The Advisory Committee on Heritable Disorders is hosting a webinar on September 24, as part of its mission to reduce morbidity and mortality in newborns and children who have, or are…
According to a story from curetoday.com, the American Society of Clinical Oncology (ASCO) recently announced its 2018 Advance of the Year. For 2018, the organization chose to highlight progress that…
According to a story from BioPortfolio, the drug company Alnylam Pharmaceuticals recently presented research findings related to hATTR amyloidosis, a rare disease. The study was presented at the Second European…
When people think of the effects of climate change, it is usually about how it affects our external world, causing storms, floods, heat, and rapidly changing and more severe climates.…
According to a story from biotech-now.org, the behavior of health insurance companies in the US is just one of the many problems that plagues our health system. While Americans pay…
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A recent article in Northwestern's University Health reported that although the survival rate for cancer patients has vastly improved over the past twenty years, the deaths due to metastatic cancer…
According to a story from Benzinga, the biopharmaceutical company Inventiva has recently announced that it has recruited the first patients in a study of biomarkers in Maroteaux-Lamy syndrome. The study…
According to a story from sectorpublishingintelligence.co.uk, the biopharmaceutical company Orchard Therapeutics recently announced the release of some data from an ongoing proof-of-concept study. This special trial is testing the company's…
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Clustered Regularly Interspaced Short Palindromic Repeats is more commonly known as CRISPR. As reported recently in Science News, the CRISPR/Cas9 “molecular scissors” is slated to make its highly anticipated debut…
According to a press release from Maryland-based Viela Bio, the US Food and Drug Administration (FDA) recently agreed to review the Company's Biologics License Application for its neuromyelitis optica spectrum…
Wearable monitoring technology that tracks a persons movement, heartbeat, and bodily functions has become popular across society because it gives us a window into our bodies and to watch the…
According to a story from The Globe and Mail, Canada's Patented Medicine Prices Review Board announced last month that drug prices would be subject to new regulations. These new rules…
According to a publication from Charcot Marie Tooth News, biomedical law expert Timo Minssen recently gave a presentation at the New York Genome Center where he discussed the potential ethical…
Hey...Is That Autumn on the Horizon? Well...kind of but sort of no, it is still pretty hot where we are; but it is only a matter of time before we…
Maisie Green Maisie Green is a 20-month-old little girl whose insurance has finally approved coverage for a life-altering spinal muscular atrophy treatment. Two weeks ago she received the singular infusion…
According to a story from curetoday.com, cancer patient registries have had a major impact in improving outcomes for patients. Take the story of Rhonda and Jeff Meckstroth as an example.…
As reported in Forbes Magazine, Researchers at the University of Pennsylvania are exploring a new tool for encouraging patients to comply with health care recommendations for colonoscopies, an invasive procedure…
As reported in Cystic Fibrosis News Today, a new drug combination created for Cystic Fibrosis, a mix of Vertex's elexacaftor, tezacaftor, and Kalydeco has been granted priority review. The new…
Originally reported in People Magazine, a family struggled for years to figure out what was happening to their son, Cohen Bramlee, who for years received his nutrients from a central…
According to a story from The Rheumatologist, a rare complication linked to the monoclonal antibody drug rituximab called rituximab-induced serum sickness (RISS) appears when patients using the drug have immune…
Last week, we spotlighted a New York Times story about how under the Trump Administration’s new immigration policy, six migrants undergoing lifesaving treatments would be abruptly deported; including a young woman…
According to a story from globenewswire.com, the biopharmaceutical company Processa Pharmaceuticals, Inc., has recently announced that it has completed enrollment for its phase 2 clinical trial. This trial will be…
According to a story from news-medical.net, a team of researchers associated with the University of Alberta made a significant discovery when the identified a never before recognized biomarker for myasthenia…
According to a story from the Sunday Post, sisters Shona and Kirsty Young, aged 24 and 29 years respectively, were both born with the devastating rare disease cystic fibrosis. However,…
According to a press release from California-based biotechnology company Zogenix, the Company recently completed a multi-million dollar acquisition of Modis Therapeutics. Before its acquisition, Modis focused on the development of…
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