A team of researchers from the University of North Carolina have been exploring an experimental method of delivering drugs to medulloblastoma that involves converting skin cells into stem cells that…
Tetra Bio-Pharma has submitted several Orphan Drug Designation applications to the US Food and Drug Administration. The applications are on behalf of cannabinoids for the treatment of multiple rare forms…
Senator John McCain passed away on Saturday, August 25th after his year-long battle with glioblastoma, a rare form of brain cancer. He was four days short of his 82nd birthday.…
According to a story from nbcnews.com, a recent map from the Centers for Disease Control and Prevention (CDC) indicates that children have the highest rates of cancer in the Northeast.…
The US FDA has awarded Breakthrough Therapy Designation to encorafenib (braftoviTM) combined with binimetinib (mektovi®) and cetuximab for use as an investigational (not FDA-approved) treatment of BRAFV600E–mutant metastatic colorectal cancer.…
A Biologics License Application for ElzonrisTM (also known as tagraxofusp and SL-401) for the treatment of blastic plasmacytoid dendritic cell neoplasm has been accepted for filing by the United States FDA.…
A research team led by scientists from the Beth Israel Deaconess Medical Center (BIDMC) have found that arsenic, in combination with the drug all-trans retinoic acid (ATRA), may have the potential…
Dr. David Scadden is a hematologist, oncologist, and Harvard medical school professor. He is also the author of a memoir for a book recalling his early medical schooling and career.…
We here at Patient Worthy shine a spotlight on rare diseases, but these disorders often get overlooked by much of the media. So anytime a rare disease is discussed out…
In a Washington Post article by Ben Guarino, new cancer treatments lasso the power of naturally occurring immune cells in the body. Researchers are looking into ways modify them to…
Filipa Vance, a woman who was diagnosed with osteosarcoma when she was 15, now celebrates 30 years of living post-diagnosis. Filipa is now cancer-free, but lives with many of the…
A patient with Waldenström Macroglobulinemia taking part in a clinical trial of the experimental drug CLR 131 for the treatment of B-cell hematologic cancers is reported to have achieved a…
According to a story from PR Newswire, the biopharmaceutical company AbbVie has recently announced that it has sent a supplemental New Drug Application to the FDA for its product venetoclax,…
Clovis Oncology, Inc. has announced that they have submitted an application to the European Medicines Agency (EMA). The application is to extend the drug Rubraca’s®(rucaparib) marketing authorisation to include maintenance…
A recent study, published here in the journal Nature Medicine and used as the source for this article, has found that certain kinds of cells may be useful for predicting…
Results from research into an experimental therapy called SL-401 for the treatment of patients with blastic plasmacytoid dendritic cell neoplasm have been shared at the Congress of the European Haematology…
A recently published study found that, out of the people studied, young cancer survivors were more likely to develop endocrine diseases than people who had no history of cancer. The…
Dewayne Johnson used to work as a school groundskeeper. Now, some days, he can’t manage to speak as a result of the cancer he lives with. Now, despite professional expectations…
The Orphan Drug Designation awarded to the drug dovitinib for treating adenoid cystic carcinoma has been transferred from Novartis to Oncology Venture. The full article can be found here, at…
July 13th is Gastrointestinal Stromal Tumors Awareness Day! And that "13" has extra relevance. 5,000 Americans are diagnosed with Gastrointestinal Stromal Tumors (GIST) each year. That’s 13 people diagnosed each day.…
According to a report from the University of Toledo, researchers developed a new molecule that could stop cancer in its tracks. The molecule, known as Sweet-P, works by targeting a…
According to a report by The Herald Scotland Online, a landmark study recently revealed that flight crews are exposed to greater risk than the average citizen. Surprisingly, the results have…
According to a report by NBC news, despite seemingly endless advancements in cancer treatment, many experts agree that chemotherapy is still a powerful and valid tool. In fact, many see…
The US FDA has awarded Orphan Drug Designation to the experimental drug CPI-613, for the treatment of Burkitt lymphoma. The full article can be read here, at Globe Newswire. About…
The Australian government will give $33 million to researchers to study rare cancers and rare diseases. The original article can be read here, at the Department of Health’s website. Background…
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