Review of Rare Movement Disorders in India and the United States

A recent article published in India’s Pharma Literati cites The World Health Organization as not having endorsed a definition for rare diseases. The European Union defines 'rare' as less than…

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Experimental Treatment for Cryopyrin-Associated Periodic Syndrome (CAPS) Shows Potential in Early Trial
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Experimental Treatment for Cryopyrin-Associated Periodic Syndrome (CAPS) Shows Potential in Early Trial

According to a story from Financial Buzz, the biotechnology company Inflazome recently announced that it has completed a phase 1 clinical trial. This trial was testing the company's experimental treatment…

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Immunocompromised During COVID-19? Not Much Has Changed in the Lives of Many Rare Patients

Relapsing polychondritis is a rare disease which causes damage to the cartilage, trachea, and lungs. It's an autoimmune condition meaning an overzealous immune response causes the body to attack its own…

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Study Highlights Need to Support Youth Acting as Amyotrophic Lateral Sclerosis Caregivers

A recent study, conducted my Melinda Kavanaugh from the University of Wisconsin, Milwaukee, examined the role of children who are acting as caregivers for those diagnosed with amyotrophic lateral sclerosis…

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Will Gene Therapy Finally Provide a Cure for Huntington’s Disease?

According to a recent article published in Pharmaceutical-Technology, uniQure’s gene therapy AMT-130 may lower levels of the huntingtin protein that causes the disorder. An abnormal gene is responsible for damage…

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Biotherapeutics Reduced This Patient’s Tumors After Seven Other Therapies Failed

A recent Biospace article covers a news release from 4D Pharma in Leeds, England. 4D has announced the first worldwide clinical confirmation of a biotherapeutic product. MRx0518 has been combined…

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Ten Year TARGET-ASTHMA Study Using Data for New Therapies and to Develop New Drugs

TARGET PharmaSolutions Inc. recently announced enrollment of the first patients in its ten year, ten thousand patient asthma study. Professor Michael Wechsler, M.D. pulmonologist at the National Jewish Health organization…

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