According to a publication from EurekAlert, high-cholesterol patients, who do not take statins (a type of cholesterol-lowering medication often prescribed by doctors) due to adverse side effects may benefit from…
Though it may surprise you, according to an article from CURE magazine, there’s a lot that makes solid tumors in children different from solid tumors in adults. They can be…
According to a publication from Scleroderma News, the first patient in the study of experimental cutaneous systemic sclerosis (SSc) drug AVID200 has been enrolled in the ongoing phase 1b clinical…
According to a publication from CURE Magazine, in a phase 2 clinical trial nearly 50% of patients with a certain type of cholangiocarcinoma responded to a treatment comprised of two…
According to a publication Biospace, the American Food and Drug Administration has drafted a series of five new documents meant to better structure and organize future participation in cancer clinical…
According to a publication from Multiple Sclerosis News Today, German biotechnology company Immunic Therapeutics has successfully enrolled the first participant for its phase 2 clinical trial for experimental relapsing-remitting multiple…
According to a publication from Impact Lab, clinical testing for a new kind of Alzheimer's treatment is slated to begin at Weill Cornell Medicine (Cornell University's medical school) in Manhattan…
A recent publication from the Massachusetts Institute of Technology announced promising results from research into a novel new type of therapy called RNA interference (RNAi). RNAi could potentially be used…
According to a publication from McGill University and obtained via EurekAlert, a massive study of 1,280 individuals confirmed a strong, long-suspected connection between rapid eye movement (REM) sleep behaviour disorder…
Earlier this week, a press release from Alnylam Pharmaceuticals, Inc, announced the that the phase 3 study of their experimental acute hepatic porphyria drug Givosiran yielded positive results. According to the…
A publication from OncLive recently reported that the FDA has granted the experimental myelofibrosis drug Fedratinib a priority review designation, following Celgene Corporation's submission of a New Drug Application (NDA) to the…
A recent press release from the French biopharmaceutical company Inventiva announced that the Food and Drug Administration (FDA) had granted the company's experimental mucopolysaccharidosis VI (MPS VI) drug odiparcil rare…
According to a news wire from Sound Pharmaceuticals, the biotechnology company has completed patient enrollment for its Phase 2b clinical trial involving Meniere's disease. About Meniere's Disease Meniere's disease (MD)…
According to a publication from MarketWatch, many people living with cancer are going broke just trying to stay alive. Millennials seem to be particularly vulnerable to falling into a self-perpetuating…
This week, a publication from BioSpace announced that a second individual has been cleared of HIV in another astounding success for stem cell therapy. The individual known only as the…
According to a publication from ANCA Vasculitis News, a sizable number of people who do not have ANCA-associated vasculitis could falsely test positive due to the presence of the associated…
A press release put out last month by American pharmaceutical company Adverum Biotechnologies announced some of the long-term preclinical safety data collected about their experimental drug ADVM-022. The drug hopes…
A publication at Science Daily recently announced that findings from Children's Hospital of Philadelphia suggested that cysteamine bitartrate, already used for nephropathic cystinosis (a rare kidney disease), might potentially benefit patients…
According to a publication from SMA News Today, Scotland is now the latest country to make spinal muscular atrophy (SMA) drug Spinraza available to patients at low or no cost…
The Star Gazette recently reported that Alan Ramsay Evans, a 34-year-old man from Horseheads, New York, remains in the hospital after developing respiratory failure. Three decades ago, when he was…
According to a publication from BioSpace, the French biopharmaceutical company Sanofi has successfully secured FDA approval for their acquired thrombotic thrombocytopenic purpura (aTTP) drug Cablivi. This represents the first approved…
According to a publication from Genetic Obesity News, a new genetic mutation has been discovered in an Iranian family that has differing affects on early-onset obesity based on sex. Leptin,…
An article recently published by the Guardian shared the stories of three families affected by recent breakthroughs in gene therapy treatments. What is Gene Therapy? Gene therapy is an increasingly…
The Washington Post reported in December of last year that the 8-year-old Matadi Sela Petit had died during surgery in a Los Angeles hospital. The accident was caused by a…
Chronic inflammatory demyelinating polyneuropathy (CIDP) is a rare disease that affects the nervous system. It causes peripheral nerves and nerve roots (the sites where nerves are attached to the central…
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