I lost my fiancé, Ashley “Bea” Briggs, due to complications from cystic fibrosis a little over a year ago in early 2017. We met early in the summer of 2015…
The prolonged legal battle over Alfie Evans, a toddler with a serious undiagnosed degenerative neurological disease, has reached a final verdict. The UK doctors currently caring for Alfie made the…
The US Food and Drug Administration (FDA) has just approved a new drug called Tavalisse™ to treat adults who have thrombocytopenia as a result of chronic immune thrombocytopenia (ITP), following…
The charity organisation Stand Up To Cancer (SU2C) has just announced that $10 million is going to be given to a team of researchers to fund their work to improve…
According to a story from edinburghnews.com, mother Karen Gray is about to seek access to cannabidiol oil for her five-year-old son, Murray, who has a rare type of epilepsy, Myoclonic Astatic…
According to a story from cbc.ca, Michelle Boich, 33, was facing the prospect of blindness if she is unable to get access to a crucial procedure that could treat her…
According to a story from the US News, Teresa Tostenrud-Hoff, a woman from Kansas, was only 22 years old when she was first diagnosed with primary sclerosing cholangitis. Since then,…
According to a story from BBC, Health ministers are starting to put pressure on Vertex Pharmaceuticals to lower the cost of its treatment Orkambi. The drug is indicated for the…
A press release from Aprea Theraputics has just announced the results of a Phase II clinical trial of the drug APR-246 in patients with myelodysplastic syndromes (a group of blood…
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