Experimental Limb-Girdle Muscular Dystrophy Drug May Have Path to Accelerated Approval
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Experimental Limb-Girdle Muscular Dystrophy Drug May Have Path to Accelerated Approval

According to a story from BioPharma Dive, the drug company BridgeBio has been working on the development of a new treatment for limb-girdle muscular dystrophy, a rare disease. At the…

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Rare Classroom: WHIM Syndrome
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Rare Classroom: WHIM Syndrome

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

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Experimental Metastatic Castration-Resistant Prostate Cancer Therapy Earns Fast Track Designation
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Experimental Metastatic Castration-Resistant Prostate Cancer Therapy Earns Fast Track Designation

According to a story from Cure Today, the biopharmaceutical company Ambrx Biopharma, Inc., recently announced that the US Food and Drug Administration (FDA) has given Fast Track designation to the…

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Researchers Use AI to Identify New Cystinosis Treatment Targets
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Researchers Use AI to Identify New Cystinosis Treatment Targets

According to a story from SciTech Daily, a team of researchers affiliated with the University of Zurich's ITINERARE University Research Priority Program recently collaborated with Insilico Medicine to conduct research…

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A New Treatment for Diffuse Large B-Cell Lymphoma Could be on its Way to EU Approval
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A New Treatment for Diffuse Large B-Cell Lymphoma Could be on its Way to EU Approval

According to a story from Market Screener, the drug company AbbVie recently announced that its investigational therapy epcoritamab has received a positive opinion from the European Union's Committee for Medicinal…

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Updated Phase 2 Trial Data Looks Promising for Experimental Alpha-1 Antitrypsin Deficiency Therapy
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Updated Phase 2 Trial Data Looks Promising for Experimental Alpha-1 Antitrypsin Deficiency Therapy

According to an a press release published on Business Wire, Arrowhead Pharmaceuticals Inc. recently presented updated phase 2 data at the 2023 European Association for the Study of the Liver…

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Pembrolizumab Combo Fails to Reach Endpoint in Gastroesophageal Junction Cancer Trial
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Pembrolizumab Combo Fails to Reach Endpoint in Gastroesophageal Junction Cancer Trial

According to a story from Healio, a phase 3 clinical trial evaluating pembrolizumab plus perioperative chemotherapy as a treatment for locally advanced and resectable gastric adenocarcinoma and gastroesophageal junction cancer…

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Study of the Week: Investigational Treatment Shows Promise for Treating Nonalcoholic Steatohepatitis
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Study of the Week: Investigational Treatment Shows Promise for Treating Nonalcoholic Steatohepatitis

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…

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These Clinical Trials Could be Game Changers in the Latter Half of 2023
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These Clinical Trials Could be Game Changers in the Latter Half of 2023

In a story from BioPharma Dive, a number of high-profile clinical trials are under way that could see conclusive results by the end of 2023. While some of these are…

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