Great news for our friends in the the Gaucher community! The FDA and its counterpart across the pond, the European Medicines Agency (EMA), have outlined a new strategy to spur…
You heard that right, Starbucks lovers! According to two different studies - one from the US and one from Europe - drinking anywhere from one to three cups of coffee…
A recent Canadian study published in Seminars in Arthritis and Rheumatism announced findings that psoriatic arthritis disease activity showed trends of stabilizing and even improving during pregnancy. Psoriatic arthritis is…
Could crizanlizumab be the next treatment to prevent pain in those with sickle cell disease (SCD)? Is this the medicine you've been hoping for? Sickle cell disease (SCD) is an…
There's some new information available about Parkinson's disease, and researchers are really excited about it. Earlier this month, researchers found that visual system changes in recently diagnosed Parkinson's patients can…
A new study detailed in Nature, involving synthetically replicating certain cell activity has been hailed as a major breakthrough in developing therapies for many neurological disease – Parkinson’s chiefly among…
As reported in Nature (an international medical publication), research scientists have uncovered the atomic makeup of an important protein found in those with Alzheimer's Disease. This is being touted as a…
Has your healthcare provider ever talked to you about using an FDA-approved drug for an unapproved use (sometimes called an “off-label” use) to treat your disease or medical condition? It…
Have you ever tried to fit a square peg into a round hole? Short of taking a mallet to the peg, you’re not going to be successful in pushing it…
Nope, we're not joking! US SWAT teams (Special Weapons And Tactics, military weapons-equipped law enforcement teams) have been asked to step in to help with backlogged FDA applications to get experimental treatments designated as orphan…
Oh the joys of a 17-month-old toddler… I remember some of the typical behaviors of those days—the throwing heaving of everything and anything, the opening of the fridge a million…
3:15 a.m.? Are you kidding? Why am I awake and staring at a digital clock that says it’s 3:15 a.m.? Ever have a night like that? The more you get…
Allergan and Paratek Pharmaceuticals Inc. recently tested a drug called sarecycline for treatment of severe acne. The medicine is a tetracycline-derived antibiotic that is taken orally, and the best part…
Status epilepticus is a rare and sometimes fatal condition. About 60 percent of those with this super-refractory status epilepticus (SRSE) die, making it the most dangerous type of seizure. This…
According to the Salk Institute for Biological Studies, scientists have had a breakthrough in past efforts to develop a technique that can determine which proteins in a cell interact with…
The goal has always been to better manage and get a diagnosis earlier for inflammatory bowel diseases like ulcerative colitis and Crohn’s disease. The newest study at the University of…
Moms: The ultimate multitaskers. Whether they're stay-at-home moms or working mom, these strong ladies have a way of getting stuff done, come hell or high water - or a chronic…
Evidation Health’s goal is to make it easier for you to share your symptoms with the professionals who most need to know. Their program, in partnership with others, enables patients…
She was given 15 months if she didn't take action. Heather Von St. James was in the prime of her life. She was the co-owner of a salon/spa where she…
FAiRE is a clinical study program for children and young adults with Dravet syndrome. On their website, they provide information and an opportunity to get involved and be a study…
Si usted tiene narcolepsia, somnolencia diurna excesiva, y / o cataplexia, usted sabe lo difícil que puede ser para funcionar en el tiempo del "mundo real". Y mientras que los…
¿Quién sabía que el colonialismo podría ser una de las principales causas de las enfermedades raras ?! Al menos, ese es el caso de muchos quebequenses. La tirosinemia, que afecta…
If a treatment that would cure me or my child had to use dogs for testing, what would I do? That’s the question I had to ask when I saw…
By 2013, 17 states plus the territory of Washington, DC legalized or formed legislation around medical marijuana. A study by the University of Georgia suggests that this change caused about a…
A May 25, 2016 article from Pulmonary Fibrosis News reports that Italian researchers are making headway in determining if a person’s IPF is progressing or not (which is in the…
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