Global Blood Therapeutics (GBT) will submit their Marketing Authorization Application (MAA) for Oxbryta to the EMA by 2021, says a recent BioSpace press release. Ultimately, the MAA will seek regulatory…
According to Parkinson's News Today, researchers have created a silicon-based antioxidant agent that can be supplemented into the diet to prevent neurodegeneration and issues with coordination and motor skills associated…
Pulmonary hypertension can be caused by a variety of other conditions, often making it difficult to distinguish. A problem that medical professionals often encounter is differentiating pulmonary arterial hypertension (PAH)…
Oncternal Therapeutics, Inc. (Nasdaq: ONCT), a clinical-stage biopharmaceutical company focused on the development of novel oncology therapies, today announced that the United States Food and Drug Administration (FDA) has granted…
If you could take a vaccine to prevent disease progression, would you? Well, researchers recently tested the efficacy of such a vaccine for patients with Parkinson's disease. The experimental and…
According to Medical Xpress, a new gene therapy has been studied for the treatment of Duchenne muscular dystrophy. This treatment, SRP-9001, has been shown to deliver micro-dystrophin and improve functional…
Why are most people able to tolerate cat’s hair while some people have severe reactions to the ubiquitous and practically invisible dust mites? A recent SciTech Daily article followed La…
During the beginning stages of COVID-19, there was a common refrain: "It's no big deal. It's just like the flu." But just a few months into this global pandemic, we…
This morning, SynAct Pharma AB announced in a press release that they began a Phase II clinical trial to determine the efficacy and safety of AP1189 on treating patients with…
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
