The Australian government has announced that almost that new treatments worth $300 million are being added to the Pharmaceutical Benefits Scheme. This program provides subsidized medical treatments to citizens of…
According to an article from the Chicago Tribune, many medical specialists are coming to the realization that the eligibility criteria for clinical trials should be reassessed. The problem is that…
A recent study conducted by researchers from National University of Singapore Medicine laboratory shows that eating vegetables, specifically broccoli, might prevent and even kill cancer cells that develop into colorectal…
Happy Friday Patient Worthians! Believe it or not, we've almost made it through the first month of 2018! This week, we have a story of a young girl with Sanfillipo…
Many cancer and blood specialists will not have encountered systemic mastocytosis. A new drug targets the underlying defect of the disease and will help put doctors on the lookout. Keep…
Out-of-pocket expenses for rare disease are astronomical, and the Ministry of Health (MOH), is taking time to find a more positive way to help benefit children and their families burdened…
A phase three clinical study is beginning for a new glioblastoma treatment. The new drug is called VAL-083 and is specially designed for treatment of late-stage glioblastoma. The study will…
The holidays are a little extra special for best friends Diana Caldon and Stephanie Smith. As optimistic cancer survivors, these two refuse to let holidays get away from them and…
The Alabama Rare Disease community has come together to host a special week in honor of the upcoming date February 28th, 2018, which is now the official International Rare Disease…
Ded Rranxburgaj, 48, currently living in Southgate, Michigan is being threatened with deportation, although his wife suffering from multiple sclerosis, reported MSN News. While fighting the deportation from every angle, Ded…
Patients suffering from the rare blood disease, hemophilia, deal with daily demands of their treatment. A recent study supports self-infusion for these patients, reported Harrison Daily Times. Self-infusion is when…
Reported by Strait Times, it was announced by Ministry of Health last week that there may be a potential fund developed to help children who suffer not only from a…
The gene therapy development company, AveXis, Incorporation, just announced that they will be expanding their clinical trial development program for the potential gene therapy treatment: AVXS-101, reported Globe News Wire.…
The Driscoll family is left devastated and shocked after receiving a letter from social services that states the government could be taking their daughter, who is suffering from Rett syndrome,…
Potentially good news arrived for patients with hereditary TTR amyloidosis, as the treatment drug inotersen received it's New Drug Application approval and will go into review by the U.S. Food…
According to an article from PRNewswire, the drug MVASI (biosimilar bevacizumab) was just granted marketing authorization by the European Commission. Developed by Amgen and Allergan, this treatment has been approved…
According to a story from Drug Discovery & Development, The European Commission announced its approval of marketing certification for OCREVUS, a treatment for relapsing types of Multiple Sclerosis (MS). The…
Tiffany and Caleb isn't your typical engaged couple. They are passionately in love and excited for their wedding, but their romance could literally end any moment. NBC 5 Chicago reported…
The Hempel family decided to take action against Vtesse and Sucampo Phamaceuticals who allegedly stole and sold their private information for profit, reported Forbes. The Hempel family has two twin…
The FDA, US Food and Drug Administration, unanimously agreed upon the recommendation for a new gene therapy that treats a rare form of blindness, reported ScienceNordic. Spark Therapeutics, a biotech…
There is potential for a new treatment for Duchenne muscular dystrophy. Duchenne muscular dystrophy (DMD) is a genetic disorder characterized by progressive muscle degeneration and weakness.To learn more about this…
TGIF, Patient Worthians! This week, kids went to bed wearing inside out pajamas and wishing for snow. Their wishes came true-- and so did the wishes of many rare disease…
According to an article from deccanchronicle.com, a common treatment for cancer, called carfilzomib, may increase the risk of hypertension, heart failure, and heart attacks in patients with multiple myeloma. Multiple…
According to a story from wepclinical.com, the Creating and Restoring Equal Access to Equivalent Samples Act, also known as the CREATES Act, was introduced in 2017 in order to accelerate…
On January 5th the NFL announced it will be contributing just over $16 million to research. The money will be split among three different programs that focus on neurodegenerative diseases.…
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
