It's shocking and quite frankly, devastating, to be diagnosed with any type of cancer at any age. It can be hard to stay positive as your life completely changes as…
According to a story from publicnow.com, the drug development company Sarepta Therapeutics recently announced that is has completed negotiations for a licensing agreement with Lysogene, a biopharmaceutical company. This agreement…
According to a story from The Sydney Morning Herald, the Australian government recently announced that it will be adding Galafold, a drug used to treat rare Fabry disease, to the…
A study funded by the Lustgarten Foundation, the largest private funder of pancreatic cancer research in America, has shown promising results. The scientists are hopeful that their work could lead…
According to a story from ScienceNews, a recent study has revealed an unusual connection between the appendix and Parkinson's disease. This research found that people who received an appendectomy (surgery…
Happy November! As we recover from Halloween and prepare for Thanksgiving, take a moment to check out some recent FDA announcements. FDA grants breakthrough therapy designation to UGN-101 for urothelial…
According to a story from BioPortfolio, the biopharmaceutical company GenSight Biologics recently announced that the first patient has received treatment in a Phase I/II clinical trial testing the company's experimental…
According to a story from The Daily Texan, professor Marian Williams-Brown from the University of Texas is conducting research in an effort to develop a more effective approach for detecting…
According to a story from Business Insider, two researchers from Stanford University, Lawrence Steinman and Jonathan Rothbard, have decided to start a new company called Katexco Pharmaceuticals. This startup will…
A recent article published by the University of California San Francisco looks back at the development of gene therapy technology and explores how scientists at the university are working to…
RAREfest, an event organised by the Cambridge Rare Disease Network (CRDN), will bring together patients, scientists, researchers, clinicians, support groups, businesses, and the public, to engage and educate people about…
According to a story from Biospace, the biopharmaceutical company Ultragenyx Pharmaceutical Inc. recently reported that its experimental product UX007 failed to achieve its primary endpoint in a recent clinical trial.…
According to a story from bioengineer.org, a new bacterial imaging tool has been deemed to be safe and practical device for used in the medical setting, a recent study claims.…
According to a story from Medical Xpress, a recent study suggested that the targeted cancer drug olaparib could be an effective treatment for women with ovarian cancer that has been…
November 1st is Acromegaly Awareness Day! What is Acromegaly? Acromegaly is a hormonal disorder characterized by significant, abnormal growth, caused by an excess amount of growth hormone, or GH. GH is produced…
Goethe University in Frankfurt, Germany has been awarded a grant of more than one million euros as part of a large-scale project in Europe to standardise and make available clinical…
An on-going study of an investigational drug for primary biliary cholangitis has been given the go-ahead to continue by a safety monitoring board. The planned review recommended that the Phase…
Ellen Pompeo, who plays a doctor on Gray's Anatomy and was featured as a guest on Ellen Degeneres' The Ellen Show. We recently read an opinion piece on drjengunter.wordpress.com from OB/GYN,…
Any research that's done with rare disease patients in mind, working to improve their treatment and experience is wonderful. However, when collaboration between both researchers and organizations working to support…
The Cambridge Rare Disease Network’s RAREfest, a festival focusing on rare diseases, will bring together researchers, scientists, patients, and the public. It’s taking place on the 30th November and 1st December in…
CNS-PNET brain cancers are typically diagnosed by type according to their specific location in the brain as well as how they appear underneath a microscope. However, its recently become clear…
Growing up without a diagnosis is hard. In a world which frequents new scientific discoveries, you're still living as a medical mystery. When no one knows the answer, patients often…
Novartis has announced positive findings from their research into brolucizumab, an investigational drug being developed to treat neovascular age-related macular degeneration. This data comes from year two of the…
According to a story from Parkinson's News Today, a recent review of Parkinson's disease research found that there is not enough data that explains the link between mutations of several…
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