According to Scientific American, medication has long been the primary mode of treatment for those with Tourette syndrome. While these medications are effective in controlling the disease, the drawbacks…
According to a story from the Vancouver Sun, an extremely poisonous mushroom appears to contain some compounds that could be potentially effective in fighting cancer cells. A 2012 study demonstrated…
Denise Albert is a busy woman. She founded The MOMs media company. She enjoys music, concerts, and time with her boyfriend. She is also a happily divorced mom of two…
An ongoing Phase 3 clinical trial program is investigating the drug PXT3003 as an experimental treatment for Charcot-Marie-Tooth disease type 1A in adults. Pharnext SA says that they expect to…
The first patient has been enrolled onto a Phase 3 clinical trial investigating topical dermal reproxalap as a possible treatment for Sjögren-Larsson syndrome associated ichthyosis. The original article can be read…
We here at Patient Worthy shine a spotlight on rare diseases, but these disorders often get overlooked by much of the media. So anytime a rare disease is discussed out…
Researchers have investigated whether self-management electronic health (eHealth) interventions, such as text messaging, apps, and online cognitive-behavioural therapy, should be used to help patients with sickle cell disease self-manage the…
In a Washington Post article by Ben Guarino, new cancer treatments lasso the power of naturally occurring immune cells in the body. Researchers are looking into ways modify them to…
We recently read an article in Health News and Information that connected two conditions we weren't expecting to read about together. Scientists have discovered a potential link between rheumatoid arthritis.…
Kruz and his sister Paizlee are the only known siblings diagnosed with the ultra-rare condition Schimke Immuno-Osseous Dysplasia. Their parents, Jessica and Kyle, are doing everything they can to raise…
According to a story from globenewswire.com, the biopharmaceutical company Chiasma, Inc., recently announced that it has completed the enrollment of 135 patients for its Phase 3 clinical trial. This trial…
There’s good news coming out of MIT this week. In an article on Medical Xpress, new findings are coming out using CRISPR, a tool that is known for its ability…
Filipa Vance, a woman who was diagnosed with osteosarcoma when she was 15, now celebrates 30 years of living post-diagnosis. Filipa is now cancer-free, but lives with many of the…
The US Food and Drug Administration has awarded Orphan Drug Designation to the drug lenabasum as a treatment for dermatomyositis. The use of lenabasum for treating this condition, and others,…
Pets brighten the lives of many people across the world. There are a variety of studies and pieces of evidence that point to pets improving the quality of life for…
According to a story from Medical Xpress, a long term study testing a treatment for autosomal dominant polycystic kidney disease (ADPKD) has recently concluded. The treatment in question is a…
Patients living with PKU (phenylketonuria) have hope as researchers look into new drugs that may help the body break down phenylalanine. PKU is an genetic disease in which the body lacks…
I am a patient who has ITP and attended the PDSA conference this year in Cleveland, Ohio. I learned so many new things from other attendees and from the outstanding…
As vice chair of the National Comprehensive Cancer Network ‘s (NCCN) committee on multiple myeloma, Dr. Natalie Callander helps to set guidelines for effective evaluation and treatment. The NCCN commonly…
The organisations Takeda Pharmaceutical Company and Ovid Therapeutics are collaborating over the development of the experimental drug TAK-935/OV935 as a possible treatment for several rare epilepsy syndromes. Takeda has just…
Aidan Maddocks, 14, from Pietermaritzburg, was diagnosed with Biliary Atresia at birth, a childhood liver disease that only affects 1 in 10,000–15,000 live births. He was given a life expectancy…
Results from a Phase 2 clinical trial comparing the effects of baricitinib to a placebo in patients with systemic lupus erythematosus (SLE) have been announced. For more detailed information, please…
Researchers from the Newcastle University are investigating the personal and financial impacts of persistent facial pain on patients in the UK, and what can be done to improve medical…
According to a story from ABC News, Alexia Baier was four years old when she came down with strep throat, an infection caused by group A streptococcus bacteria. It is a…
According to a story from the Los Angeles Daily News, for children with debilitating rare illnesses like cerebral palsy, epilepsy, or muscular dystrophy, it can often take a long time…
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