According to an article from Righting Injustice, a recent study suggests that TNF inhibitors may increase the risk of rare cancers in pediatric patients. The study recommends that children that…
An article from SRN News is reporting that a lot of people with familial hypercholesterolemia are going through life without getting the treatments that could help them, such as statins.…
The EveryLife Foundation for Rare Diseases hosted a panel discussion on Right to Try Proposals, as part of their 2018 Legislative Program for Rare Disease Week on Capitol Hill. What…
A pre-clinical study investigating the effects of antioxidants on mitochondrial diseases has shown promising results, reports EurekAlert. Out of the seven antioxidants trialled, at least two (vitamin E and N-acetylcysteine)…
According to a story from triblive.com, Roger Ziegler has self-published a book about his family's experience with his son Noah. Noah is now a healthy 24-year-old, but there were multiple…
Two-year-old Jeremiah Nelson, born with a condition called spina bifida, has very limited mobility. However, a Michigan high school’s robotics team has decided to help the toddler get moving. Forgoing…
According to a story from the Lancashire Telegraph, Dr. John Timms, age 48, was recently diagnosed with a rare and deadly form of cancer: mesothelioma. Dr. Timms had committed much…
A gene therapy for Pompe disease is the first treatment of its kind to be clinically tested, reports Duke University. Researchers at the University, working with NCATS Therapeutics for Rare…
According to a story from biopharmadive.com, the Swiss pharmaceutical company Novartis has entered a partnership with researchers from the engineering and applied sciences school at Harvard University. The team will…
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