According to a story from Check Orphan, a group of scientists from Stanford have begun the process of developing a new test that could help patients with rare Fanconi anemia…
The US FDA has awarded Orphan Drug Designation to the experimental drug CPI-613, for the treatment of Burkitt lymphoma. The full article can be read here, at Globe Newswire. About…
Results from a Phase 3 trial of the medicine Lynparza (olaparib) for the treatment of advanced ovarian cancer in women with the BRCA-mutation have been announced as positive. The full…
According to a story by CBS News, an unsuspecting virus may become a potential treatment for brain cancer. The study showed that those who were given a genetically modified version…
According to a story from news-medical.net, a team of scientists from Delaware have recently released a study in the journal BMC Bioinformatics. In this study, the researchers found that patters…
According to a story from Reuters, the drug development company Merrimack Pharmaceuticals decided to abort its development of a new treatment for pancreatic cancer. The company chose to let go…
Amicus Therapeutics is developing a treatment for Pompe disease through its AT-GAA program. They have recently announced that they have met with regulators from the European Union and Germany who…
According to a story from globenewswire.com, the company Revive Therapeutics, which is dedicated to the development of treatments derived from cannabis and cannabinoids, recently announced that the FDA has decided…
According to a story from bioengineer.org, a group of scientists working at the Columbia University Irving Medical Center (CUIMC) have managed to develop a computational model that could potentially make highly…
According to a story from news-medical.net, a group of scientists from the Cincinnati Children's Cancer and Blood Diseases Institute have recently published a study in the journal Nature Cell Biology. This…
According to a story from triblive.com, a recent study demonstrated that Lyme disease cases increased at an "exponential" rate in the ten year period from 2003 to 2013. The area…
According to uk.reuters.com, the pharmaceutical company Sanofi is playing catch up to put itself ahead of the competition in developing the new cancer treatments. The French company didn't join in…
According to a story from today.com, Dr. David Fajgenbaum was first diagnosed with Castleman disease in 2010. His first encounter with the illness was terrifying. He was confined to the…
Understanding diseases and the mechanisms behind them is a crucial step towards developing treatment. Many times, however, it's difficult to accomplish this due to the rarity of a condition, or…
According to EurekAlert! Science News, researchers have pinpointed the certain immune cell that further inflames a heart attack. The immune cell, however, comes with good intentions of trying to fix…
According to Sleep Review, researchers at the University of North Carolina School of Medicine are studying DNA repair after damage from anti-cancer drugs as well as DNA repair and how…
In April, Congress approved the 2018 budget for the Department of Defense (DoD). Included in the DoD is a sizable portion dedicated to the investigation and development of new and…
According to a story from PR Newswire, the drug development company AIVITA Biomedical recently announced that the first patient in its Phase II clinical trial has been randomized. This is…
According to a story from GlobeNewswire, the biotech company Saniona has recently announced plans to begin the design and initiation of a Phase 2a clinical trial study of its investigational…
The drug Jakavi (ruxolitinib) is being investigated as a possible treatment for polycythemia vera (PV) and myelofibrosis. Results from studies into this were presented by Novartis at the 23rd Congress of…
A study that looked into what genetic factors influence medulloblastoma development has been published in Lancet Oncology. In it, researchers outline several genes they believe are linked to tumour formation…
According to a story from the National Hemophilia Foundation, a recent study examined the prevalence and impact of cardiovascular disease among hemophilia patients. It is widely assumed that people with…
Avedro has announced that patients are now being enrolled in a Phase III trial of an epithelium-on (epi-on) corneal collagen cross-linking procedure designed as a treatment for patients who have…
According to a story from GlobeNewsWire, the biopharmaceutical company Orphazyme A/S, which is committed to the development of treatments for patients that are living with rare diseases, has recently announced…
According to a story from Angelman Syndrome news, Angelman syndrome was recently given its own disease unique disease code: Q93.51. The new code will help make researching and tracking the…
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