If you’re anything like me, you enjoy a nice cup of tea in the morning - and maybe the afternoon. Okay, you’ve got me, probably at night as well. In…
Charlene Marshall was diagnosed with idiopathic pulmonary fibrosis (IPF) in 2016. The condition unfortunately has no cure. However, Charlene explains how grateful she is for the scientists that are investigating…
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
According to a news release from pharmaceutical company Citryll, the first healthy volunteer was dosed with CIT-013 in a Phase 1 clinical trial. Altogether, the drug is being developed to…
In the Phase 3 PANTHER clinical trial, also known as the Pevonedistat-3001 study, researchers were evaluating pevonedistat in conjunction with azacitidine for patients with acute myeloid leukemia (AML), myelodysplastic syndromes…
782 words (source) vs. 472 words (mine) - 1% match Some rare diseases or rare cancers are exceedingly difficult to treat. For example, for patients with early-stage cutaneous T-cell lymphoma…
327 words (source) vs. 385 words (mine) - 6% match Looking into the future, new forms of medical technology offer the opportunity to improve patient outcomes like never before. For…
September 7, 2021 will be recognized as World Duchenne Awareness Day. This day will be set aside in recognition of awareness surrounding Duchenne muscular dystrophy, a rare and debilitating genetic…
Nivolumab has recently received an additional indication for the treatment of urothelial carcinoma with a high risk for recurrence following radical resection, a form of bladder cancer. This decision came…
Clinical trial recruitment has always been challenging. It is especially challenging for therapies being tested for rare diseases, an already small population. Clinical trials for rare diseases are small out…
According to a story from Healio, recent research has suggested that giant cell arteritis, a rare immune-mediated disease, could be made worse from the use of checkpoint inhibitors, a class…
What’s a great way to spark an understanding of diversity and the complex and beautiful differences between different people? A children’s book! Children’s books are often designed to both tell…
On July 18, 2021, the World Health Organization (WHO) first reported two cases of yellow fever within the Democratic Republic of the Congo (DRC), shares Outbreak News Today. This rare…
For Bryson Ackermann of Pittsburgh, PA, baseball has always been his passion. Now 9 years old, Bryson was kept from his team for the last few years. According to KDKA…
In the United States, Orphan Drug designation is granted to drugs or biologics intended to treat rare or chronic illnesses. For the purpose of this designation, "rare illnesses" are defined…
A recent study conducted by researchers at the Broad Institute of MIT and Harvard University uncovered that a small group of cancer cells is responsible for recurrence. Considering that most…
Genetics play a huge role in health and disease development. Certain genetic mutations are associated with the development of specific conditions; for example, DMD gene mutations cause Duchenne muscular dystrophy.…
A recent study has uncovered just how many people with pulmonary fibrosis (PF) do not receive an immediate diagnosis. This study conducted in Europe was published in Frontiers of Medicine.…
According to Pharmaceutical Business Review, Abecma (idecabtagene vicleucel), a CAR T-cell therapy designed to treat patients with relapsed and refractory (R/R) multiple myeloma (MM), received conditional marketing authorization from the…
Clinical trials are often used to understand the safety, efficacy, and tolerability of specific treatments. Unfortunately, sometimes the drugs in these studies fail. According to Targeted Oncology, this occurred in…
Chimeric antigen receptor (CAR) T-cell therapy has proven to be a successful therapy for a number of conditions; however, we do not see the same success in follicular lymphoma and…
In the past, researchers have noted an association between neuroinflammation (inflammation of nervous system tissue) and Alzheimer’s disease. However, researchers often believed that neuroinflammation was more of a result of…
In the past, atrial fibrillation (AFib), the most commonly seen heart arrhythmia, was linked to chronic alcohol abuse or long-term alcohol consumption. However, a new study has shown that drinking…
In a story posted on msn.com, primary biliary cholangitis patient Cathy Mumford talks about why she feels it is important for patients living with a rare disease to participate in…
Written by Venus Loreto In 2011 and 2016 I lost two children who were both 2 days old. My baby boy who was born in 2011 had an onset of…
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