A groundbreaking advance in diabetes care has emerged from recent clinical research: a new cell therapy has successfully restored natural insulin production in 83% of participants living with diabetes. This…
Duchenne Muscular Dystrophy (DMD) is a severe, progressive neuromuscular disease that primarily affects boys, leading to muscle weakness, loss of ambulation, and premature death. Among therapeutic advances, ataluren has emerged…
June 2025 marked a month of significant progress in cancer care, as the FDA approved several new therapies and treatment combinations across a range of cancer types. As reported by…
The Accredited Duchenne Centers (ADC) Program, spearheaded by the World Duchenne Organization (WDO), is a pioneering global initiative designed to standardize and elevate care for individuals living with Duchenne Muscular…
For decades exercise has been recommended to improve the quality of life. More recently and perhaps more importantly, exercise has been highly recommended for cancer patients. Most people realize that…
KalVista Pharmaceuticals has achieved a significant milestone with the U.S. Food and Drug Administration’s (FDA) approval of its new oral therapy for hereditary angioedema (HAE), marking a breakthrough for patients…
A new milestone has been reached in the search for effective treatments for dry age-related macular degeneration (AMD), as the first patient has now been dosed in a clinical trial…
Fujifilm Corporation’s investigational therapy FF-10832 has received Orphan Drug Designation from the U.S. Food and Drug Administration (FDA) for the treatment of biliary tract cancer, according to a recent announcement…
Editor's Note: This article was originally published on 3/5/25, and is being republished due to ongoing efforts by Patient Worthy to raise awareness of COPD. A presenter at the COPD…
My name is Kelly Baughman, and I grew up in a small town in Louisiana—tight-knit, faith-driven, and yes, I went to church and summer camp with the Duck Dynasty family.…
The United States is experiencing its worst measles outbreak in decades, with cases rising sharply across multiple states. Health officials attribute this surge primarily to declining childhood vaccination rates, fueled…
A recent study has brought attention to the complex challenges faced by children with hidradenitis suppurativa (HS), a chronic and often painful skin condition. According to new research summarized by…
A new study has found that corticosteroids, commonly used to manage symptoms in lung cancer patients, may reduce the effectiveness of immunotherapy treatments. The research, highlighted by News-Medical.net, sheds light…
Recent research highlights a significant connection between eosinophilic gastrointestinal diseases (EGIDs) and atopic conditions such as asthma, eczema, and allergic rhinitis. EGIDs, which include disorders like eosinophilic esophagitis, gastritis, and…
Chronic obstructive pulmonary disease (COPD) remains one of the leading causes of illness and mortality worldwide, but new research highlights how its prevalence and overall disease burden vary considerably across…
Editor's Note: This article was originally published on 7/11/23 and is being republished in an ongoing effort by Patient Worthy to raise awareness of COPD. Tobacco consumption has been heavily…
Cogent Biosciences has announced new clinical trial results indicating that its drug BEZUCLASTINIB offers promising benefits for patients with indolent systemic mastocytosis (ISM), a rare and chronic disorder characterized by…
Saarland University’s medical team, led by Professor Bergita Ganse, has discovered an entirely new approach for monitoring the healing of bone fractures through measuring blood supply to the tissue at…
For most families, a sunny day is a source of joy, but for the family of five-year-old Evie-Rose, sunlight brings distress and fear. As was reported in the Scottish Sun,…
Recent research outlined by Medical Xpress offers a deeper understanding of why CDK4/6 inhibitors, a class of drugs widely used to treat certain cancers, sometimes fail to deliver lasting benefits.…
Go here to read Part 1, Part 2, Part 3, and Part 4 of this series provided by TREND Community about Prader-Willi Syndrome. On March 5, 2025, TREND Community released its…
In 2017, Jamie Shultz was feeling on top of the world. She was 25 years old, engaged to the man of her dreams, had just passed the Bar exam, and…
The Vancouver Island community has come together in an emotional show of support for nine-year-old Charleigh Pollock after news broke that the B.C. government is discontinuing coverage of the only…
A groundbreaking development in respiratory medicine has emerged with the launch of a first-of-its-kind inhaler designed for conditions beyond the traditional scope of asthma and chronic obstructive pulmonary disease (COPD). …
A recent research article in ScienceDirect.com details a breakthrough in visualizing the rapid, complex movements of proteins using high-speed atomic force microscopy (HS-AFM). This cutting-edge imaging technology allows scientists to…
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