The European Commission (EC) has granted the Orphan designation to Passage Bio for their Krabbe disease treatment, PBKR03. This adds another designation to the medication's list, as it has already…
Since the onset of the COVID-19 pandemic, the novel coronavirus has led to 130 million diagnoses worldwide, with an associated 2.84 million deaths. While doctors and researchers are diligently working…
Connor Dobyn's parents recognized that their son was missing important developmental delays early on. They brought their concern to the doctor, where Connor was diagnosed with autism. For the next…
Each year, researchers make advances in the medical field which assist with the identification, diagnosis, and treatment of patients with rare conditions. According to Genetic Engineering & Biotechnology News, one…
On April 2nd, NFL scouts made their way to Eugene, Oregon to check out some of college football's most talented players. They watched as athletes completed the vertical jump, 40-yard…
According to a recent report in Medical Xpress, over twenty studies have indicated escalating events of nonalcoholic fatty liver disease (NAFLD) in children worldwide. In the United States, NAFLD heads…
Lauren Peikoff’s painful and discouraging experience is unfortunately very common. According to an account reported in NBC’s Think section, Lauren, an associate producer of a national news program, manages…
According to a story from Markets Insider, the biopharmaceutical company CStone Pharmaceuticals has announced that China's National Medical Products Administration (NMPA) has approved avapritinib (marketed as Ayvakit) as a treatment…
The month of April is recognized as Sarcoidosis Awareness Month, a time for spreading awareness about sarcoidosis among the general public and the medical community. The Foundation for Sarcoidosis (FSR)…
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