Lisa Deck’s Journey Part 1
At age twenty one, Lisa was about to graduate college and had a promising future career in front of her. All that was left was graduation itself. The week before…
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Lisa Deck’s Journey Part 1
Study Measures Adherence to Improve Outcomes for Chronic Kidney Disease Patients
"We want to have better ways to figure out who is non-adherent so we can focus our efforts better on those patients who may require more assistance or specific resources…
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Study Measures Adherence to Improve Outcomes for Chronic Kidney Disease Patients
National Geographic Features Innovative Research That Will Advance Precision Medicine
Perhaps the most difficult thing about rare disease research is that not only do the conditions affect only a small portion of the population, but like every diagnosis, they affect…
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National Geographic Features Innovative Research That Will Advance Precision Medicine
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Will Pancreatic Cancer Become The Second Most Common Cause of Cancer-Related Death in the US?
According to a story from PR Newswire, pancreatic cancer rates in the US are increasing by almost two percent each year. This puts the disease in position to become the…
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Will Pancreatic Cancer Become The Second Most Common Cause of Cancer-Related Death in the US?
New Discovery Could Lead to New Treatments for Anemia in Juvenile Idiopathic Arthritis, Lupus, and Malaria
Juvenile idiopathic arthritis, Lupus, and Malaria are diseases which currently have limited treatment options. But a new discovery by researchers at the Benaroya Research Institute (BRI) could potentially lead to…
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New Discovery Could Lead to New Treatments for Anemia in Juvenile Idiopathic Arthritis, Lupus, and Malaria
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An AI Tool Was Able to Predict The Severity of Ovarian Cancer
According to a story from New Scientist, a team of scientists at the Institute of Cancer Research in London were able to develop an AI tool that was able to…
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An AI Tool Was Able to Predict The Severity of Ovarian Cancer
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New Combination Therapy for Renal Cell Carcinoma Gains European Approval
According to a story from BioPortfolio, the Bristol-Myers Squibb Company recently announced that the European Commission has recently approved the first combination treatment for renal cell carcinoma available in the…
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New Combination Therapy for Renal Cell Carcinoma Gains European Approval
Research in Humans Promote Findings for Deadly Age-Related Disease Treatment
A January 4th post by the Lancet's EBioMedicine headlined the first-in-human pilot study results published by UT Health San Antonio in collaboration with the Mayo Clinic and the Wake Forest School…
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Research in Humans Promote Findings for Deadly Age-Related Disease Treatment
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Researchers Pioneer Method to Reverse IPEX Syndrome Mutation
According to a story from news-medical.net, a team of researchers from UCLA have successfully developed an approach that allows for the reversal of the mutation that is responsible for the…
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Researchers Pioneer Method to Reverse IPEX Syndrome Mutation
Free MDS Patient and Caregiver Forum in CA!
A free MDS Patient & Family/Caregiver Forum, sponsored by The MDS Foundation Inc., will be held in Beverly Hills, California on February 2nd. When: Saturday, February 2nd, 2019 Where: Beverly…
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Free MDS Patient and Caregiver Forum in CA!
Third Party Medical Providers: a Necessity for the Right to Life
For those with a complicated medical diagnosis, state-funded health insurance bodes little practicality. Patients living with rare and chronic disease must schedule visits to multiple specialty clinics and physicians, especially…
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Third Party Medical Providers: a Necessity for the Right to Life
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Graphene Might One Day Help Diagnose ALS, MS
According to an article at UIC Today, scientists at the University of Illinois at Chicago have conducted experiments suggesting graphene might be useful in diagnosing amyotrophic lateral sclerosis (ALS) or…
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Graphene Might One Day Help Diagnose ALS, MS
Reata Pharmaceuticals Announces Phase 3 Study of ADPKD Treatment
According to an article from PM360, Reata Pharmaceuticals has announced that its end-of-Phase 2 meeting with the Food and Drug Administration went according to plan. The American pharmaceutical company based…
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Reata Pharmaceuticals Announces Phase 3 Study of ADPKD Treatment
Heidi Jo in her days of service.
Heidi Jo’s Familial Chylomicronemia Syndrome Story
Heidi Jo Price, beautiful and brave, has jumped out of airplanes with a pack on her back as a member of the 173 Airborne Brigade Combat Team. What brought this…
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Heidi Jo’s Familial Chylomicronemia Syndrome Story
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First Patient Enrollment Announced for Angelman Syndrome Nutritional Study
According to a story from BioPortfolio, the keto-medical nutrition company Disruptive Nutrition recently announced that the first patient had been enrolled in a research study which will test a unique…
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First Patient Enrollment Announced for Angelman Syndrome Nutritional Study
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Finding New Treatment Combinations for Chronic Lymphocytic Leukemia
According to a story from Onclive, combination therapies are likely to play an increasing role in the treatment of chronic lymphocytic leukemia. In this video, leukemia treatment experts discuss the…
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Finding New Treatment Combinations for Chronic Lymphocytic Leukemia
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How Does a Patient’s Sex Determine Outcomes in Glioblastoma?
According to a story from The Conversation, scientists have determined that sex plays a significant role in outcomes when it comes to treating the rare and deadly brain cancer glioblastoma.…
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How Does a Patient’s Sex Determine Outcomes in Glioblastoma?
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Medical First – Boy Born with Gaucher Disease and Kostmann Syndrome
According to an article at Gaucher Disease News, the first known case of a person with both Gaucher disease and severe congenital neutropenia was examined in a case study that…
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Medical First – Boy Born with Gaucher Disease and Kostmann Syndrome
First “Right-To-Try” Drug Administered to Glioblastoma Patient
The Right-To-Try Law is a federal legislation which allows terminally ill patients the opportunity to use experimental drugs that don't yet have FDA approval. It's controversial at best, but some…
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First “Right-To-Try” Drug Administered to Glioblastoma Patient
New Phase 2 Clinical Trial for Merkel Cell Carcinoma will Combine Therapies
Merkel cell carcinoma (MCC) is a form of skin cancer. In the United States, about 2,500 people are diagnosed with MCC each year. The condition is treated with chemotherapy, immune…
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New Phase 2 Clinical Trial for Merkel Cell Carcinoma will Combine Therapies
FDA Sets Date for Ruling on EPP New Drug Application
According to CheckOrphan, Clinuvel Pharmaceuticals recently announced that their drug Scenesse has received a Prescription Drug User Fee Act (PDUFA) date from the FDA, set for July 8th of this…
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FDA Sets Date for Ruling on EPP New Drug Application
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Sanofi Announces Successful Phase 3 Study of aTTP Drug
According to an article from PM360, the French biopharmaceutical company Sanofi has announced successful results at the end of a phase 3 study of their hopeful acquired thrombotic thrombocytopenic purpura…
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Sanofi Announces Successful Phase 3 Study of aTTP Drug
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Recruitment for Phase 3 Study of Heart Failure Drug Complete
According to a press release published by Global News Wire, Australian pharmaceutical company Mesoblast Limited has completed recruitment for its phase 3 study of Revascor - their experimental drug to…
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Recruitment for Phase 3 Study of Heart Failure Drug Complete
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More Effective Mouse Model for Hirschsprung’s Disease Developed
According to a story from Eurek Alert!, a team of scientists affiliated with the University of Helsinki have successfully developed a new, more useful Hirschsprung's disease mouse model. This disease…
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More Effective Mouse Model for Hirschsprung’s Disease Developed
Lack of Diversity in Clinical Trials is a Danger to Multiple Sclerosis Patients
According to an article at Multiple Sclerosis News Today, at least one doctor at U.K. Healthcare's Kentucky Neuroscience Institute wants more diversity in clinical trials. It's not just about social…
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Lack of Diversity in Clinical Trials is a Danger to Multiple Sclerosis Patients
