Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
Unfortunately, while a variety of treatment options exist for different conditions, many come with unwanted adverse reactions or side effects. However, this might soon change for patients with HER2 positive…
Drug development is important in creating new therapeutic options for patients with rare or chronic illnesses. One incentivizing program is the Orphan Drug program. Orphan Drug designation is granted to…
According to a recent press release from biopharmaceutical company NFlection Therapeutics, Inc. (“NFlection”), the FDA granted Orphan Drug designation to the company’s drug candidate NFX-179. Altogether, this treatment is designed…
On August 9, 2021, biopharmaceutical and RNAi therapeutics company Alnylam Pharmaceuticals, Inc. (“Alnylam”) shared that enrollment is now complete for the Phase 3 HELIOS-B clinical trial. During the trial, researchers…
In early August, via a press release, biotechnology company Athersys, Inc. shared that its Japanese partner, biotechnology company HEALIOS K.K. (“Healios”), recently released positive topline data from a medical study…
During clinical trials, the FDA may sometimes order a clinical hold. This order is often given to halt or suspend trial operations if the FDA believes that participants would…
In mid-August 2021, Parkinson's News Today reported that dosing was complete in a Phase 2a clinical trial. During the trial, researchers were evaluated ANVS401, an investigational compound for patients…
In early August 2021, the Icahn School of Medicine at Mount Sinai announced that it had received over $4M in grant funding from the National Cancer Institute (NCI). Mount…
In 1970, ketamine was used to treat injured soldiers on the tail end of the Vietnam War. The treatment helps relieve pain, but doesn't affect cardiac or respiratory function.…
Earlier this year, in June 2021, Guinea declared the end to the Ebola virus outbreak. However, just in case of a resurgence, some community health workers remained in Guinea…
In a news release from August 10, 2021, biotechnology company CohBar, Inc. shared that positive topline results were available from a Phase 1a/1b clinical trial evaluating CB4211 for patients…
It's no secret that drugs can sometimes be expensive, especially in regards to rare diseases or conditions. But how much would you guess a new drug is priced when…
As many people within the rare disease or chronic illness community know, having support is crucial and important. Being able to find support means that you find others with…
Currently, there are no treatments available for patients with hereditary ATTR amyloidosis (hATTR); most available therapies are designed to aid with symptom management. However, biotechnology company and RNA-targeted therapeutics leader…
One key facet of the healthcare system is working to improve patient outcomes and finding new, effective, and innovative lines of treatment. According to Hematology Advisor, a study showed that…
Clinical trials are important tools in determining the safety, efficacy, and tolerability of new therapeutic options. So it is important to learn when patients are dosed, what those dosages are,…
Grants offer helpful funding for medical research and scientific development. In case you missed it, researchers from Cleveland Clinic and Case Western Reserve University earned a $2.95M grant from…
On August 11, 2021, biopharmaceutical company Lantern Pharma, Inc. ("Lantern") shared the news that its small molecule drug candidate, LP-184 (hydroxyureamethylacylfulvene), received Orphan Drug designation from the FDA. This status…
Actress, dancer, and producer Christina Applegate is best known for her roles in Dead to Me, Married...with Children, Samantha Who?, and Up All Night. But now, she has revealed a new role: a member…
In a recent news release, biopharmaceutical company Retrotope shared that enrollment was complete in its Phase 2 clinical trial. During the trial, researchers will evaluate RT001, a first-in-class oral…
Unfortunately, recurrent ovarian cancer can be difficult to treat and often comes with a poor prognosis. However, according to a news release from biopharmaceutical company IMV Inc. ("IMV"), the company…
Typically, statins, or HMG-CoA reductase inhibitors, are prescribed to help reduce cholesterol levels in the blood. But could this class of drugs be repurposed for the treatment of another group…
When Ashley and Connor Henderson received news that they were pregnant, the family was overjoyed. After all, the Henderson family already had Liam and was hoping to add another child…
In an August 3rd news release, biopharmaceutical company RELIEF THERAPEUTICS Holding AG ("Relief") shared that its therapy RLF-100 (aviptadil) for sarcoidosis received Orphan Drug designation from the FDA. This…
For many patients, certain treatments can be expensive, invasive, or difficult to access. But it doesn't have to be this way. According to aHUS News, researchers are running two separate…
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