Preclinical data supporting the efficacy of GKT831 as a potential therapy for cholestatic fibrosis has just been published in the Journal of Hepatology. GKT831 GKT831 is both a NOX1 enzyme and…
Primary Sclerosing Cholangitis (PSC) and Autoimmune Hepatitis (AIH) are both rare and chronic liver diseases. They cause the bile ducts in the liver to become inflamed, resulting in severe liver damage.…
According to a story from finanzen.at, the biotechnology company Orbsen Therapeutics recently announced that its immunotherapy product ORBCEL-C is to be tested in a multi-site clinical trial called MERLIN that…
According to a story from northjersey.com, Adam Levitz's life was hanging in the balance just a few weeks ago. His liver, which had endured years of damage from the rare…
Nonalcoholic fatty liver disease (NAFLD) is a condition which causes fat to accumulate in the liver. Nonalcoholic steatohepatitis (NASH) is a severe form of the disease in which the patient also…
Pliant Therapeutics, Inc., a biotechnology company specializing in developing and commercializing treatments for fibrotic diseases, announced on January 3, 2019 through PRNewswire, that it has initiated a Phase 1 first-in-human…
According to a story from The Straits Times, Nicole Lim, who recently turned eighteen, learned that she had three different rare diseases when she was just thirteen years old. Getting…
The United States Food and Drug Administration has awarded twelve research grants worth a total of over $18 million for research into rare diseases. For more information about this news,…
At 16 years old, I was told I would need a liver transplant within ten years. Being told at any age that you will eventually need a liver transplant is…
According to a story from the US News, Teresa Tostenrud-Hoff, a woman from Kansas, was only 22 years old when she was first diagnosed with primary sclerosing cholangitis. Since then,…
According to NBC Right Now, the liver disease advocacy organization called The American Liver Foundation is launching an online platform designed to pair liver disease patients to clinical trials. The website,…
Kendall and Ava are not related by blood. They do, however, have one amazing thing in common- something that saved their lives and defeated autoimmune hepatitis. Keep reading, or follow…
This past Sunday, October 22nd, Steve Nugent, 53, crossed the finish line at the 42nd annual Marine Corps Marathon in Arlington, Virginia. A big group of the people who loved him…
When it comes to talking about families, there is a one-of-a-kind love between siblings. A form of admiration that only siblings can understand. At the end of the day, the…
In the post-Sputnik era, science was king—or so says Peter Agre as he recalls the golden age of science. But, when is it wise to dismiss the “ivory tower” mentality…
With a title about courage, you might think that I am going to write about facing fierce enemies, not running from brutal battles, and boldly standing on blood-stained ground in…
Does the name Ludwig van Beethoven ring a bell? It should. He was one of the greatest composers the world has ever seen. He also suffered from cirrhosis of the liver, infectious…
Primary sclerosing cholangitis, or PSC, is a chronic progressive disease that damages the bile ducts. And, if you didn't know, bile is a liquid that assists the body in the…
Nice guys finish last? Hardly. Especially if we’re talking about Vanessa Smith, a mother of six, and Peter Brouwer, a father living with primary sclerosing cholangitis (PSC) who needed a…
I can honestly say that I have never gone to a doctor’s appointment and remembered everything I wanted to ask—not even when the appointment is the most basic of physicals.…
Are you living with primary sclerosing cholangitis (PSC) and looking for a suggestion on dietary improvements? If so, there may be help navigating your options (I know there are many). I…
I can still remember the day when my overt trust in my doctor put my own health at risk. The ideal doctor and patient relationship never really developed. In retrospect,…
This stage of life is hard. I’m talking right now to all the moms who are probably somewhere between late 20’s to early 40’s. You likely have a kid or…
It's liver awareness month so remember that not all liver problems are related to alcohol use(for example, Primary Biliary Cholangitis). You may never drink a drop nor use any kind…
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