Cyndi Strzynski was always a bubbly, active little girl. Even though she has been facing an immense challenge, she still tries to keep a smile on her face at all…
The Orphan Drug Act was passed with a goal in mind: to incentivize the development of therapeutics for orphan drugs. These drugs are used for patients with rare conditions,…
In August 2021, the U.S. Food and Drug Administration (FDA) approved Opdivo (nivolumab) for the adjuvant treatment of a rare form of cancer called urothelial carcinoma. More particularly, the drug…
If there’s one way that 11-year-old Cristian Muñoz would describe himself, it would be an athlete. Cristian has always been drawn to playing sports: the rigor, the competition, the connection…
Vivienne (“Vivi”) Horton has always been a bright and kind, albeit a bit shy and quiet, little girl. So her parents, Valerie and Terry, noticed when she wasn’t acting quite…
Stephanie Felix knew exactly what she wanted for her ninth birthday: to ring the bill at Beverly Knight Olson Children’s Hospital and signify that she was—officially!—cancer-free. When Stephanie was seven…
Each year, March 1 marks the start of Myeloma Action Month; during this month, the International Myeloma Foundation (IMF) encourages people to get involved, share stories, raise awareness and…
It’s no secret that diet and nutrition contribute greatly to our health. But how can dietary or nutritional changes help people who are living with certain illnesses? In the past,…
At first, 52-year-old Lisa Wolff thought that she was dealing with sciatic pain. The pain was sometimes dull, sometimes burning, but generally manageable. When the pain became too much to…
February marked National Cancer Prevention Month. This month is designed to better understand, and raise awareness of, preventable causes of cancer; cancer warning signs; and different ways that we can…
In March of 2021, twenty-eight-year-old Alix Burnard of Newbury, Berkshire UK had several Covid-19 tests due to a suspected infection. All three tests were negative, so she felt it…
In the United States, Orphan Drug designation is granted to drugs or biologics designed to treat, prevent, or diagnose rare conditions. “Rare” conditions refer to those affecting under 200,000…
Researchers have been grappling for years with the STAT5 protein as a tool to fight cancer. STAT5 is critical because it is partly responsible for the development and progression…
It can be difficult to spur interest in rare disease drug development. Forty years ago, the Orphan Drug Act passed as a way to incentivize drug development within this space.…
Currently, a glioblastoma multiforme (also known simply as glioblastoma or GBM) diagnosis comes with a poor prognosis. There is a 40% survival rate after one year which falls to…
There have been rising incidences of gastric cancer on a global scale. As a result, this cancer is now considered the fourth leading oncological cause of death worldwide. Gastric cancer…
Rare Pediatric Disease designation (RPDD) is granted by the U.S. Food and Drug Administration (FDA) to drugs or biologics in development for rare pediatric diseases. In the United States, “rare”…
Summer Wroniecki fell in love with dancing at a young age. At just 2.5 years old, she was already taking over the dance floor at Highland Dancing; her teachers were…
In the past, research has found connections between polycystic ovary syndrome (PCOS) and pancreatic cancer. For example, one study suggested that having PCOS could increase pancreatic cancer risk by…
In 2018, Libby Porter welcomed her first child into the world. Her family was thrilled, especially her father John, who was so excited to have a granddaughter. But things…
Researchers are closing in on cancer from every angle. Recently a team at the Colorado University (CU) Cancer Center has been focusing on p53, a common gene mutation found…
Early identification and diagnosis of cancers or rare conditions can significantly improve patient outcomes. For example, early ovarian cancer detection contributes to a better prognosis. Yet many women remain…
Scientists are always looking into new ways to advance treatments and improve patient outcomes, especially in disease states with high mortality rates. Currently, ovarian cancer is associated with a…
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
Pancreatic cancer unfortunately comes with a poor prognosis. It is the third leading cause of cancer-related deaths within the United States, though it is on track to become the second…
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