Rheumatoid (RA) is one of the most common forms of arthritis that affects people. According to Rheumatoiarthritis.org statistics, 1% of the global population has rheumatoid arthritis. While this includes both…
According to a story from finanznachrichten.de, the Korean biopharmaceutical company Biocure Technology, Inc., recently announced the results of a pre-clinical trial that tested CAR-T cell therapy as a treatment for acute…
According to a story from Healio, recent testing has found that FibroScan, a form of medical imaging, is capable of detecting nonalcoholic steatohepatitis earlier than it would be possible to…
According to a story from Market Screener, the pharmaceutical company Retrotope has recently released data that indicates that the company's experimental product RT001 is capable of halting disease progression for…
According to a story from EurekAlert!, a recent study from the University of Zurich has illuminated the connection between the gastrointestinal flora and multiple sclerosis. The discovery illuminates the potential…
According to a story from Charcot-Marie-Tooth News, a recent meeting between the US Food and Drug Administration (FDA) and patient advocacy groups took place to discuss the future development of…
The United States Food and Drug Administration has awarded Orphan Drug Designation to an investigational drug for narcolepsy, and there are plans to carry out a Phase 2 study to…
According to a story from the New York Times, Harvard University has recently called for the retraction of 31 studies authored by a cardiologist associated with the school. The cardiologist…
Encouraging topline results from a pivotal Phase 3 study into a drug for Charcot-Marie-Tooth type 1A disease have been shared by Pharnext. To find out about this news in more…
Don't miss this special two day event made possible by The Myelodysplastic Syndromes Foundation , Sylvester Comprehensive Cancer Center at the University of Miami and The Aplastic Anemia and MDS International Foundation MDS…
According to recent research, a bacteria that causes some forms of stomach cancer may also be responsible for increased risk of colon cancer. The research points to this being especially…
Of pediatric cancers, brain cancer has the highest rate of mortality and medulloblastoma is the most common of brain cancer diagnoses in children. It's a brain cancer that originates in…
The Undiagnosed Diseases Network (UDN) is working to help patients with rare undiagnosed conditions find answers. So far, they have helped more than two hundred patients achieve a diagnosis. About…
October is Achondroplasia (Dwarfism) Awareness Month! Achondroplasia is a bone growth disorder that causes dwarfism. Dwarfism is defined as a condition of short stature as an adult. People with achondroplasia are…
According to a story from globenewswire.com, the biopharmaceutical company Orphazyme has officially endorsed a set of guidelines that outline how rare disease patient advocacy organizations and drug companies should interact…
Increasingly, researchers are looking into how the human microbiome – the trillions of microbes that live on and in your body – can influence various aspects of health, from nutrition…
According to a story from Pharma Voice, Dr. Scott Gottlieb, the current commissioner of the US Food and Drug Administration (FDA) has recently released a statement in regards to efforts…
When you’re first diagnosed with something like breast cancer, ovarian cancer or another rare condition there’s a million things racing through your mind and a million and one things to…
According to a story from BioSpace, AstraZeneca and Merck released a joint announcement recently stating that the US Food and Drug Administration (FDA) has granted Orphan Drug designation to olaparib…
The Patient Advocate Foundation has recently begun to expand the reach of its popular Co-Pay Relief program. The Co-Pay Relief program is designed to provide financial assistance to qualifying patients.…
According to a story from baledezi.wordpress.com, a recent study demonstrated that a chemotherapy agent that originates from a sea sponge was able to prolong the lives of women with metastatic…
According to a story from pm360online.com, the orphan lung disease company Savara recently announced that they had completed their enrollment target of 135 patients for a Phase 3 clinical trial…
According to a story from Roche, the pharmaceutical company recently released new data from its ongoing clinical trial, which is testing the company's investigational product risdiplam. In this study, the…
Gene editing has come a long way as a treatment option in the last several years. Rapid advances in technology continue to find more and more novel therapies. According to…
According to a story from the Washington Post, new cases of the unusual, polio-like disease called acute flaccid myelitis have continued to appear through the United States recently. There are…
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