According to a publication from Karolinska Institutet, a medical research university near Stockholm, Sweden, new research led by the University suggests that regulatory T cells have an especially important role…
According to a press release from Massachusetts-based biotech company Fulcrum Therapeutics, the company has successfully secured global commercialization rights of GlaxoSmithKline-developed experimental facioscapulohumeral muscular dystrophy (FSHD) drug losmapimod. Losmapimod, an…
According to a publication from the BBC, a novel new technology could help some with Parkinson's disease regain limited walking ability. However, unlike medical technology we often showcase on Patient…
According to a publication from Healio, recent breakthroughs in medical science have renewed hopes of finding a cure for the rare Cushing disease. Dr. Shlomo Melmed, dean and executive Vice…
According to an article from CW associate WBCB, Dutch startup Nori Health has started open enrollment in the six-week test of its eponymous experimental chatbot, Nori. Nori aims to help…
According to a press release from the American Academy of Neurology published by EurekAlert, new research published in Neurology further suggests that established spinal muscular atrophy (SMA) drug nusinersen could…
According to an article from Medical Xpress, an experimental chemical compound being developed by Oregon Health & Science University (OHSU) has proven effective in reversing simulated symptoms of multiple sclerosis…
According to a press release from biotechnology company Forbius (Formation Biologics Inc.), the first patient in the Company's phase 1b trial of experimental myelofibrosis (MF) drug AVID200 has successfully received…
According to a January article from The Shields Gazette, nearly 21% of cancer patients from South Tyneside in the UK were first diagnosed without any prior knowledge during emergency admissions…
An article at ASH Clinical News recently detailed some of the history of genetic testing for bleeding disorders like hemophilia or von Willebrand Disease. Although true genetic screening has only…
According to an article from Stat News, patients, doctors, and advocates around the country are starting to push more energetically for a repeal of a U.S. law that effectively bans…
Anna Landre is a sophomore at Georgetown University in Washington, D.C. It’s a good school, you’ve probably heard of it. On top of the normal stresses of her college life,…
According to a press release from British biopharmaceutical manufacturer Autolus Therapeutics, the American Food and Drug Administration (FDA) has granted the Company's experimental acute lymphoblastic leukemia (ALL) cell-based immunotherapy treatment…
According to a report from ArsTechnica, scientists believe that some people might have medicinal poop. What might sound like a bad punchline to a child’s joke is actually the result…
According to a publication from KYN24, the Food and Drug Administration recently approved mucopolysaccharidosis type VII (MPS VII) drug Mepsevii for marketing and administration to patients in the United States.…
According to a publication at BioPortfolio, Belgian researchers are developing an orally-administered antibody medication for patients living with gastrointestinal disorders. In most cases, antibodies are injected into the bloodstream for…
A recent publication from Charcot-Marie-Tooth News announced that this year, for the first time ever, the Muscular Dystrophy Association will be hosting its annual clinical conferences at the same event…
A press release from American biopharmaceutical company AMO Pharma, published by PR Newswire, detailed the recent completion of the Company's new congenital myotonic dystrophy type 1 (CDM1) symptom-evaluation scale. The…
According to a press release from American biotechnology company Intercept Pharmaceuticals, the company recently released additional data supporting its phase 3 clinical trial of obeticholic acid (OCA) in the treatment…
According to a press release from Inovio Pharmaceuticals, the American biotech company's experimental recurrent respiratory papillomatosis (RRP) drug INO-3106 showed promising results at the end of a pilot clinical study…
According to a publication from Multiple Sclerosis News Today, recent studies of mesenchymal stem cells (MSCs - adult stem cells) suggest that autologous transplant of stem cells could one day…
According to a publication from health website Stat, a new way of thinking about the price of drugs is taking root in Washington D.C. and beyond. "Value-based agreements" are a…
According to a publication from Neuroscience News, a team of researchers has managed to examine how amyotrophic lateral sclerosis (ALS) progresses on a cellular level for the first time. The…
In a recent video interview with Healio, Dr. David Rubin recapped some of his discussion at the 2019 Interdisciplinary Autoimmune Summit. At the summit, he and his colleagues spoke about…
According to a recent article from CBC News, two patients treated for cataracts at Moncton Hospital in New Brunswick this winter were later diagnosed with Creutzfeldt-Jakob disease. The prion disease…
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