In a new article in the journal Science Advances, neuroscientists have found a specific mechanism that is responsible for the familial migraines. A type of brain cell called astrocytes have…
The Michael J. Fox Foundation has awarded a grant of $750,000 to researchers at the University of California, Los Angeles for their work to improve the Parkinson's disease registry in…
According to a story from Globe Newswire, the biopharmaceutical company Ovid Therapeutics and the University of Connecticut School of Medicine (UConn) have announced a new license agreement and research collaboration…
According to a recent article in the Myasthenia Gravis News, a team of doctors in Japan had been treating a man now aged sixty for multiple myeloma (MM). The…
According to a story from Myasthenia Gravis News, a recent case report describes a unique case of a 60 year old male multiple myeloma patient. After receiving treatment for the…
In a study published in BMC Pediatrics, researchers have found atypical hemolytic uremic syndrome (aHUS) and autoimmune thyroid disease may not only be a relatively common pair of rare diseases…
According to a story from Markets Insider, the biotechnology company NMD Pharma A/S has recently announced that the Dutch ethics committee has approved the company's plan for a combined phase…
According to a story from BioSpace, the biopharmaceutical company Bioniz Therapeutics, Inc., has recently announced the release of interim results from its phase 1/2 clinical trial. This trial is investigating…
According to Parkinson's News Today, an intestinal gel comprised of levodopa and carbidopa (LCIG) is able to lower the amount of time that Parkinson's patients spend in off episodes. These…
According to a story from Parkinson's News Today, a recent study describes the development of a new technology called computational mapping algorithms for neural drug delivery (COMMAND), which was designed…
According to a recent article in BioSpace, Biogen and Eisai have launched a new preclinical Phase III trial of BAN2401 to treat pre-clinical Alzheimer's disease. The new study follows…
Results of a Phase III study of CC-486 (oral form of azacitidine) showed a significant improvement for older patients who had been transfusion dependent. The results were favorable when…
Not much is known about the novel coronavirus; medical professionals are working to learn more every day. One of those things we are trying to understand is how this virus…
According to the American Cancer Society, there are approximately 1.7 million people in the U.S. diagnosed with cancer each year. About forty percent of these cases may be eligible…
According to a story from Fabry Disease News, a recent case study analyzed the situation of two cousins living with Fabry disease who were being treated with enzyme replacement therapy,…
According to a story from Parkinson's News Today, older patients with Parkinson's disease appear to have a higher than average rates of vision problems. These issues are also associated with…
According to a story from Physician's Weekly, while measuring the concentration of albumin (albuminuria) is widely considered the standard method for staging and screening for chronic kidney disease, a different…
Orphan drug designations are granted by the FDA to drugs and biologics that are developed for the treatment of rare diseases. According to a recent article in Biospace, Oncternal…
According to a recent press release from Albireo Pharma, the first participant has enrolled in the BOLD trial. The BOLD trial, which stands for Biliary atresia and the use…
According to a story from Parkinson's News Today, a recent study has found a new connection between two different features that appear in Parkinson's disease. These features are lysosomal dysfunction…
According to a story from Korea Biomedical Review, Seoul National University Hospital (SNUH) in South Korea has just announced recently that the process of recruiting patients for the National Bio…
Alpha-synuclein cause damage to mitochondria in patients with Parkinson's disease. These researchers wanted to see if they could see the membrane changes fostered by the alpha-synuclein. The examination of such…
While the world is waiting for a vaccine to prevent, mitigate, or cure COVID-19, the investigational drug remdesivir continues to show promise. The FDA recently gave it Emergency Use…
According to a story from Buzzfeed News, a recent test of an experimental COVID-19 vaccine being developed by Moderna Therapeutics demonstrated that it was able to produce antibodies in all…
The National Institutes of Health (NIH) recently published the results of studies based on a controversy that has remained unresolved for decades. The ISCHEMIA study is not only the…
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