Enrollment Complete for Phase 3 Study Evaluating aPAP Treatment Molgramostim
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Enrollment Complete for Phase 3 Study Evaluating aPAP Treatment Molgramostim

Clinical-stage biopharmaceutical company Savara Inc. was founded on a desire to develop innovative therapies for people living with rare respiratory diseases. The company's work over the past few years centers…

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These Nonprofits Just Shelled Out $5.2 Million to Fund An Experimental Parkinson’s Drug
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These Nonprofits Just Shelled Out $5.2 Million to Fund An Experimental Parkinson’s Drug

According to a story from PR Newswire, the biotech company Mission Therapeutics was just awarded $5.2 million in funding to support MTX325, the company's investigational Parkinson's disease therapy. Intended to…

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Toripalimab Combined with Bevacizumab Meets Primary Endpoint for Advanced Hepatocellular Carcinoma
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Toripalimab Combined with Bevacizumab Meets Primary Endpoint for Advanced Hepatocellular Carcinoma

Shanghai's Junshi Biosciences Co. (The Company) recently announced in Biospace, that its product, toripalimab (TUOYI®), combined with bevacizumab as a first-line therapy for hepatocellular carcinoma (HCC), met its endpoints in a…

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Rare Community Profiles: Volv’s Innovative Approach Harnesses the Power of AI for Rare Disease Detection
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Rare Community Profiles: Volv’s Innovative Approach Harnesses the Power of AI for Rare Disease Detection

  Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families, advocates, scientists, and more.…

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SLEEP 2024: Presented Data Highlighted Possible Benefits of ALKS 2680 for Narcolepsy Type 1
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SLEEP 2024: Presented Data Highlighted Possible Benefits of ALKS 2680 for Narcolepsy Type 1

The American Academy of Sleep Medicine and the Sleep Research Society held the 38th annual SLEEP meeting in early June 2024. The meeting allows stakeholders across the sleep sphere to…

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Rare Community Profiles: Astellas Pharma’s Dr. Anthony Yanni Discusses the Success of the First-Ever Patient Advocacy Organization Action Week (PAOAW)
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Rare Community Profiles: Astellas Pharma’s Dr. Anthony Yanni Discusses the Success of the First-Ever Patient Advocacy Organization Action Week (PAOAW)

  Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families, advocates, scientists, and more.…

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Long-Term Safety and Efficacy Data Available on Vabysmo for Diabetic Macular Edema
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Long-Term Safety and Efficacy Data Available on Vabysmo for Diabetic Macular Edema

Since its development and approval, Vabysmo has been a game-changer in the ophthalmologic space. The injectable VEGF and Ang-2 inhibitor treats diabetic macular edema (DME), macular edema with retinal vein…

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Phase 2 Obesity Clinical Trial from Palatin Set to Begin
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Phase 2 Obesity Clinical Trial from Palatin Set to Begin

According to a story from drugs.com, the biopharmaceutical company Palatin Technologies, Inc., which is specializing in the development of therapies that interact with the melanocortin receptor system, recently announced the…

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SLEEP 2024: Two Studies Explore Link Between Narcolepsy and Cardiovascular Disease Risk
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SLEEP 2024: Two Studies Explore Link Between Narcolepsy and Cardiovascular Disease Risk

The SLEEP 2024 Annual Meeting took place this year from June 1 to June 5 in Houston, TX. During the course of this premier sleep conference, stakeholders across the sleep…

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Rare Community Profiles: The Third Elephant on the Ramp to the Ark: How Carl’s Advocacy Affected His iMCD Journey
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Rare Community Profiles: The Third Elephant on the Ramp to the Ark: How Carl’s Advocacy Affected His iMCD Journey

  Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families, advocates, scientists, and more.…

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Long COVID: What Have We Learned?
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Long COVID: What Have We Learned?

Individuals who appear to have Long COVID may exhibit a variety of symptoms lasting weeks or even years. The latest estimates are that about 10-20% of people infected with SARS-CoV-2…

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Rare Community Profiles: Superhero Liam Battles KAND with the Help of Shriners Children’s
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Rare Community Profiles: Superhero Liam Battles KAND with the Help of Shriners Children’s

  Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families, advocates, scientists, and more.…

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