Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
Clinical trials have many endpoints - or milestones they are looking to achieve. These endpoints help signify the safety, efficacy, and tolerability of the treatments. In the Phase 3…
Sometimes, certain drugs may be approved in different countries and not in others. However, drug approval spanning multiple countries highlights the importance of getting drugs and treatments into the hands…
I don’t know about you, but I always get incredibly happy when I see stories about a community rallying to support one of its own members. For example, those in…
In 1992, Elsa Burgos and her husband, living in Puerto Rico at the time, welcomed a new addition to their lives: their daughter Nicole. The pair were thrilled to have…
Within the United States, uveitis is considered a leading reason for preventable blindness. As the uveitis progresses, patients may also develop complications such as uveitic glaucoma. But this can…
It's no secret that, over the last 1.5-2 years, COVID-19 has played a huge role in all of our lives. The novel SARS-CoV-2 coronavirus is present in over 200…
Sometimes, it can be difficult to spur drug development for rare or life-threatening diseases, considering the number of patients. To address this, and improve patient outcomes, the FDA developed the…
Unfortunately, clinical trials do not always proceed the way that drug developers - and patients - hope. For example, an ongoing Phase 1/2 clinical trial evaluating BMN 307, an investigational…
It's that time of the year again when mosquito-borne illnesses begin becoming more widespread. Thus, extra vigilance - and bug spray - is needed to ensure that you stay safe…
It's no secret that genetic mutations can alter the way our bodies - and bodily processes - work. For example, explains Charcot-Marie-Tooth News, GARS gene mutations stop protein production in ribosomes. These…
In the past, researchers believed that Valley Fever, a fungal disease caused by coccidioides fungus, was mostly found in the southwestern United States, as well as areas in Mexico and…
The 59th Annual European Society for Paediatric Endocrinology (ESPE) Meeting is taking place virtually from September 22-26, 2021. During the Meeting, researchers are discussing best practices and treatments, as well…
It's no secret that mosquitos can carry a variety of viruses and diseases: Zika virus, malaria, Chikungunya, and even the West Nile virus. However, Pennsylvania authorities recently detected another mosquito-borne…
Medical research drives a huge amount of our understanding around rare diseases. Recently, researchers from Brown University performed a study to deepen their understanding of a rare, X-linked genetic disorder…
Within the United States, Orphan Drug designation is granted by the FDA to facilitate the development and review of drugs or biologics intended to treat rare conditions. In this…
When you think of effective fundraisers, do you think of pickleball? Well, a Kansas community did just that. According to a video and transcript on KMBC News 9, his community…
From certain partnerships can emerge not only a better understanding of rare diseases but potential therapeutic options. As described by BioProcess International, a nonprofit organization called the Institute for Life…
Treatment for patients with GM2 Gangliosidosis - which consists of Tay-Sachs disease and Sandhoff disease - has often been symptomatic and supportive. However, a new therapy shows promise in benefiting…
Pregnancy can be stressful enough as is without the looming threat of COVID-19, a novel coronavirus which has played a huge role in our lives since the beginning of 2020.…
In the past, Exelixis' drug CABOMETYX (cabozantinib) has been approved for use in a variety of patients. For example, the treatment is approved for patients with renal cell carcinoma (RCC)…
An estimated 30% of patients with psoriasis go on to develop psoriatic arthritis (PsA), a type of inflammatory arthritis that can affect joints throughout the body. One particular spot which…
In the United States, Orphan Drug designation is granted to drugs or biologics intended to treat patients with rare or life-threatening illnesses, defined as those affecting under 200,000 people or…
In the United States, Fast Track designation is granted to help expedite drug development and review for serious, rare, or life-threatening conditions. To receive Fast Track designation, the treatment must…
Medical studies are crucial to understand the effect of diseases and treatments on patients. Over the last year and a half, the medical field has distinctly focused on COVID-19, a…
It’s no secret that physical fitness can, in many cases, improve our overall health and wellness. But could being physically fit also improve healthcare and treatment response? According to Medical…
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