Marketing Application for Experimental Niemann-Pick disease Type C Drug

According to a press release from Danish biopharmaceutical company Orphazyme, the Company intents to proceed with a marketing authorisation application (MAA) for its experimental Niemann-Pick disease type C treatment arimoclomol.…

Continue Reading Orphazyme Preps to File European Marketing Application for Experimental Niemann-Pick disease Type C Drug
Development Progresses on a Possible Therapy for Idiopathic Pulmonary Fibrosis
source: pixabay.com

Development Progresses on a Possible Therapy for Idiopathic Pulmonary Fibrosis

According to a story from Market Screener, the drug developer Reviva Pharmaceuticals, Inc. recently announced that it has completed a recent meeting with officials from the US Food and Drug…

Continue Reading Development Progresses on a Possible Therapy for Idiopathic Pulmonary Fibrosis

Extremely Positive Results Announced from Interim Analysis of Phase 2 Clinical Trial for Hemochromatosis

Hereditary Hemochromatosis Hereditary hemochromatosis (HH) is a rare disease caused by hepcidin deficiency or hepcidin insensitivity. Hepcidin naturally regulates iron absorption/distribution in the body. Without hepcidin, HH patients suffer from…

Continue Reading Extremely Positive Results Announced from Interim Analysis of Phase 2 Clinical Trial for Hemochromatosis

The FDA is Reversing Course on Unapproved Products Sold by Stem Cell Manufacturers

  The FDA’s “untitled letter” to R3 Stem Cell (R3), based in Scottsdale Arizona, cautioned R3 that the product they are marketing is considered a drug. It must, therefore, be…

Continue Reading The FDA is Reversing Course on Unapproved Products Sold by Stem Cell Manufacturers
Rare Diseases and Abortion Bans: What is the Impact?
WilliamCho / Pixabay

Rare Diseases and Abortion Bans: What is the Impact?

With the advent of a majority conservative Supreme Court with the appointment of Brett Kavanaugh last year, several US states have recently passed laws that effectively ban abortions. Many of…

Continue Reading Rare Diseases and Abortion Bans: What is the Impact?
Think You Have Lyme Disease? Make Sure You Don’t Have One of These Other Diseases First
skeeze / Pixabay

Think You Have Lyme Disease? Make Sure You Don’t Have One of These Other Diseases First

According to a story from the Madison Area Lyme Support Group, one of the most difficult challenges about Lyme disease is getting a confirmed diagnosis. Testing for Lyme disease is…

Continue Reading Think You Have Lyme Disease? Make Sure You Don’t Have One of These Other Diseases First
Close Menu