According to a story from theindychannel.com, brothers Elias, age eleven, and Emmett, age seven, were both born with the rare bleeding disorder hemophilia A. However, this has not stopped them…
Orphan drug designations are granted by the FDA to drugs and biologics that are developed for the treatment of rare diseases. According to a recent article in Biospace, Oncternal…
According to Ankylosing Spondylitis News, a new treatment, Hulio, has been approved by the FDA. It is a treatment for ankylosing spondylitis and other inflammatory disorders. Although it has been…
According to a recent press release from Albireo Pharma, the first participant has enrolled in the BOLD trial. The BOLD trial, which stands for Biliary atresia and the use…
In the early 1990s, Dean Kamen was at the mall when he came up with an idea. After seeing a man in a wheelchair struggle to be noticed by…
According to a story from Parkinson's News Today, a recent study has found a new connection between two different features that appear in Parkinson's disease. These features are lysosomal dysfunction…
According to a story from Korea Biomedical Review, Seoul National University Hospital (SNUH) in South Korea has just announced recently that the process of recruiting patients for the National Bio…
Alpha-synuclein cause damage to mitochondria in patients with Parkinson's disease. These researchers wanted to see if they could see the membrane changes fostered by the alpha-synuclein. The examination of such…
While the world is waiting for a vaccine to prevent, mitigate, or cure COVID-19, the investigational drug remdesivir continues to show promise. The FDA recently gave it Emergency Use…
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