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Daily Archives: April 14, 2021

Home » Archives for April 14, 2021
WM: The Latest Treatment Approaches
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WM: The Latest Treatment Approaches

  • Post author:James Moore
  • Post published:April 14, 2021
  • Post category:Waldenstrom Macroglobulinemia

Recently the Leukemia & Lymphoma Society (LLS), in coordination with the International Waldenstrom's Macroglobulinemia Foundation (IWMF), hosted its Waldenström's Macrogloblinemia (WM) Patient Education Program webinar on April 7th, 2021. Patient…

Continue Reading WM: The Latest Treatment Approaches
IP6 Can Starve and Kill Medulloblastoma
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IP6 Can Starve and Kill Medulloblastoma

  • Post author:Jessica Lynn
  • Post published:April 14, 2021
  • Post category:Medulloblastoma

What if we could harness a naturally occurring compound to starve and kill serious brain tumors? According to Medical XPress, researchers from Queen Mary University of London are working to…

Continue Reading IP6 Can Starve and Kill Medulloblastoma
Study: Treatment and Clinical Factors in Occlusive Retinal Vasculitis
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Study: Treatment and Clinical Factors in Occlusive Retinal Vasculitis

  • Post author:Kendall Mason
  • Post published:April 14, 2021
  • Post category:Vasculitis

A study published in Physician's Weekly investigated the visual outcomes, clinical features, and treatment of individuals with occlusive retinal vasculitis (ORV), a condition that is characterized by inflammation in the vessels of…

Continue Reading Study: Treatment and Clinical Factors in Occlusive Retinal Vasculitis
Txnip Gene Therapy Shows Promise for RP
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Txnip Gene Therapy Shows Promise for RP

  • Post author:Jessica Lynn
  • Post published:April 14, 2021
  • Post category:Retinitis pigmentosa

A variety of gene mutations cause retinitis pigmentosa (RP) - but how do those genes affect the degeneration of rod and cone photoreceptors in the eyes? According to Medical XPress,…

Continue Reading Txnip Gene Therapy Shows Promise for RP
April is Fabry Disease Awareness Month: Spreading Rare Disease Awareness
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April is Fabry Disease Awareness Month: Spreading Rare Disease Awareness

  • Post author:James Moore
  • Post published:April 14, 2021
  • Post category:Fabry Disease

According to a story from Fabry Disease News, the month of April is recognized as Fabry Disease Awareness Month, a time dedicated to spreading awareness about Fabry disease in the…

Continue Reading April is Fabry Disease Awareness Month: Spreading Rare Disease Awareness
New Data Available on GTB-3550 for AML, MDS
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New Data Available on GTB-3550 for AML, MDS

  • Post author:Jessica Lynn
  • Post published:April 14, 2021
  • Post category:Acute Myeloid Leukemia/Myelodysplastic syndromes

In a recent press release, immuno-oncology and biopharmaceutical company GT Biopharma, Inc. ("GT") shared the release of new data and results from the Phase 1/2 GTB-3550 TriKE clinical trial. Through…

Continue Reading New Data Available on GTB-3550 for AML, MDS
Rare Classroom: Pulmonary Arterial Hypertension
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Rare Classroom: Pulmonary Arterial Hypertension

  • Post author:James Moore
  • Post published:April 14, 2021
  • Post category:pulmonary arterial hypertension

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

Continue Reading Rare Classroom: Pulmonary Arterial Hypertension
Managing Excessive Worry and Fear to Avoid Health Consequences
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Managing Excessive Worry and Fear to Avoid Health Consequences

  • Post author:Tom Seaman
  • Post published:April 14, 2021
  • Post category:Dystonia

I think it would be safe to say that everyone is afraid of something. Sometimes the fear is justified and sometimes not. In this article, I want to focus on…

Continue Reading Managing Excessive Worry and Fear to Avoid Health Consequences
April 15 is International Pompe Day: Spreading Pompe Disease Awareness
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April 15 is International Pompe Day: Spreading Pompe Disease Awareness

  • Post author:James Moore
  • Post published:April 14, 2021
  • Post category:Pompe Disease

According to a story from Pompe Disease News, April 15th will be recognized as the eighth annual International Pompe Day. This day is meant to spread awareness about Pompe disease…

Continue Reading April 15 is International Pompe Day: Spreading Pompe Disease Awareness

OF INTEREST


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X-Linked Hypophosphatemia: Unnderstanding this Hereditary, Progressive, and Lifelong Condition


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Catalyst’s LEMS Aware Podcast Helps Connect Patients

Patient Stories

STUDY OF THE WEEK

Welcome to Study of the Week. We go in-depth and select a study we think is of particular interest, discussing details, explaining its importance, who may be impacted and lots more!

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RARE CLASSROOM

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most mysterious diseases and conditions. This series is an opportunity to learn the basics about some of the diseases that almost no one hears much about.

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