Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
According to Multiple Sclerosis News Today, the European Commission (EC) recently approved PONVORY (ponesimod) for the treatment of adult patients with relapsing and remitting (R/R) or active secondary progressive (SP)…
In 2020, Dr. Paul Orchard, a pediatric blood and bone marrow transplant physician at M Health Fairview University of Minnesota Masonic Children’s Hospital, attended a medical conference that would change…
Currently, there are a number of potential treatment options for patients with multiple myeloma: immunomodulators, chemotherapy, HDAC inhibitors, steroids, and proteasome inhibitors. But according to Medical XPress, Peter Mac scientists…
Continue ReadingP300/CBP Inhibitors Show Promise for Multiple Myeloma
According to Medical XPress, researchers from the Cerebrovascular Surgery and Interventions Center at Boston Children's Hospital recently developed a new test that can benefit patients with Moyamoya disease. This rare…
In many cases, therapies for patients with rare disease are first tested or developed in either 2D cell cultures or in animal models, such as fruit flies, mice, or zebrafish.…
The amount of marijuana users in the world is steadily growing. While some people use marijuana to relax, others use medical cannabis for chronic pain, rare epilepsies, glaucoma, multiple sclerosis…
Continue ReadingSmoke Marijuana? Be Wary of Cannabinoid Hyperemesis Syndrome
Our livers play a huge role in our health. The liver regulates chemicals in the blood, filters toxins and wastes out of the body, breaks down fat, and even plays…
In a news release from early May 2021, biopharmaceutical company Bold Therapeutics ("Bold") shared that its treatment BOLD-100 received Orphan Drug designation for the treatment of patients with gastric…
Continue ReadingBOLD-100 for Gastric Cancer Granted Orphan Drug Designation
Nobody knew how much of an impact COVID-19 would have when it first appeared on the scene. Now, as of May 20, 2021, the novel coronavirus pandemic has led to…
Continue ReadingPatients with IBD Should Not Delay 2nd COVID-19 Vaccine
In a news release from May 19, 2021, startup biotechnology company GeneTx Biotherapeutics LLC ("GeneTx") and biopharmaceutical company Ultragenyx Pharmaceutical Inc. ("Ultragenyx") shared that the pair received Health Canada clearance…
Continue ReadingPatient Enrollment Begins in GTX-102 Trial for Angelman Syndrome
In a news release from May 18, 2021, biopharmaceutical company Catalyst Biosciences, Inc. ("Catalyst") shared that the first patient was dosed in the Phase 1/2 MAA-202 clinical trial. During…
Continue ReadingFirst Patient Dosed in MarzAA Study for Bleeding Disorders
According to corporate news shared on Street Insider, biopharmaceutical company BridgeBio Pharma, Inc. ("BridgeBio") is making ground with its AAV5 gene therapy, BBP-631. Recently, the FDA granted Fast Track designation…
Clinical trials are extremely beneficial in learning how new and burgeoning treatment options can benefit patients. At the same time, these trials also offer insight into where treatments may not…
Continue ReadingArimoclomol for ALS Fails to Meet Trial Endpoints
Sometimes, in the midst of performing medical research, researchers may discover an association between two conditions. According to Lambert Eaton News, University of Turin researchers recently determined a link between…
Unfortunately, the COVID-19 pandemic has sidelined many events, fundraisers, and other opportunities over the last 14 months. But the pandemic won't stop the Kidney Foundation of Canada from holding…
Continue ReadingVirtual Kidney March to Take Place Aug. 9 to Sept. 12
This year, the American Academy of Neurology (AAN) Annual Meeting took place virtually from April 17-22, 2021. During the meeting, a variety of stakeholders discussed new treatments and research…
Continue ReadingSoticlestat Reduced LGS and Dravet Associated Seizures
Currently, there is no cure for mesothelioma, and many treatment options revolve around surgery, radiation, or therapy. But could targeted treatment and precision oncology provide better patient outcomes? According to…
Continue Reading48 Genes Identified that Predict Mesothelioma Survival
From April 23 to 25, 2021, the American Academy of Dermatology (AAD) held their 2021 Virtual Meeting Experience (AAD VMX 2021). During the meeting, a variety of dermatology stakeholders discussed…
Continue ReadingAAD VMX 2021: Sofpironium Bromide Gel Beneficial for Primary Axillary Hyperhidrosis
Have you ever thought about whether measuring caffeine levels could give you insight into disease progression? Well according to Parkinson's News Today, researchers have discovered a potential link between…
For many patients with diffuse large B-cell lymphoma (DLBCL), one first-line treatment is rituximab, cyclophosphamide, doxorubicin, vincristine, and prednisone (R-CHOP). However, even aggressive chemotherapy is not always enough for patients…
Continue ReadingFirst Patient Dosed in Trial Evaluating Tafasitamib, Lenalidomide, R-CHOP for DLBCL
Poly ADP ribose polymerase (PARP) inhibitors are targeted cancer therapies which block PARP, an enzyme. Normally, PARP plays a role in DNA repair. Thus, inhibiting PARP prevents cancer cells from…
Continue ReadingDNA Repair Gene Mutations Predict Rucaparib Response for Ovarian Cancer
Over the last 15~ months, the world has grappled with the impact of COVID-19, a novel coronavirus. Altogether, COVID-19 has led to over 156 million million cases with an associated…
There are two types of osteosarcoma, a rare bone cancer: localized or metastasized. If the cancer is localized, or in one area, the 5-year survival rate sits around 70-75%. However,…
Continue ReadingMifamurtide for Osteosarcoma Improves Survival Rates
19 seasons. 1,109 regular-season games. 35 playoff games. Multiple All-Star Games. This is the impressive resume of Tony Brown, a veteran referee for the National Basketball Association (NBA). Unfortunately, Brown…
Continue ReadingNBA Ref Tony Brown Diagnosed with Pancreatic Cancer, Will Miss Season
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