A New Trial Testing Urine Analysis for Diagnosing Pulmonary Exacerbations in Cystic Fibrosis Begins
markusspiske / Pixabay

A New Trial Testing Urine Analysis for Diagnosing Pulmonary Exacerbations in Cystic Fibrosis Begins

According to a story from BioPortfolio, the company Mologic Ltd recently announced that its clinical trial to test HeadsUp, its urine-based diagnostic tool, is starting. The clinical trial will specifically…

Continue Reading A New Trial Testing Urine Analysis for Diagnosing Pulmonary Exacerbations in Cystic Fibrosis Begins
The First Patient Has Been Dosed on a Clinical Trial of an Investigational Gene Therapy for the Treatment of GSDIa
qimono / Pixabay

The First Patient Has Been Dosed on a Clinical Trial of an Investigational Gene Therapy for the Treatment of GSDIa

According to a source article that can be found here on Ultragenyx’s website, the first patient has been dosed in a trial of an investigational gene therapy called DTX401 that…

Continue Reading The First Patient Has Been Dosed on a Clinical Trial of an Investigational Gene Therapy for the Treatment of GSDIa
A Planned Study Will Investigate the Effects of an Investigational Drug in Children with Glioma
DarkoStojanovic / Pixabay

A Planned Study Will Investigate the Effects of an Investigational Drug in Children with Glioma

A study is planned to investigate the effects of the experimental drug PTC596 in children with recently diagnosed diffuse intrinsic pontine glioma and high-grade glioma. The study is made up…

Continue Reading A Planned Study Will Investigate the Effects of an Investigational Drug in Children with Glioma
The First Patient Has Been Treated in a Gene Therapy Study for MPS I
Thor_Deichmann / Pixabay

The First Patient Has Been Treated in a Gene Therapy Study for MPS I

The first patient has been treated in the Empowers study, a clinical trial investigating an experimental gene editing therapy for the treatment of mucopolysaccharidosis type I. The source article, which…

Continue Reading The First Patient Has Been Treated in a Gene Therapy Study for MPS I

After Struggling With Keratoconus, This Man Helps Connect Rare Patients With Clinical Trials

According to a story from Buffalo News, Brett Perla was graduating high school when he first starting to experience symptoms of a rare condition of the cornea called keratoconus. This…

Continue Reading After Struggling With Keratoconus, This Man Helps Connect Rare Patients With Clinical Trials
How Rising Drug Costs Affected a Family Living with Infantile Spasms
kschneider2991 / Pixabay

How Rising Drug Costs Affected a Family Living with Infantile Spasms

The Foltz family relates to a number of usual, happy family evenings. Some of them, however, include unnerving moments in which their son, Trevor, experienced multiple seizures. At first they…

Continue Reading How Rising Drug Costs Affected a Family Living with Infantile Spasms

New Delivery System for Pulmonary Arterial Hypertension Treatment Remodulin Approved by the FDA

According to a story from PR Newswire, the U.S. Food and Drug Administration had approved the New Drug Application for an innovative new delivery system for Remodulin, a therapy that…

Continue Reading New Delivery System for Pulmonary Arterial Hypertension Treatment Remodulin Approved by the FDA