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In a collaborative effort between University College Institute (UCL) and the University of Cambridge, researchers have engineered personalized computational frameworks—often termed tumor "digital twins"—to forecast therapeutic responses and overcome drug…
Clear cell renal cell carcinoma (ccRCC) is the most common type of kidney cancer. It begins in the kidney’s filtering cells and gets its name from the appearance of the…
As reported on Inside Precision Medicine, a large study from Denmark found that children conceived with certain assisted reproductive technologies had a higher relative rate of cancer than children conceived…
One of the most persistent hurdles in biology is the natural, age-related decline of female fertility. As women age, both the quantity and quality of their eggs (the "ovarian reserve")…
Exercise, yoga, psychological support and other approaches that do not involve medication or surgery may help people with low back pain—and may be cost-effective, according to a review of 20…
A C. diff infection can turn a hospital stay into a much harder experience. The bacterium can cause severe diarrhea, abdominal pain and inflammation of the colon. In some cases,…
Many people spend very little time contemplating their liver, often ignoring this critical organ until a major medical issue arises. In contrast, health culture in countries like France has long…
For decades, patients diagnosed with IgA nephropathy—an autoimmune condition where trapped immune complexes inflame and damage the kidney’s filtering units (glomeruli)—faced a discouraging outlook. Typically diagnosed in young adults aged…
The international study will examine whether MTX325 affects processes linked to Parkinson’s disease, as well as assess its safety and tolerability. As reported in a recent press release, Mission Therapeutics says…
CAPS, or Cryopyrin-Associated Periodic Syndromes, is a group of rare autoinflammatory diseases caused by a genetic mutation affecting the cryopyrin protein, leading to increased inflammation. CAPS is usually linked to…
The University of Michigan has opened a $10 million research center dedicated to histotripsy, a technique that uses focused sound waves to destroy tumors. The center will make specialized equipment…
Fabry disease is a rare inherited condition caused by changes in the GLA gene. These changes can lead to low or absent activity of an enzyme called alpha-galactosidase A. As…
IndoUSrare and GORD Foundation are honored to announce the 2026 Abbey Meyers Khushi Bridging RARE Award Honorees: Rare Disease is a global problem, a human problem, and the individuals below…
Two papers published in Nature Communications report new findings about roginolisib, an experimental cancer drug being developed by iOnctura. One study describes how the drug interacts with a cancer-related enzyme…
As reported on Inside Precision Medicine, a novel optogenetics-based treatment may offer a new path toward restoring some visual function in people with advanced retinitis pigmentosa (RP), according to findings…
Aspire: “ We aspire to improve the lives of children and adults affected by PANS/PANDAS and other immune-related encephalopathies by closing the gap between symptom onset and access to treatment…
Two-year University of Arizona study will use human brain-cell models to investigate sex-specific biology and help guide future research and clinical trials. Critical Path Institute (C-Path) and the University of…
Genetic testing is now more available than ever before. For those who suspect a genetic disorder, the best route is often through a genetic counselor. They can advise you not…
As reported on SciTechDaily, a large research review suggests age-related losses in muscle mass, strength, and physical function may have a stronger association with dementia risk than obesity alone. Maintaining…
Diabetic retinopathy affects approximately 30% of adults with diabetes and stands as one of the leading causes of vision loss among working-age individuals worldwide. The condition damages the delicate blood…
People who inherit a rare change in the EGFR gene may be much more likely to develop lung cancer. Their risk is about 25 times higher than that of people…
Patients in the United States wait an average of 34 to 50 days (roughly 1 to 1.5 months) for an initial neurology appointment, with wait times stretching up to 4…
As reported on MedPage Today, an experimental immunotherapy called gotistobart helped patients with advanced squamous non-small cell lung cancer (NSCLC) live longer than standard chemotherapy in the phase III PRESERVE-003…
“For people living with a progressive rare disease, time is measured differently. Research and clinical trials can take years while patients continue to lose strength and function,” said Kathryn Bryant…
One-time treatment provides a new option for pediatric patients with a rare, progressive genetic disorder As announced in a recent press release, the U.S. Food and Drug Administration has approved…
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