Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia four years ago. He was treated with a methylating agent While he was being treated with a hypomethylating agent, Rose researched investigational drugs being developed to treat relapsed/refractory AML.

    Doctor Urges His Colleagues to Apply Lessons from COVID-19 to Rare Diseases
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    Doctor Urges His Colleagues to Apply Lessons from COVID-19 to Rare Diseases

      In a recent contribution to MSN, Dr. Christopher Austin, director of the NIH Advancing Translational Sciences, compared the medical community’s record-breaking approach to the COVID-19 pandemic with current efforts…

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    Researchers Have Uncovered a Missing Link That May Lead to Development of Brain Disorder Treatments

    For years, scientists have known the mechanisms underlying normal, as well as the disease-causing (pathogenic) versions, of prions. But according to a recent article published in Sci-Tech Daily, no one…

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    Parents Receive News That Their Child’s Niemann-Pick Disease Medication Will be Discontinued

    Marian McGlockin was eighteen months old when she was diagnosed with Niemann-Pick Type C disease, a rare and fatal disorder. Marian could barely speak and was unable to walk. According…

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    Levodopa, Parkinson’s Disease, and Dyskinesia: The Benefits of Levodopa May Not Outweigh the Risk

    The majority of Parkinson’s patients treated with Levodopa experience relief from the major motor effects of Parkinson’s. However, according to a recent article in Biospace, after prolonged use of Levodopa…

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    Oncology Researchers Are Beginning to Focus on Ways to Stop Uncontrolled Cancerous Cell Division

    According to a recent article in Fierce Biotech, most cancers progress through constant cell division. Scientists at Vanderbilt University are determined to find the reason for this mysterious cell division.…

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    Two Sisters With Rare Diseases Are Working Towards Recovery With the Help of Their Family

    According to a recent article featured in News5Cleveland.com, there are over seven thousand rare diseases worldwide that affect over thirty million people in the United States. Several days ago, patients…

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