Sam Nicholson was a small child. His mother, Erica, did not find this surprising. Erica is only about five feet tall. She weighs about 100 pounds. She describes all of…
Nitu is eleven years old. She lives in Shayestanagor in Habiganj (a region within Bangladesh). While most 11-year-old children are full of energy, Nitu must stay at home. Nitu lives…
Gaucher patients in New Zealand are facing a change. New Zealand’s Pharmaceutical Management Agency (PHARMAC) recently proposed a change in their supported Gaucher treatment from Cerezyme to Elelyso. The switch…
According to information provided by the National Hemophilia Foundation, people living with hemophilia now have the opportunity for a greater level of financial support. This new form of aid comes…
According to a report by EuroInvestor, biopharmaceutical company Novelion Therapeutics, Inc. was recently granted permission to market their drug MYALEPTA. Novelion intends MYALEPTA to function as a method of treating…
Diseases affecting the brain are often pose numerous difficulties in research. One such challenge is that animal models of the diseases never quite replicate the human reality. In mice, for…
According to a story by Mirror, the Rare Disease Centre at Birmingham Children’s Hospital is set to begin operations after a massive donation by readers of The Star Appeal. Readers…
According to a report by Science Daily, researchers recently discovered a disease in monkeys which imitates human Batten disease. Establishing the closest analog to the condition in humans, the version…
According to a Science Daily report, new research by a group in Liverpool recently uncovered a drug for the treatment of alkaptonuria. Researchers published the collaborative study in the journal…
According to PRNewswire, Beverly Hills and Frankfurt based INFUSIO donated $5,000 each of their patient’s Lyme disease treatment in May. Interest in the program was high. As a result, INFUSIO…
The Foltz family relates to a number of usual, happy family evenings. Some of them, however, include unnerving moments in which their son, Trevor, experienced multiple seizures. At first they…
Famous poetic thought suggests that "the eyes are the window to the soul." Doctors studying Wilson disease, however, may see the eyes as the window to a diagnosis. According to…
According to a report by The Herald Scotland Online, a landmark study recently reveled flight crew to be exposed to greater than average risk of thyroid cancer. Surprisingly, the results…
What could make a family in Lebanon travel all the way to UCLA? The answer is a unique stem cell gene therapy designed to combat SCID. The El Kerdi family…
According to a report by Evening Times, two new drugs targeting Huntington’s disease are on the way. Developed by Wave Life Sciences, the new drugs will soon undergo clinical trials…
Who couldn’t use a little extra money now and again? Better still, what if earning that money was as easy as a mouth swab? According to a report on Journal…
Pancreatic cancer is known to be dangerous because of its ability to spread. The most common areas the cancer will metastasize are the liver and lungs. In many cases, the…
Treatments for neurological diseases have been developing rapidly in the modern era. Despite the development of new medicines and therapeutic techniques for many conditions, no cure has been found for…
According to an article published on BioPortfolio, a charitable foundation known as The Assistance Fund recently began a program to assist with the medical costs of hemophilia. The Assistance Fund…
Ailani Banuelos is a 12-year-old with a dream. She not only wants to see the ocean but paddle in it. Living in Chicago made the dream fairly difficult. There simply…
Ashley Wibberly’s son Levi was born in September of 2013 and lived for just 20 months with Krabbe disease. Ashley couldn’t have seen it coming. Now, however, a new test…
What do Dave Winfield, Steve Garvey, and Don Baylor Jr. all have in common? Besides all being big names in major league baseball, each of the famous athletes is contributing…
Filipa Vance, a woman who was diagnosed with osteosarcoma when she was 15, now celebrates 30 years of living post-diagnosis. Filipa is now cancer-free, but lives with many of the…
Pets brighten the lives of many people across the world. There are a variety of studies and pieces of evidence that point to pets improving the quality of life for…
As vice chair of the National Comprehensive Cancer Network ‘s (NCCN) committee on multiple myeloma, Dr. Natalie Callander helps to set guidelines for effective evaluation and treatment. The NCCN commonly…
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