Possible Treatment for WHIM Syndrome Earns Orphan Drug Designation in the EU
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Possible Treatment for WHIM Syndrome Earns Orphan Drug Designation in the EU

According to a story from home.suddenlink.net, the biopharmaceutical company X4 Pharmaceuticals recently announced that the European Commission has granted Orphan Drug designation to the company's lead investigational drug candidate, mavorixafor.…

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Researchers Discover “Testicular Cancer-Associated Paraneoplastic Encephalitis,” an Autoimmune Disease
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Researchers Discover “Testicular Cancer-Associated Paraneoplastic Encephalitis,” an Autoimmune Disease

According to a story from Cancer Health, a team of scientists affiliated with Mayo Clinic, UC San Francisco, and the Chan Zuckerburg Biohub have discovered a new rare, autoimmune disease…

Continue Reading Researchers Discover “Testicular Cancer-Associated Paraneoplastic Encephalitis,” an Autoimmune Disease
Researchers Continue Search for Role of Type-1 Interferon Pathway in Rheumatic Disease
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Researchers Continue Search for Role of Type-1 Interferon Pathway in Rheumatic Disease

According to a publication from the Rheumatologist, past studies have suggested that type 1 interferons may play a significant role in determining susceptibility to several classic connective tissue diseases. Although…

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Experimental Treatment for Neurofibromatosis Type 1 Earns Orphan Drug Designation in the EU
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Experimental Treatment for Neurofibromatosis Type 1 Earns Orphan Drug Designation in the EU

According to a story from BioPortfolio, the biopharmaceutical company SpringWorks Therapeutics, Inc., has recently announced that the European Commission has given the company's investigational drug candidate mirdametinib Orphan Drug designation.…

Continue Reading Experimental Treatment for Neurofibromatosis Type 1 Earns Orphan Drug Designation in the EU
Company Seeks to Treat Hunter Syndrome (MPS II) in China With New Drug Application
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Company Seeks to Treat Hunter Syndrome (MPS II) in China With New Drug Application

According to a story from BioSpace, the biopharmaceutical company CANBridge Pharmaceuticals announced that it has recently submitted a New Drug Application with China's National Medicinal Products Administration (NMPA) for its…

Continue Reading Company Seeks to Treat Hunter Syndrome (MPS II) in China With New Drug Application