What if there was a non-invasive option for patients who need surgery for Parkinson's disease? Something that involved no scalpels, no incision, no opening of the skull. A new study…
Two years ago, a seven-year-old boy from Syria was in dire condition. 80% of his skin was gone; his entire body covered in wounds and abrasions. He still had some…
When you hear your doctor say the C word, it feels like the whole world stops or launches into fast forward. I’ve spoken to many people who have had that…
It's became common knowledge to the healthcare community that the Zika virus was the source of microcephaly, a birth defect that causes baby's heads to develop much smaller than they…
At some point in your life, you might have taken a melatonin supplement from a bottle to get to sleep, or to get over jet-lag. Your body naturally produces melatonin…
Good news for mantle cell lymphoma patients! A new treatment called Calquence has just received approval from the U.S. Food and Drug Administration (FDA) for adults who suffer from this rare…
If you or someone you love have Friedreich's Ataxia, you know how badly we need an adequate treatment. Friedreich's Ataxia (FA) is a rare disorder, which results in neurological and…
Exciting updates have come out of Alnylam Pharmaceuticals. They just released data from one of their highly anticipated trials for its leading rare disease drug. It looks like it did…
Up until now, diagnosing ovarian cancer hasn't been so easy. Most of the time, it goes undiagnosed until it's already advanced. At that point, treatment is harder and less reliable.…
Dogs, with their pure hearts and boundless supply of affection, have made life better for humans for a long time. Dogs aren't just making people feel better by giving them…
An ongoing clinical trial called ARROW is making advances in the treatment of people with relapsed and refractory multiple myeloma. Patients who took a dose of a drug called Kyprolis (carfilzomib)…
If you or someone you love has Cushing Disease (often confused with the umbrella term, Cushing Syndrome), you've probably heard about microadenas. Microadenas are the tiny, benign tumors that develop…
A recent study, published in the Journal of Neurology, Neuroscience & Psychiatry, suggests that diets heavy in fat can increase the risk of relapse in children with multiple sclerosis (MS).…
Health scientists at the University of Leicester and University of Nottingham have heralded the discovery of a gene associated with lung fibrosis, such as idiopathic pulmonary fibrosis (IPF), as "a…
Presage Biosciences will be receiving its first grant from The Mark Foundation for Cancer Research, a brand new nonprofit organization. Presage developed something called CIVO, which is a drug-development platform.…
It's not every day that you hear about how nicotine may help lung disease. However, researchers at The Ohio State Wexner Medical Center are asking this question. They're testing whether…
Our bodies are complex and unpredictable machines. We can try our best to keep them healthy, but sometimes nature does its work, resulting in something we never could have planned…
You may have heard the buzz during the Zika outbreak in 2016. Many professionals suspected a relationship between the Zika virus and Guillain Barre Syndrome (GBS). Guillain Barre Syndrome is…
Do you ever find yourself tossing and turning in bed for several nights in a row? You might just have a lot on your mind or you might be suffering…
A team of researchers at the Cincinnati Children’s Hospital Medical Center has developed a method to test for Gaucher disease using dried blood samples - marking a big breakthrough for the Gaucher…
There's a new treatment for X-Linked Hypophosphatemia (XLH) that may be available in the not-so-distant future. XLH occurs when the kidneys process phosphate abnormally, leading to excess phosphate loss in…
There’s been a lot of talk in recent years about interdisciplinary projects. The idea is to put together people with different skillsets to address problems. The goal is for everyone…
It seems like copper is all the rage right now. A quick stop by any pharmacy shows copper-infused knee, ankle, wrist, and even back braces. Even the ironman of the…
Rare disease research can feel like an uphill battle. First of all, rare diseases have a harder time receiving funding. After that, it takes months or even years to have…
Sickle cell anemia results from a single mutation in the hemoglobin gene. The mutation creates a protein which has an atypical structure. This altered structure throws a wrench in the…
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